PTC Therapeutics Receives $2.6 Million in Government Grants

... - Funding supports continued focus on rare disorders - SOUTH PLAINFIELD, N.J., June 15 ... to support clinical development programs in rare disorders. The U.S. Department of Defense ... PTC299 in neurofibromatosis type 2 (NF2), a rare genetic tumor. Separately, the Food and Drug ...

Cimzia(R) (certolizumab pegol) Provides Long-Term Remission and Response Rates in Infliximab-Refractory Crohn's Patients

... including CIMZIA, has been associated with rare cases of new onset or exacerbation of clinical ... radiographic evidence of demyelinating disease. rare cases of neurological disorders, including ... of CIMZIA in patients with these disorders. rare reports of pancytopenia, including aplastic ...

ViroPharma Incorporated Honored by the National Organization for Rare Disorders

... Corporate Award at the National Organization for rare Disorders (NORD) Annual Gala for its work in ... (C1 esterase inhibitor (human)) to market for a rare and devastating disorder -- hereditary angioedema ... achievements to improve the lives of people with rare diseases. NORD represents the nearly 30 million ...

Europium discovery

... belongs to a group of elements called the rare earth elements. These elements are magnetic; ... the magnetism," Schilling explained. Of the rare earths, europium is most likely to lose its ... structure. In an elemental solid almost all rare earths are trivalent, which means that each atom ...

23andMe and mondoBIOTECH Partner to Advance Research of Rare Diseases

... dedicated to the development of treatments for rare diseases, today announced at the World Economic ... they are collaborating to advance research of rare diseases. The announcement marks the return of ... to facilitate research of the genetic bases of rare and potentially fatal diseases, such as Pulmonary ...

New Data Suggest CIMZIA(R) (Certolizumab Pegol) Active in Treating Moderate to Severe Crohn's Patients With Fistulizing Disease

... CIMZIA (R) , has been associated with rare cases of new onset or exacerbation of clinical ... radiographic evidence of demyelinating disease. rare cases of neurological disorders, including ... (R) in patients with these disorders. rare reports of pancytopenia, including aplastic ...

University of Florida and Cyntellect Collaborate to Unlock Mysteries of Cancer Stem Cells

... and analysis of cancer stem cells (CSCs), rare cells which are believed to be directly involved ... signaling pathways and markers associated with rare cells, such as CSCs. This information will ... efficient and highly accurate means of isolating rare cells and making them readily available for ...

Gleevec Receives FDA Priority Review as First Therapy to Reduce Recurrence of Gastrointestinal Stromal Tumors After Surgery

... therapeutic approaches to patients with rare diseases EAST HANOVER, N.J., Aug. 27 ... myelogenous leukemia (Ph+ CML) and five other rare diseases. Novartis also has a therapy for the ... and multiple treatments in the pipeline targeting rare diseases. Filing data The study on which the ...

Edison Pharmaceuticals Receives Commendation From the City of San Jose

... recognizes contribution to city and children with rare diseases SAN ... the company's contributions in fighting rare childhood diseases. The commendation recognizes ... Biocenter, is focused on developing drugs for rare diseases that impair energy metabolism. Edison ...

Highmark Blue Cross Blue Shield and National Association Name Area Hospitals as Blue Distinction Centers for Complex and Rare Cancers

... as Blue Distinction Centers for Complex and rare Cancers. Complex and rare cancers comprise approximately 15 percent of ... Blue Distinction Centers for Complex and rare Cancers are facilities within participating Blue ...

Aton Pharma Announces the Appointment of Dr. Fred Eshelman to Management Board

... Chief Executive Officer of Aton Pharma. "He is a rare individual -- both an accomplished entrepreneur ... treatments for under-treated diseases and rare illnesses around the world. Aton's mission is to ... with sales in over 30 countries, targets rare and orphan metabolic, neurological, ...

Abbott Receives FDA Approval for SIMCOR(R) (Niaspan(R) / simvastatin), a Novel Combination Medicine for Comprehensive Cholesterol Management

... occur, as this may be a sign of a serious but rare muscle disorder, from which rare cases of death have occurred. Health care ... may increase the risk of rhabdomyolysis, a rare condition that causes muscles to breakdown. The ...

Genzyme and Isis Announce Strategic Alliance Including Exclusive Worldwide License of Mipomersen

... is preserved. The homozygous form is a very rare condition estimated to affect approximately one ... company's products and services are focused on rare inherited disorders, kidney ... in disease areas including CNS and certain rare diseases. Any statement describing Isis' ...

The World Economic Forum Announces Technology Pioneers 2008: Mondobiotech Selected

... of treatment options for fatal and neglected rare diseases. It successfully develops human peptides to treat patients affected by rare diseases. This is done through its "search and ... of treatment options for fatal and neglected rare diseases. Mondobiotech currently has 30 products ...

Abbott's HUMIRA(R) Receives Positive Opinion From EMEA for Treatment of Moderate to Severe Plaque Psoriasis

... information. Serious infections, sepsis, rare cases of tuberculosis (TB), and opportunistic ... including HUMIRA, have been associated in rare cases with demyelinating disease and serious allergic reactions. rare reports of pancytopenia including aplastic anemia ...

REMICADE(R) Becomes First Anti-TNF Biologic Therapy to Treat One Million Patients Worldwide

... in patients on REMICADE or other TNF blockers are rare but occur more often than expected for people in ... azathioprine or 6-mercaptopurine have developed a rare type of lymphoma, hepatosplenic T cell lymphoma ... skin rash and/or joint pain. There have been rare cases of serious liver injury in people ...

MedImmune to Present RSV Surveillance and Cost-Effectiveness Data at American Academy of Pediatrics National Conference & Exhibition

... visit http://www.medimmune.com . Very rare cases (<1 per 100,000 patients) of anaphylaxis and rare (<1 per 1,000 patients) severe acute ... reported following re-exposure to Synagis and rare severe hypersensitivity reactions occurred on ...

Micromet Receives European Orphan Drug Designation for Treatment of Acute Lymphoblastic Leukemia with BiTE Antibody Blinatumomab

... is to stimulate research and development of medicinal products for rare diseases by providing incentives to the pharmaceutical industry such as ... resources. This initiative helps to give patients suffering from rare diseases access to the same quality of treatment as other patients. ...

PacificGMP and USC to Collaborate on Recombinant Protein Development and Manufacturing for Phase 1 Clinical Trial

... 1 clinical trial for treatment of dystrophic epidermal bullosa (DEB), a rare disease in children born with defects in the gene that encodes type VII ... pride to work with a team so determined to develop treatments for this rare but debilitating disease." "We appreciate the PacificGMP team's ...

Morphotek(R), Inc. Announces a Research Collaboration Agreement with Synageva BioPharma Corporation to Develop Potential Treatments for Cancer and Infectious Disease

... areas including oncology, organ dysfunction, autoimmune diseases and rare disorders. The company has generated a diverse pipeline of product ... ADCC (Antibody Dependent Cellular Cytotoxicity), novel proteins for rare diseases, and next generation and follow-on cytokines. Further information ...

YM BIOSCIENCES' SUBSIDIARY RESOLVES PROPOSED ARBITRATION WITH ONCOSCIENCE AG

... based in Wedel, Germany founded with the goal developing treatments for rare diseases that are not being addressed by major pharmaindustrial companies. ... mission and therefore the scientific benefit, lies in the research of rare diseases and the improvement of therapeutic possibilities. Oncoscience's ...

China Sky One Medical, Inc. Signs Agreement with Taiwan Golden Biotechnology Corp. on Development of New Anti-Cancer Drug

... a kind of compound extracted from Antrodia Cinnamomea Chang & Chou, a rare medicinal fungus that grows naturally inside the Cinnamonum kanehirae tree ... project, which we believe has a very bright future, especially since it is rare to find a compound that can fight cancer without any side effects," said ...

Publication of Shire plc's Annual Report 2008

... products when commercialized, in particular products for the treatment of rare genetic diseases such as REPLAGAL and ELAPRASE, may be high compared to ... portion of the Group's revenues for certain products for treatment of rare genetic diseases are concentrated with a small number of customers. ...

DOR BioPharma Appoints Gregg Lapointe, CPA, MBA, to its Board of Directors

... to the development and commercialization of medicines for patients with rare diseases. Sigma-Tau is DOR's North American partner for orBec(R) and its ... and is a member of the Corporate Council of the National Organization for rare Diseases (NORD). "We are very pleased to welcome Gregg Lapointe to our ...

Shire Announces Opening of Office in Japan

... of Shire Human Genetic Therapies, the business unit focusing on treating rare diseases. "Through the opening of this new office, we have taken a ... a significant amount of time working on the development of products for rare diseases. In his new role, Mr. Fujiwara will oversee the implementation ...

VAP Cholesterol Test Helps In Search For New Heart Disease Drugs

... University of Maryland researchers have found an association between a rare gene mutation and heart protection. The information reported in a recent ... present in 5 percent of a Lancaster County, Pa., Amish community. This rare genetic occurrence prevents the production of a protein (apoC-III) that ...

BioMarin Announces the Planned Retirement of Dr. Emil Kakkis, Chief Medical Officer

... him to be able to devote more of his time to personal endeavors related to rare diseases. Dr. Kakkis will continue to be a consultant for the company for ... the opportunity to devote additional time to developing an institute for rare diseases and legislation to support ultra-orphan drug development," said ...

Alexion Reports Third Quarter 2008 Results

... authorities in 2009. Soliris as a Treatment for Patients with Other rare and Severe Diseases With the FDA approval of Soliris as a treatment for ... disorders, including three severe, life-threatening and rare hematologic disorders: atypical hemolytic uremic syndrome ("aHUS"), a ...

Large-scale genetic study sheds new light on lung cancer

... in this gene have previously been shown to cause neurofibromatosis 1, a rare inherited disorder characterized by unchecked growth of tissue of the ... previously been shown to play a role in ataxia telangiectasia, which is a rare inherited neurological disorder of childhood, and in various types of ...

SAFC Hitech(TM) Expands Electronic Materials Portfolio With the Introduction of Scintillation Crystal Growth Halides

... meet these changing conditions. SAFC Hitech's portfolio includes several rare earth and alkali earth halides specifically designed to tackle these ... continued, saying, "Looking ahead, we anticipate an increase in demand for rare earth halides as the technology for crystal growth continues to improve. ...

GBS/CIDP Foundation to Hold 10th International Symposium

... relatives and caregivers who have experienced or had to deal with these rare and potentially catastrophic disorders. GBS is an inflammatory disorder ... muscles and face. GBS can develop in persons of any age. CIDP is a rare disorder of the peripheral nerves with weakness occurring over two or more ...

Alexion's Soliris(R) Receives 2008 Prix Galien USA Award for Best Biotechnology Product

... evaluating the promise of complement inhibition for the treatment of other rare and life-threatening kidney, blood, transplant and neurologic disorders." ... from drugs approved during the past five years. About PNH PNH is a rare blood disease that affects an estimated 8,000 to 10,000 people in North ...

Enobia Pharma Presents PreClinical Data Showing ENB-0040 Significantly Improved Survival and Healed Skeletal Manifestations of Severe Hypophosphatasia in Mice

... and prevents bone hypomineralization associated with hypophosphatasia, a rare genetic bone disease. Dr. Isabelle Lemire presented the positive results ... clinical program investigating ERT with ENB-0040 as a treatment of this rare and often crippling genetic bone disorder in August. Dr. Thomas Loisel, ...

Biotest Diagnostics Receives FDA Clearance for Full Line of Traditional Blood Bank Reagents

... Blood Grouping Reagents -- Biotestcell(R) Reagent Red Blood Cells -- rare Typing Reagents -- Anti-Human Globulins -- Enhancement Reagents -- ... identification panels, Coombs control cells and reverse ABO products. rare typing reagents will include anti-C, anti-E, anti-c, anti-e, anti-Lea, ...

Genzyme Corporation and PTC Therapeutics Announce Collaboration on Small Molecule for Genetic Diseases

... cause of disease in a subset of patients affected by more than 2,400 rare genetic disorders. PTC and Genzyme are well suited as partners to realize ... in the life sciences. The company's products and services are focused on rare inherited disorders, kidney disease, orthopaedics, cancer, transplant, and ...

A New President at the Head of the Genethon Laboratory

... and developing the innovative biotherapies for the treatment of rare diseases. My ambition is also to open the way to substantial joint ... biotechnology enterprise whose aim is to develop biotherapies for rare genetic diseases. Genethon is the promoter of the first gene therapy trial ...

Raptor Pharmaceuticals Corp. Receives FDA Orphan Drug Designation for Cysteamine in Huntington's Disease

... Agency ("EMEA") to treat nephropathic cystinosis ("cystinosis"), a rare lysosomal storage disease. Preclinical results suggest that cysteamine has ... ("Bennu"), plans to evaluate cysteamine in patients with HD. HD is a rare and hereditary neurological disease thought to occur in approximately 1 ...

Aton Pharma Announces Distribution Partnership in the Asia Pacific Region

... company providing essential treatments for under-treated diseases and rare illnesses around the world. Aton's mission is to improve patient outcomes ... portfolio of seven products, with sales in over 30 countries, targets rare and orphan metabolic, neurological, cardiovascular and ophthalmic ....

Aton Pharma Announces Distribution Partnership in Brazil

... company providing essential treatments for under- treated diseases and rare illnesses around the world. Aton's mission is to improve patient outcomes ... portfolio of seven products, with sales in over 30 countries, targets rare and orphan metabolic, neurological, cardiovascular and ophthalmic ....

Alexion Reports First Quarter 2008 Results

... patients with PNH and research promising therapies for other serious and rare diseases." Research and Development: Soliris as a Treatment for ... analyze data later this year. Soliris as a Treatment for Patients with rare and Severe Diseases ...