Navigation Links
Spark Therapeutics Achieves Recruitment Goal in Phase 3 Gene Therapy Clinical Study for Inherited Blindness
Date:1/14/2014

rm the lives of patients and re-imagine the treatment of debilitating diseases. Spark's lead gene therapy candidate, for RPE65-related blindness, is currently in Phase 3 clinical trials with the potential to be the first approved gene therapy in the U.S., and the first in a series of therapies to address the significant unmet needs of patients living with blindness due to inherited retinal dystrophies.

Spark's founding team includes scientists who led the movement to develop gene therapy as a new treatment paradigm, establishing clinical proof of concept in the eye and liver and contributing key insights to the field that have resulted in a resurgence of industry interest in gene-based medicines. In addition to the Phase 3 program in RPE65-related blindness, the company has a Phase 1/2 program in hemophilia B, and preclinical programs to address neurodegenerative diseases and other inherited retinal dystrophies and hematologic disorders. Spark has rights to a proprietary manufacturing platform that has an unparalleled track record of success in supporting clinical studies across diverse therapeutic areas and routes of administration. The company's expertise across research, clinical, regulatory and manufacturing builds on a legacy of innovation and excellence in gene therapy established by Spark's team while at The Children's Hospital of Philadelphia Center for Cellular and Molecular Therapeutics. To learn more visit www.sparktx.com.

Media Inquiries:
Jessica Rowlands
202-729-4089
Jessica.Rowlands@fkhealth.com


'/>"/>
SOURCE Spark Therapeutics
Copyright©2012 PR Newswire.
All rights reserved

Page: 1 2 3

Related medicine technology :

1. New Snoring Therapy Awarded The Prestigious Spark Award
2. Kalyspo Awarded Best of Ann Arbor SPARK Boot Camp
3. Next Generation Sequencing Bioinformatics Heats up: Nearing $1000 Genome Sparks Soaring Data Output
4. Spark Therapeutics to Present at 32nd Annual J.P. Morgan Healthcare Conference
5. Cell Therapeutics, Inc. (CTI) to Report First Quarter Financial Results on April 20
6. Faruqi & Faruqi, LLP Encourages Investors Who Suffered Substantial Losses Investing in Chelsea Therapeutics International, Ltd. to Contact the Firm
7. Argos Therapeutics Secures $25 million Series D Financing to Commence Phase 3 ADAPT Study in Patients with Metastatic Renal Cell Carcinoma (mRCC) in Mid-2012
8. Novelos Therapeutics Announces Successful Completion of First Cohort In Lung Cancer Trial With I-124-CLR1404 (LIGHT) Cancer-Targeted PET Imaging Agent at UW Carbone Cancer Center
9. Zacks Industry Outlook Highlights: Eli Lilly, Forest Labs, ViroPharma, Novartis and United Therapeutics
10. Oxford BioTherapeutics Appoints Senior Industry Leader to Head its New Clinical Development Operations in Basel, Switzerland
11. Nektar Therapeutics Reports Financial Results for the First Quarter of 2012
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:12/15/2014)... 2014 As medical device manufacturers join pharmaceutical ... language standard, content teams have a greater role to ... with the standard. Starting January 2015, Data Conversion Laboratory ... the benefits and the critical aspects of implementing SPL. ... by Howard Shatz , DCL,s SPL expert, and ...
(Date:12/15/2014)...   DaVita HealthCare Partners Inc.  (NYSE: ... and most innovative health care communities, today announced ... Clinical Research  (DCR) and  HealthCare Partners Clinical Research , ... clinical research and data analytics services, specifically in ... renal disease (ESRD), as well as primary care ...
(Date:12/15/2014)... BOSTON , December 15, 2014 ... discovery and development company, is pleased to announce the ... United States relating to its GPCR-focused drug ... US significantly strengthens the global patent estate covering Heptares, ... The suite of patents recently granted by the ...
Breaking Medicine Technology:Data Conversion Laboratory Helping Life Sciences Content Producers Understand the Impact and Benefits of Structured Product Labeling 2Data Conversion Laboratory Helping Life Sciences Content Producers Understand the Impact and Benefits of Structured Product Labeling 3DaVita Clinical Research and HealthCare Partners Clinical Research to Merge and Expand Clinical Trials and Data Analytics Capabilities 2DaVita Clinical Research and HealthCare Partners Clinical Research to Merge and Expand Clinical Trials and Data Analytics Capabilities 3DaVita Clinical Research and HealthCare Partners Clinical Research to Merge and Expand Clinical Trials and Data Analytics Capabilities 4Heptares Extends Global Patent Protection for GPCR-Focused Drug Discovery Platform With Grant of Core Patents in the United States 2
(Date:12/15/2014)... December 15, 2014 Cancer researchers have ... underlying genetic causes of deadly malignant pleural mesothelioma. Surviving ... on their website. Click here to read it ... of Hawaii Cancer Center, and New York’s Langone Medical ... pleural mesothelioma patients in an effort to pinpoint ...
(Date:12/15/2014)... Main Street Dental Team ( http://www.MainStreetDentalTeam.com ), Unionville’s ... new study providing evidence on the impact of 100% ... , Sufficient enough evidence already exists showing a negative ... drinks, with the onset of tooth decay. One question ... as 100% fruit juice, meaning it is completely natural ...
(Date:12/15/2014)... SIMpalm, a leading mobile app development company , ... client, which allows users to keep track of wines ... the right wine. At the center of WineMatch ... and wine information. All this information is assembled to ... that are close counterparts to one another are called ...
(Date:12/15/2014)... 15, 2014 Health Dialog, a ... today that it has received Patient Oriented Accreditation ... for its Disease Management (DM) Programs for asthma, ... coronary heart disease and diabetes. This marks the ... Health Dialog’s Disease Management (DM) Programs, reaffirming Health ...
(Date:12/15/2014)... (HealthDay News) -- Expert pilots process visual information more ... make better decisions during landings, a new study shows. ... for pilots to master, and 36 percent of all ... during final approach and landing. Researchers monitored the ... experienced pilots while they were at the controls of ...
Breaking Medicine News(10 mins):Health News:New Study Reveals Genetic Mutations That May Trigger Mesothelioma, According to Surviving Mesothelioma 2Health News:Main Street Dental Team, Unionville’s Most Innovative Dental Clinic, Comments on New Study Relating Pure Fruit Juice to Poor Oral Hygiene 2Health News:Use WinMatch Connect App to Keep Track of Wines You Like 2Health News:Health Dialog Receives NCQA Accreditation for Disease Management Programs 2Health News:Study Shows Why Expert Pilots Are Experts 2
... July 11 The Natural Orifice Surgery Consortium ... of the American Society for Gastrointestinal Endoscopy (ASGE) ... Surgeons (SAGES), today announced Olympus, continuing commitment to ... therapy known as Natural Orifice Translumenal Endoscopic Surgery(R), ...
... With the two year ... provider, has seen a 70 percent increase in women booking themselves in for botox and fillers ... ... the smoking ban upon us (1st July 2009), SurgiCare, a leading UK cosmetic surgery ...
... American ... providers of nutritional supplements and health-related content, today announced that Jim Barch has joined Healthy ... ... and ACI Capital , majority owners of Healthy Directions, LLC , one ...
... for American Medical Innovation today applauded President Obama,s appointment ... National Institutes of Health (NIH). , , (Logo: ... , "Dr. Collins is both a friend to ... said Council President Dick Gephardt. "His passion and understanding ...
... CHICAGO, July 10 Fundamental American freedoms suffered a ... rule of the Washington Board of Pharmacy took precedence over individual ... Stormans v. Selecky , overturning a lower-court decision blocking a ... Washington will now be forced to provide RU-486 (the abortion pill), ...
... Physicians for Human Rights (PHR) has ... a major New York Times story with ... investigations into alleged war crimes in Afghanistan in 2002. , ... why the Bush Administration impeded an FBI criminal probe of the ...
Cached Medicine News:Health News:NOSCAR(R) Increases NOTES(R) Research with Olympus Medical Systems Corporation Grant 2Health News:NOSCAR(R) Increases NOTES(R) Research with Olympus Medical Systems Corporation Grant 3Health News:NOSCAR(R) Increases NOTES(R) Research with Olympus Medical Systems Corporation Grant 4Health News:UK Smoking Ban Fuels Rise In Surgery 2Health News:Healthy Directions, LLC Welcomes Jim Barch as New Chief Executive Officer 2Health News:Healthy Directions, LLC Welcomes Jim Barch as New Chief Executive Officer 3Health News:Council for American Medical Innovation Applauds Appointment of Geneticist Francis Collins to Head National Institutes of Health 2Health News:Americans United for Life: Ninth Circuit Ruling on Pharmacists Endangers Fundamental Freedoms 2Health News:New Evidence that Bush Administration Impeded 3 Investigations into Alleged Massacre of Up to 2,000 Prisoners in Afghanistan 2Health News:New Evidence that Bush Administration Impeded 3 Investigations into Alleged Massacre of Up to 2,000 Prisoners in Afghanistan 3Health News:New Evidence that Bush Administration Impeded 3 Investigations into Alleged Massacre of Up to 2,000 Prisoners in Afghanistan 4
... assays are designed for ... 2000, a high-throughput, continuous ... IMMULITE 2000 offers testing ... a rapidly expanding menu ...
... radiography. The XPERT represents a research tool that ... in every digital x-ray image, thus being able ... heretofore were lost to the human eye. With ... to 8 x 8 in size, multi-color digital ...
The Solar Radius Chair is a multi-functional and cost effective working environment. It can be used for simple and advanced urodynamic studies as well as for routine gynecology investigations....
... is the ultimate in positioning ... popular accessories, the 6202 is ... of exam and treatment procedures. ... allow fast & precise positioning ...
Medicine Products: