Navigation Links
PTC Therapeutics Announces Additional Study of Ataluren in Patients with Advanced Nonsense Mutation Duchenne/Becker Muscular Dystrophy
Date:1/19/2010

for assessing heart, lung and muscle function in patients with more advanced disease as we all continue to work to halt its progressive and debilitating effects on all affected individuals."

PTC announced in February 2009 that it has completed enrollment of a registration-directed clinical trial in patients with nonsense mutation Duchenne and Becker muscular dystrophy.  The trial is a multi-center, randomized, double-blind, placebo-controlled study to determine whether ataluren can improve walking, activity, muscle function, and strength and whether the drug can safely be given for a long period of time.  Results from this trial are expected to be available in the first half of 2010.

ABOUT DUCHENNE/ BECKER MUSCULAR DYSTROPHY

Duchenne and Becker muscular dystrophy (DBMD) are progressive, debilitating and life-threatening genetic disorders representing a single disease continuum with the same underlying cause.  Patients with DBMD do not produce adequate levels of dystrophin, an essential protein that is critical to the structural stability of skeletal and heart muscles.  DMD is the most common and most severe form of muscular dystrophy in children, and approximately 20,000 children worldwide are born with DMD annually (one of every 3,500 male children).  Patients with BMD typically experience initial symptoms later and have a slower disease progression.  Nonsense mutations cause about 10 to 15 percent of all DBMD cases which results in an estimated 1,900 boys and young men with nonsense mutation DBMD in the United States.  Further information regarding DBMD is available through the Muscular Dystrophy Association (

SOURCE PTC Therapeutics, Inc.
Copyright©2010 PR Newswire.
All rights reserved

Page: 1 2 3 4 5 6

Related medicine technology :

1. NASDAQ Trading for Oxygen Biotherapeutics, Inc. Shares to Begin January 15, 2010
2. Echo Therapeutics Announces Major Milestone: The Completion of Product Development Work of its Revolutionary, Patented Prelude(TM) SkinPrep System
3. Advanced Cardiac Therapeutics Completes $5 Million Financing
4. Cell Therapeutics, Inc. (CTI) to Present at the 28th Annual JP Morgan Healthcare Conference
5. Oxygen Biotherapeutics, Inc. Announces Approval for NASDAQ Listing
6. Anesiva Announces Merger With Arcion Therapeutics Will Not be Completed
7. Cell Therapeutics, Inc. Adopts Shareholder Rights Plan
8. Orexigen(R) Therapeutics Reports Inducement Grants Under NASDAQ Listing Rule 5635
9. PTC Therapeutics Closes $50 Million Financing
10. Fate Therapeutics iPSC Technology Awarded Top Industry Honors for Small Molecule and Protein Reprogramming Breakthroughs
11. European Medicines Agency Grants Cell Therapeutics Orphan Drug Designation for Pixantrone in Diffuse Large B-Cell Lymphoma (DLBCL)
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:5/4/2015)... 4, 2015 Henry Schein, Inc. (NASDAQ: ... products and services to office-based dental, animal health and ... quarter ended March 28, 2015. Net sales ... an increase of 1.4% compared with the first quarter ... currencies and a 6.0% decline related to foreign currency ...
(Date:5/4/2015)...  Verus Healthcare, Inc. recently completed its third year ... in 2012.  Since that original acquisition, the Company has ... (DME) industry by 1,000%.  Verus Healthcare now services approximately ... and processes nearly 14,000 new orders per month. ... the systems and processes weren,t in place to scale," ...
(Date:5/4/2015)...  NeuroSigma ® , Inc. (NeuroSigma), a California ... animal study of its Thin Film Nitinol (TFN) flow diverter ... researchers at the 53 rd Annual Meeting of the ... . A copy of the study abstract can be accessed ... at Mayo Clinic was primarily funded through a Small Business ...
Breaking Medicine Technology:Henry Schein Reports Record First Quarter Results 2Henry Schein Reports Record First Quarter Results 3Henry Schein Reports Record First Quarter Results 4Henry Schein Reports Record First Quarter Results 5Henry Schein Reports Record First Quarter Results 6Henry Schein Reports Record First Quarter Results 7Henry Schein Reports Record First Quarter Results 8Henry Schein Reports Record First Quarter Results 9Henry Schein Reports Record First Quarter Results 10Henry Schein Reports Record First Quarter Results 11Henry Schein Reports Record First Quarter Results 12Henry Schein Reports Record First Quarter Results 13Henry Schein Reports Record First Quarter Results 14Henry Schein Reports Record First Quarter Results 15Henry Schein Reports Record First Quarter Results 16Henry Schein Reports Record First Quarter Results 17Verus Healthcare Celebrates 1,000% Growth on Third Anniversary 2NeuroSigma's Thin Film Nitinol Flow Diverting Stent Results Presented at the American Society of Neuroradiology Meeting 2NeuroSigma's Thin Film Nitinol Flow Diverting Stent Results Presented at the American Society of Neuroradiology Meeting 3NeuroSigma's Thin Film Nitinol Flow Diverting Stent Results Presented at the American Society of Neuroradiology Meeting 4
... Dec. 13, 2011 /PRNewswire-Asia/ -- Bristol-Myers Squibb Company ... Pharmaceutical Group (NYSE: SCR ), a ... companies have expanded the strategic partnership formed last year ... area. The companies agreed to co-develop BMS-795311, Bristol-Myers Squibb,s ...
...  BioMed Realty Trust, Inc. (NYSE: BMR ) ... agreement to acquire Prudential Real Estate Investors, (PREI) 80% ... a 20% interest in the properties in April 2007 ... and PREI.  The Rogers Street properties are located in ...
Cached Medicine Technology:Simcere and Bristol-Myers Squibb Enter Innovative Partnership to Develop Cardiovascular Compound 2Simcere and Bristol-Myers Squibb Enter Innovative Partnership to Develop Cardiovascular Compound 3Simcere and Bristol-Myers Squibb Enter Innovative Partnership to Develop Cardiovascular Compound 4Biomed Realty Trust to Acquire Remaining 80% Interest in Rogers Street Properties in Cambridge, Massachusetts for $308 Million - Increasing Ownership to 100% 2Biomed Realty Trust to Acquire Remaining 80% Interest in Rogers Street Properties in Cambridge, Massachusetts for $308 Million - Increasing Ownership to 100% 3Biomed Realty Trust to Acquire Remaining 80% Interest in Rogers Street Properties in Cambridge, Massachusetts for $308 Million - Increasing Ownership to 100% 4
(Date:5/4/2015)... Pricing Healthcare announces it will ... patient receiving care at St. George Surgical Center ... be performed by July 15th, 2015, and the patient must ... front and forego the filing of insurance claims). , The ... year, and it devastates more and more individuals and families. ...
(Date:5/4/2015)... 2015 San Diego Fertility Center ... their brand new, 13,700 square foot facility scheduled to ... will not only provide fertility treatment and services for ... community and educational events to a number of local ... next door to their current Carmel Valley/Del Mar location ...
(Date:5/4/2015)... 04, 2015 Sheltering Arms announced that ... Hale House. The Mother Hale Learning Center meets a ... Childhood Education. Sheltering Arms will begin operating the site ... served by the center. , Opened in 2006, the ... weeks to five years, many of whom come from ...
(Date:5/4/2015)... (PRWEB) May 04, 2015 Dr. Benjamin ... Georgia proudly offers the latest non-surgical double-chin eliminator. ... facial plastic surgeon in Atlanta to offer Kybella ... to be injected specifically under the chin, promising to ... , Before Kybella, patients who sought immediate solutions for ...
(Date:5/4/2015)... New West Medicare is excited to announce ... manage outpatient advanced imaging services for its members. Care ... members are provided the right test at the right ... New West Medicare’s physicians and hospitals, Care to Care ... imaging and provide an objective basis for informed evidence-based ...
Breaking Medicine News(10 mins):Health News:Pricing Healthcare to Pay a Patient's Bill for a Procedure at Utah Facility 2Health News:Pricing Healthcare to Pay a Patient's Bill for a Procedure at Utah Facility 3Health News:San Diego Fertility Center Hosted a Ribbon Cutting Ceremony at Its New, Expanded Facility 2Health News:San Diego Fertility Center Hosted a Ribbon Cutting Ceremony at Its New, Expanded Facility 3Health News:Sheltering Arms Acquires the Mother Hale Learning Center 2Health News:Facial Plastic Surgeon First in Atlanta To Offer Kybella Treatments To Reduce Chin Fat 2Health News:New West Medicare Partners with Care to Care, LLC to Manage Advanced Imaging Services 2
... a fair distribution of bird flu vaccines, the World ... stockpile of vaccines// for developing countries. ,The global ... fight against avian influenza, WHO director general Margaret Chan ... ,Chan met President Susilo Bambang Yudhoyono Wednesday ...
... one million children under the age of five lose ... ,Considering the fact that these deaths are ... vaccine that addresses seven different strains of pneumococcal diseases ... ,Pneumococcal diseases, which affect the lungs, brain and the ...
... older population may soon be facing a medical care crisis ... rapidly//, say researchers at the University of Cincinnati. ... be more than 70 million people over the age of ... data collected over the last decade, the number of certified ...
... breast cancer who are treated with both chemotherapy ... patients who receive only tamoxifen//. But a combination ... ovaries from functioning—did not show any additional benefits, ... ,Survival rates improve for patients with ...
... Mediterranean diet could help protect children from respiratory allergies and ... and Spanish researchers assessed the diet and health of almost ... conditions are rare. ,Crete is the largest ... Mediterranean Sea. ,Researchers found those children reared on ...
... drugs during a recent influenza B epidemic in Japan ... the drugs//, according to a study. ,Two ... of drugs known as neuraminidase inhibitors, have been effective ... documented evidence of the emergence of oseltamivir-resistant type A ...
Cached Medicine News:Health News:Number of Students Taking Up Geriatric Medicine on the Decline 2Health News:Combining Therapies can Improve Survival for Early-stage Breast Cancer Patients 2Health News:Fruit and Vegetable Diet 'could Prevent Asthma' 2Health News:Study Suggests Some Drug Resistance to Influenza B Medications 2
... ARUP Laboratories is a national reference ... laboratory research and development. ARUP offers an ... unique medical tests in clinical and anatomic ... ARUP Laboratories' clients include more than half ...
... reference laboratory and a worldwide leader in ... an extensive test menu of highly complex ... anatomic pathology. Owned by the University of ... half of the nation's university teaching hospitals ...
... ARUP Laboratories is a national reference laboratory ... research and development. ARUP offers an extensive ... medical tests in clinical and anatomic pathology. ... Laboratories' clients include more than half of ...
... national reference laboratory and a worldwide leader ... offers an extensive test menu of highly ... and anatomic pathology. Owned by the University ... than half of the nation's university teaching ...
Medicine Products: