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Leukodystrophy in Medical Technology

Shire Enhances its Orphan Drug Pipeline With the Acquisition of a New Clinical Candidate for Metachromatic Leukodystrophy

... Replacement Therapy (ERT) in Phase 1-2 clinical trials for Metachromatic leukodystrophy (MLD) from the Danish company Zymenex A/S (Zymenex). MLD is a serious, ... Scriver et al 1995 Notes to editors Disease Background Metachromatic leukodystrophy (MLD) is in the family of lysosomal storage diseases (LSD's). MLD is an ...

AIMSPRO is Awarded TGA Orphan Status for the Treatment of Amyotrophic Lateral Sclerosis

... form of Motor Neuron Disease (MND), also known as Lou Gehrig's disease. AIMSPRO has already achieved TGA Orphan Status for the treatment of Krabbe leukodystrophy (Krabbe's disease). Daval is now evaluating an international, multi-centre, placebo controlled, Randomised Clinical Trial to determine whether later ...
Leukodystrophy in Medical Definition

Pathology

... GM1 gangliosidoses - Mucolipidosis type IV - Gaucher's disease - Niemann-Pick disease - Farber disease - Fabry's disease - Metachromatic leukodystrophy - Krabbe disease Neuronal ceroid lipofuscinosis ( Batten disease ) - Cerebrotendineous xanthomatosis - Cholesteryl ester storage disease ( ...
Leukodystrophy in Medical Dictionary

Leukodystrophy

... Adreno leukodystrophy Dr Trisha Macnair Adreno leukodystrophy (ALD) is a rare inherited disorder that leads ... death . Take a look at the causes. Adreno leukodystrophy describes any of several closely related ...

Cml

... - chronic lymph ocytic (CLL) Leukemia - hairy cell Leukemia - nonlymphocytic (ANLL) Leukemic reticuloendotheliosis Leukemoid reaction leukodystrophy - metachromatic Leukoplakia Lewy body dementia ... Previously approved for the treatment of patients with chronic myeloid leukemia ( ...

Metabolic Diseases

... sugar found in milk ( lactose ) can lead to accumulation of another sugar called galactitol, ... Storage or metabolic diseases Ad renal leukodystrophy (ALD) Gaucher's disease Hurler's syndrome Mucopolysaccharidoses (MPS) ... Adults and children over 6 months of age who need regular ...

Mixed tension migraine

... Mixed tension migraine Alternative Names: Headache - mixed tension migraine Treatment : ... Mixed Tension Migraine MLD (Metachromatic leukodystrophy ) MMK (Surgeries for Female Stress Incontinence ) MMR - Vaccine Molar Pregnancy ( Hydatidiform Mole ) ... Migraine without aura (no ...

Molar pregnancy

... : Can a mom's depression affect her baby? Postpartum thyroiditis Pre- ejaculation fluid: Can it cause pregnancy ? MLD (Metachromatic leukodystrophy ) Molar Pregnancy ( Hydatidiform Mole ) Mole ( Birthmarks - Pigmented) Molluscum Contagiosum Mongolian Blue Spots ... age younger than 20 ...

Molluscum contagiosum

... vulgaris, verruca plantar is, HPV, acrochordon, molluscum contagiosum , seborrheic keratosis , and verruca plana; ... MLD (Metachromatic leukodystrophy ) Molar Pregnancy ( Hydatidiform Mole ) Mole ( Birthmarks - Pigmented) Molluscum Contagiosum Mongolian Blue Spots ... CRYOTHERAPY: Using ...
Leukodystrophy in Biological Technology

Shire's New Product Portfolio Delivers Strong Quarterly Performance

... Shire's US development plan and to strengthen the chances of regulatory and commercial success in the US. METAZYM (HGT-1111) - Metachromatic leukodystrophy ("MLD") - Shire has an ongoing enzyme replacement therapy program for the treatment of MLD, which is a lysosomal storage disorder that results ...

Shire Delivers Strong Quarter: Driven by $243m of New Product Sales (+164% YOY Growth). Revenue Guidance Upgrade.

... It is anticipated that this development program will support global filings in the second half of 2009. METAZYM (HGT-1111) - Metachromatic leukodystrophy ("MLD") - METAZYM is being investigated for the treatment of MLD and has completed a Phase 1b clinical trial in twelve patients in Europe and an ...

Following a Good Start to the Year Shire Reaffirms Full Year 2008 Financial Guidance

... rights to the clinical candidate arylsulfatase-A ("ASA"), currently known as METAZYM(TM), being investigated for the treatment of Metachromatic leukodystrophy ("MLD"). MLD is caused by a deficiency in the enzyme ASA which causes an excess concentration of sufatide in cells and an ensuing breakdown of ....
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(Date:9/16/2014)... use among teens in the United States is on the ... the new study also found that alcohol use, binge drinking ... the ages of 12 and 17 also dropped between 2002 ... 12 and older across the United States revealed that between ... age group also dropped from 8.9 percent to 5.2 percent. ...
(Date:9/16/2014)... equally preserved in cancer patients suffering from malignant spinal ... 10 Gy of radiation therapy (RT), compared to patients ... RT each, according to research presented today at the ... , Malignant spinal cord compression (MSCC) is a ... occurs when a tumor,s secondary deposit presses on the ...
(Date:9/16/2014)... to be on the heavy side. Researchers at the ... seven in every ten obese adults underestimate how much ... much less often. Mothers of overweight or obese children ... misjudge their obese mothers, size, says lead author Tracy ... in the Journal of General Internal Medicine , ...
(Date:9/16/2014)... -- While abnormalities in the adrenergic and noradrenergic ... thought to play a role in the development ... has been no genetic evidence of this connection. ... Columbia University,s Mailman School of Public Health and ... the ADRB2 gene and childhood adversity. For individuals ...
(Date:9/16/2014)... The Pain Center of Arizona (TPC), ... has selected Analance ™, Ducen ’s BI ... TPC seeing hundreds of thousands of patients annually, the ... through “home grown” systems trying to piece together actionable ... “Our current tools were not scalable and, in ...
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(Date:9/15/2014)... Mass. (September 15, 2014) The so-called central ... makes proteinhas long provided a simplified explanation for ... living organisms. , In reality, of course, ... schema first articulated nearly 60 years ago by ... double-helix structure. For one, there are multiple types ...
(Date:9/15/2014)... both plants and animals alike. , Understanding just how ... to the design of better drugs for diabetes patients ... vegetables farmers are able to grow. Stanford University researchers ... cell by piecing together proteins slightly wider than the ... determine the size, shape and orientation of one of ...
(Date:9/15/2014)... will allow us to better understand how the ... scenarios and provide the type of environmental data ... and siting of protected areas," said Paula Whitfield, ... Coastal Ocean Science (NCCOS) and lead author of ... within the temperate-tropical transition zone, where historically, both ...
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