Navigation Links
Leukodystrophy in Medical Technology

Shire Enhances its Orphan Drug Pipeline With the Acquisition of a New Clinical Candidate for Metachromatic Leukodystrophy

BASINGSTOKE, England and CAMBRIDGE, Massachusetts, April 24 /PRNewswire-FirstCall/ -- Shire plc (LSE: SHP, NASDAQ: SHPGY), the global specialty biopharmaceutical company, announces the acquisition of arylsulfatase -A (ASA) an Enzyme Replacement Therapy (ERT) in Phase 1-2 clinical trials for Me...

AIMSPRO is Awarded TGA Orphan Status for the Treatment of Amyotrophic Lateral Sclerosis

...mon form of Motor Neuron Disease (MND), also known as Lou Gehrig's disease. AIMSPRO has already achieved TGA Orphan Status for the treatment of Krabbe leukodystrophy (Krabbe's disease). Daval is now evaluating an international, multi-centre, placebo controlled, Randomised Clinical Trial to determine whether later s...
Leukodystrophy in Medical Definition

Pathology

... GM1 gangliosidoses - Mucolipidosis type IV - Gaucher's disease - Niemann-Pick disease - Farber disease - Fabry's disease - Metachromatic leukodystrophy - Krabbe disease Neuronal ceroid lipofuscinosis ( Batten disease ) - Cerebrotendineous xanthomatosis - Cholesteryl ester storage disease ( W...
Leukodystrophy in Medical Dictionary

Leukodystrophy

Leukodystrophy refers to a group of disorders characterized by progressive degeneration of the white matter of the brain. The leukodystrophies are caused by imperfect growth or development of the myelin sheath, the fatty covering that acts as an insulator around nerve... leukodystrophy ( ...

Krabbe disease

...ine resources about Krabbe disease . United leukodystrophy Foundation: The leukodystrophies are genetically d...ty of Maryland Medical Center. globoid cell leukodystrophy ( ) n. An inherited metabolic encephalopathy of i... Krabbe disease , also called globoid cell leukodystrophy (GCL), is a rare, ... Type 1, or infantile Krabb...

Canavan

...isease, one of the most common cerebral degenerative diseases of ... Well, hello there! Welcome to Trudi Canavan's Website Index. ... United leukodystrophy Foundation: The leukodystrophies are genetically determined progressive disorders that affect the brain, spinal cord and peripheral nerves. ... ...

Adrenoleukodystrophy

...rview, X-linked adrenoleukodystrophy describes several ... Adrenoleukodystrophy is passed down from parents to their children as an ... United leukodystrophy Foundation: The leukodystrophies are genetically determined progressive disorders that affect the brain, spinal cord and peripheral nerves. ... ...
Leukodystrophy in Biological Technology

Shire's New Product Portfolio Delivers Strong Quarterly Performance

...f Shire's US development plan and to strengthen the chances of regulatory and commercial success in the US. METAZYM (HGT-1111) - Metachromatic leukodystrophy ("MLD") - Shire has an ongoing enzyme replacement therapy program for the treatment of MLD, which is a lysosomal storage disorder that results ...

Shire Delivers Strong Quarter: Driven by $243m of New Product Sales (+164% YOY Growth). Revenue Guidance Upgrade.

...dies. It is anticipated that this development program will support global filings in the second half of 2009. METAZYM (HGT-1111) - Metachromatic leukodystrophy ("MLD") - METAZYM is being investigated for the treatment of MLD and has completed a Phase 1b clinical trial in twelve patients in Europe and an ...

Following a Good Start to the Year Shire Reaffirms Full Year 2008 Financial Guidance

...global rights to the clinical candidate arylsulfatase-A ("ASA"), currently known as METAZYM(TM), being investigated for the treatment of Metachromatic leukodystrophy ("MLD"). MLD is caused by a deficiency in the enzyme ASA which causes an excess concentration of sufatide in cells and an ensuing breakdown of myelin....
Other Tags
(Date:9/16/2014)... (PRWEB) September 16, 2014 Synergy Research ... comprehensive report gives the best detail and analysis of ... pulled from a variety of sources, including Ministry of ... Orange Paper will give readers actionable intelligence on clinical ... Paper is relied on by the local and international ...
(Date:9/16/2014)... Florida Hospital announced today it is teaming up ... and become the Presenting Sponsor of the 2014-15 and ... and wellness partner. As the Presenting Sponsor for the ... and name inclusion on all Lightning advertising campaigns and ... been a sponsorship partner of the Lightning since 2011, ...
(Date:9/16/2014)... Whatisfinalexpenseinsurance.com has released a new ... life insurance for seniors. , Finding affordable life insurance ... big part of the insurance market has moved online. ... that clients can use when shopping for life coverage. ... important for providing financial security for vulnerable family members. ...
(Date:9/16/2014)... serve of dairy food may reduce the risk of ... foods have not traditionally formed part of the diet. ... by Emeritus Professor Mark Wahlqvist from Monash University,s Department ... Institute, considered the role increased consumption of dairy foods ... longevity. , "In a dominantly Chinese food culture, ...
(Date:9/16/2014)... 15, 2014A comparison of five-year sexual function ... external beam radiotherapy (EBRT) versus combination EBRT ... vessel-sparing radiation therapy makes cure possible without ... presented today at the American Society for ... , The study examined the patient-reported outcomes ...
Breaking Medicine News(10 mins):Health News:Synergy Research Group Debuts Ukraine Orange Paper 2Health News:Florida Hospital Teams up with the Tampa Bay Lightning as the New Presenting Sponsor of the 2014-15 and 2015-16 Lightning Seasons 2Health News:Florida Hospital Teams up with the Tampa Bay Lightning as the New Presenting Sponsor of the 2014-15 and 2015-16 Lightning Seasons 3Health News:Life Insurance for Seniors - Clients Can Find Fast Life Insurance By Comparing Online Quotes! 2Health News:A heart-felt need for dairy food 2Health News:Prostate cancer patients surveyed 5 years after vessel-sparing RT report preserved sexual function 2Health News:Prostate cancer patients surveyed 5 years after vessel-sparing RT report preserved sexual function 3
(Date:9/16/2014)... pipeline (KXL) would likely increase oil sands extraction, according ... the non-profit organization Near Zero. The results are detailed ... includes both supporters and opponents of the pipeline. ... lead to significantly higher greenhouse gas emissions, with the ... , "This report examines three main scenarios discussed by ...
(Date:9/16/2014)... years after the Hesperides vessel returned to Spain culminating ... have an increasingly clear picture of how the global ... the input of pollutants from the atmosphere is not ... most remote areas of the planet, and it is ... are presented this week in CSIC Residence for Researchers ...
(Date:9/16/2014)... for independence later this week, its Government could face ... fracking is necessary, research has revealed. , The University ... perception of shale gas extraction in the UK since ... of the border are the least supportive of fracking. ... the University,s School of Geography, said: "The clear move ...
Breaking Biology News(10 mins):Keystone XL would likely raise oil sands production and greenhouse gas emissions 2The Malaspina Expedition confirms that pollution reaches even the most remote areas of the ocean 2The Malaspina Expedition confirms that pollution reaches even the most remote areas of the ocean 3Scottish people most sceptical on fracking, survey shows 2Scottish people most sceptical on fracking, survey shows 3
Other Contents