PTC Therapeutics Announces Data Showing Six-Minute Walk Test Consistently Measures Ambulatory Function in Patients With Duchenne Muscular...( The study was made possible due to ...),Health

The study was made possible due to funding provided by the Parent Project Muscular Dystrophy (PPMD). In an effort to maximize the utility of the study findings, the PPMD also sponsored the development of a video demonstrating the 6MWT. The video demonstrates how to perform the test, and will ensure consistency across clinical trials and will serve as a resource for clinics using the 6MWT to follow the progress of boys with DMD/BMD.

"Identifying and promoting a clinically meaningful endpoint with proven utility has been an important goal of our organization. We are thrilled to be able to help disseminate information about the 6MWT widely, so it can be quickly and readily integrated into clinical trial protocols," said Pat Furlong, President and CEO of PPMD.

About DMD/BMD

Duchenne and Becker muscular dystrophy (DMD/BMD) are progressive muscle disorders that cause the loss of both muscle function and independence. DMD/BMD is perhaps the most prevalent of the muscular dystrophies and is the most common lethal genetic disorder diagnosed during childhood today. Each year, approximately 20,000 children worldwide are born with DMD (one of every 3,500 male children). It is estimated that one in 10 DMD patients are likely to have a Becker presentation, a milder form of the disease that is associated with later manifestation of symptoms. In essence, DMD and BMD represent a continuum of the same disease. More information regarding DMD and BMD is available through the Muscular Dystrophy Association (http://www.mdausa.org), Parent Project Muscular Dystrophy (http://www.parentprojectmd.org) and the Association Francaise contre les Myopathies (http://www.afm-france.org).

About PTC124

PTC124 is an orally delivered, investigational new drug discovered by PTC Therapeutics. The drug
'/>"/>