Navigation Links
PTC Therapeutics Completes Enrollment of Pivotal Trial in Muscular Dystrophy
Date:2/3/2009

r the next year as we continue to work to develop additional innovative therapies for the muscular dystrophy community."

About DMD/BMD

Duchenne and Becker muscular dystrophy (DMD/BMD) are progressive muscle disorders that result in the loss of both muscle function and independence. DMD/BMD is perhaps the most prevalent form of the muscular dystrophies and is the most common lethal genetic disorder diagnosed during childhood today. Each year, approximately 20,000 children worldwide are born with DMD (one of every 3,500 male children). It is estimated that one in 10 DMD patients are likely to have a Becker presentation, a milder form of the disease that is associated with later manifestation of symptoms. Further information regarding DMD and BMD is available through the Muscular Dystrophy Association (www.mdausa.org), Parent Project Muscular Dystrophy (www.parentprojectmd.org) and the Association Francaise contre les Myopathies (www.afm-france.org).

About Ataluren (PTC124(TM))

Ataluren is an orally delivered, investigational new drug discovered by PTC Therapeutics. The drug is being developed as a new approach for the treatment of nonsense mutation genetic disorders. Nonsense mutations create a premature stop signal in the mRNA causing the ribosome to terminate translation before a full-length protein is generated. This causes the protein to be truncated and non-functioning. Ataluren is designed to allow the ribosome to continue translation of the mRNA, by overriding the premature stop signal leading to the formation of a functioning protein. Ataluren is a potential therapy for patients with nonsense mutation genetic disorders.

Ataluren has demonstrated proof of concept in Phase 2a clinical trials and is currently
'/>"/>

SOURCE PTC Therapeutics, Inc.
Copyright©2009 PR Newswire.
All rights reserved

Page: 1 2 3 4 5

Related medicine technology :

1. DNA Therapeutics Closes 2.2 Million EUR Series A Financing Round
2. Synvista Therapeutics Announces Termination of Clinical Trials of Alagebrium and SYI-2074 and Provides Business Update
3. Duska Therapeutics Completes Corporate Name Change to Cordex Pharma
4. Phico Therapeutics Receives GBP1 Million Award From the Wellcome Trust to Take Anti-MRSA Nasal Product Through Early Clinical Trials
5. Pixantrone Pre-NDA Communication from FDA Provides Cell Therapeutics Basis to Begin Rolling NDA Submission
6. Cephalon Signs Option Agreement to Acquire Ception Therapeutics
7. Amicus Therapeutics Announces Positive Progress of Three Lead Clinical Programs and General Outlook for 2009
8. Cara Therapeutics Initiates Phase II Proof-Of-Concept Trial of Novel Analgesic in Acute Post-Operative Pain
9. ExonHit Therapeutics Expands Strategic Collaboration With Allergan
10. Synvista Therapeutics Announces Published Data Demonstrating Elevation of Carboxymethyl-Lysine (CML) Is Associated with Decline in Renal Function and Arterial Stiffness in Older Adults
11. Synvista Therapeutics Announces First Dosing of SYI-2074 in Clinical Trial for Psoriasis
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:5/1/2015)... May 1, 2015  Misonix, Inc. (NASDAQ: ... designs, manufactures and markets innovative therapeutic ultrasonic products ... cosmetic surgery, laparoscopic surgery and other surgical applications, ... for the third quarter fiscal year 2015 on ... a conference call that same day, Thursday, May ...
(Date:5/1/2015)... May 1, 2015  Shares of Aerie Pharmaceuticals, Inc. ... value yesterday following the results of the Phase 3 ... Despite the trial failing to meet its end points, ... may come from future studies. An analyst ... current pipeline, financial review, analyst summary, valuation, and recommendation ...
(Date:4/30/2015)... April 30, 2015 Omnicell, Inc. (NASDAQ: OMCL ... solutions to healthcare systems, today announced results for its ... results: Revenue for the first quarter of 2015 was ... first quarter of 2014, and down $5.3 million or ... First quarter 2015 net income as reported in accordance ...
Breaking Medicine Technology:Misonix, Inc. To Report Third Quarter Fiscal Year 2015 Financial Results On Thursday, May 7, 2015 2All is Not Lost for Aerie Pharmaceuticals - VLM Research Issued by BrokerBank Securities, Inc. 2Omnicell Announces First Quarter 2015 Results 2Omnicell Announces First Quarter 2015 Results 3Omnicell Announces First Quarter 2015 Results 4Omnicell Announces First Quarter 2015 Results 5Omnicell Announces First Quarter 2015 Results 6Omnicell Announces First Quarter 2015 Results 7Omnicell Announces First Quarter 2015 Results 8Omnicell Announces First Quarter 2015 Results 9Omnicell Announces First Quarter 2015 Results 10Omnicell Announces First Quarter 2015 Results 11Omnicell Announces First Quarter 2015 Results 12Omnicell Announces First Quarter 2015 Results 13Omnicell Announces First Quarter 2015 Results 14Omnicell Announces First Quarter 2015 Results 15Omnicell Announces First Quarter 2015 Results 16Omnicell Announces First Quarter 2015 Results 17Omnicell Announces First Quarter 2015 Results 18Omnicell Announces First Quarter 2015 Results 19Omnicell Announces First Quarter 2015 Results 20Omnicell Announces First Quarter 2015 Results 21Omnicell Announces First Quarter 2015 Results 22Omnicell Announces First Quarter 2015 Results 23Omnicell Announces First Quarter 2015 Results 24Omnicell Announces First Quarter 2015 Results 25Omnicell Announces First Quarter 2015 Results 26Omnicell Announces First Quarter 2015 Results 27
(Date:5/2/2015)... Las Vegas, NV (PRWEB) May 02, 2015 ... vs. Pacquiao tickets for the long awaited event today, ... Las Vegas. Diehard boxing fans will be able to ... circuit events. , The fight that boxing fans have wanted ... a few months ago. Floyd “Money” Mayweather will step inside ...
(Date:5/2/2015)... 2015 ProText Kinetic 2 is a set ... Cut Pro X. ProText Kinetic 2 features 40 ... Cut Pro X . Easily create interactive text videos ... Studios' ProText Kinetic 2. , Using ProText Kinetic is as ... ProText Kinetic presets in the FCPX timeline. Playback the ...
(Date:5/2/2015)... 2015 “ Peachtree Audio ” was ... Report, which features the latest and coolest technology products ... special reporter for NewsWatch, conducted the review and shared ... , Music is an important part of people’s ... and given the royal treatment. Peachtree Audio does just ...
(Date:5/2/2015)... Southlake, TX (PRWEB) May 02, 2015 ... of skin laxity issues of the face, neck ... a new concept with real potential for the ... published by the ThermiHealth Clinical Advisory Council, ThermiGyn’s ... MD, FACOG, FACS, ACGE, concluded that ThermiGyn’s temperature ...
(Date:5/1/2015)... Texas (PRWEB) May 02, 2015 IDLife ... Texas, is proud to announce the addition of its ... Widerstrom is a life long athlete, growing up in ... passion after college by becoming a personal trainer and ... been the face of several TV shows highlighting her ...
Breaking Medicine News(10 mins):Health News:Cheap Floyd Mayweather vs. Manny Pacquiao Tickets: Ticket Down Has Last Minute Tickets for Mayweather vs. Pacquiao at the MGM Grand Garden Arena in Las Vegas 2Health News:Cheap Floyd Mayweather vs. Manny Pacquiao Tickets: Ticket Down Has Last Minute Tickets for Mayweather vs. Pacquiao at the MGM Grand Garden Arena in Las Vegas 3Health News:Pixel Film Studios Announced the Release of Protext Kinetic 2 for FPCX. 2Health News:Affordable High-End Audio Equipment was Featured on NewsWatch Television 2Health News:Study Demonstrates Efficacy of Temperature Controlled Radiofrequency for Vulvovaginal Laxity 2Health News:Study Demonstrates Efficacy of Temperature Controlled Radiofrequency for Vulvovaginal Laxity 3Health News:IDLife LLC Announces New Partnership with Fitness Celebrity, Jen Widerstrom 2
... Sunquest ... to address HIMSS 2010 attendees , ... (PRWEB) February 3, 2010 -- Sunquest , a leading provider ... significant schedules of industry expert speakers ever assembled to address HIMSS 2010 attendees. These ...
... ... the 90 million literacy challenged Americans, including special social media workshop , ... La Habra, Calif. (PRWEB) February ... a national leader in health literacy education and services, will host its 9th ...
... ... ... Medicine (NYCOM) and School of Health Professions, in partnership with the Nassau County (N.Y.) Department ... The free vaccine will be available for all members of the NYIT community and their ...
... ... and compartmentalization, liberal arts and humanities degrees are sometimes overlooked and undervalued ... well-rounded, more classical education, a liberal arts or humanities degree can be ... to general arts and the humanities. A liberal arts education opens ...
... ... re-accreditation by the American College of Radiology (ACR) , ... Berkeley Heights (Vocus) February 2, 2010 -- Summit ... Radiology (ACR) for the period of January 2010 through January 2013. Accreditation by the ...
... , WASHINGTON , Feb. 2 ... Morris , announced today that AtriCure, Inc., a medical device company ... with the Department of Justice (DOJ) and the Office of the ... $3.8 million plus interest over a five-year period. ...
Cached Medicine News:Health News:Sunquest Announces Significant Speaker Schedule for HIMSS 2010 2Health News:Sunquest Announces Significant Speaker Schedule for HIMSS 2010 3Health News:Sunquest Announces Significant Speaker Schedule for HIMSS 2010 4Health News:Institute for Healthcare Advancement's Ninth Annual Health Literacy Conference Set for May 6-7, 2010 in Irvine, Calif. 2Health News:Institute for Healthcare Advancement's Ninth Annual Health Literacy Conference Set for May 6-7, 2010 in Irvine, Calif. 3Health News:OnlineEducation.com Announces Expansion of Liberal Arts & Humanities to its Accredited Online Degree Programs 2Health News:OnlineEducation.com Announces Expansion of Liberal Arts & Humanities to its Accredited Online Degree Programs 3Health News:OnlineEducation.com Announces Expansion of Liberal Arts & Humanities to its Accredited Online Degree Programs 4Health News:Nuclear Medicine at Summit Medical Group Earns ACR Re-Accreditation 2Health News:Relator's Attorneys Comment on AtriCure/DOJ Settlement 2Health News:Relator's Attorneys Comment on AtriCure/DOJ Settlement 3
The XCHO method used on the Dimension clinical chemistry system is an in vitro diagnostic test intended for the quantitative determination of cholesterol in serum and plasma....
For the quantitative in vitro determination of alanine aminotransferase in serum or plasma....
... The Inion S-1™ Biodegradable Anteroir Cervical ... simultaneous conservative treatment with a collar), is ... cervical discectomy and fusion procedures as a ... block bone allografts or autografts., This device ...
The Tag-It™ Cystic Fibrosis ASR reagents can be used by high complexity CLIA approved laboratories for detection of up to 70 mutations and 6 variants (polymorphisms) in the cystic fibrosis tran...
Medicine Products: