Navigation Links
PTC Therapeutics Announces Additional Results from Phase 2 Study of PTC124 in Duchenne Muscular Dystrophy
Date:10/18/2007

at PTC124 is potentially applicable to a broad range of other genetic disorders in which a nonsense mutation is the cause of the disease. The FDA has granted PTC124 Fast-Track designations and Orphan Drug designations for the treatment of CF and DMD due to nonsense mutations. PTC124 has also been granted orphan drug status for the treatment of CF and DMD by the European Commission. PTC124's development is supported by grants from the Muscular Dystrophy Association (MDA), Cystic Fibrosis Foundation Therapeutics, Inc. (CFFT), Parent Project Muscular Dystrophy (PPMD), FDA's Office of Orphan Products Development (OOPD) and by General Clinical Research Center grants from the National Center for Research Resources (NCRR).

About PTC Therapeutics, Inc.

PTC is a biopharmaceutical company focused on the discovery, development and commercialization of orally administered, proprietary, small-molecule drugs that target post-transcriptional control processes. Post- transcriptional control processes regulate the rate and timing of protein production and are of central importance to proper cellular function. PTC's internally-discovered pipeline addresses multiple therapeutic areas, including genetic disorders, oncology and infectious diseases. In addition, PTC has developed proprietary technologies and extensive knowledge of post- transcriptional control processes that it applies in its drug discovery and development activities, including the Gene Expression Modulation by Small- molecules (GEMS) technology platform, which has been the basis for collaborations with leading pharmaceutical and biotechnology companies such as Pfizer, Celgene, CV Therapeutics and Schering-Plough.


'/>"/>
SOURCE PTC Therapeutics, Inc.
Copyright©2007 PR Newswire.
All rights reserved

Page: 1 2 3 4

Related medicine technology :

1. Cell Therapeutics, Inc. Management to Discuss Todays Announcement of Interim Pixantrone Study Results
2. Halozyme Therapeutics Enhanze Technology Large Protein Molecule Therapeutic Clinical Trial Results Presented at the 34th Annual Meeting of the Controlled Release Society
3. CV Therapeutics Identifies Potential Anti-Diabetic Mechanism of Action for Ranexa
4. GTC Biotherapeutics to Webcast Corporate Presentation at the C.E. Unterberg, Towbin Emerging Growth Life Opportunities Conference
5. Fat Kills Cancer: Turning Stem Cells from Fat Tissue into Personalized, Cancer-Targeted Therapeutics
6. A 4-Week Therapy with Transition Therapeutics E1-I.N.T. Leads to Sustained Reductions in Blood Glucose Levels for 6 Months Post-treatment in Type 2 Diabetes Patients
7. Clinical Trial Suggests Bone Marrow Stem Cells Are Useful for Spinal Cord Injury; PrimeCell Therapeutics Provided Pre-Clinical Study
8. Pieris Progresses Development of its Proprietary Biotherapeutics Platform: Successful Demonstration of Dual Targeting With Duocalin(R) Technology
9. Opexa Therapeutics Reports Positive Top-line Data in Phase I/II Extension Trial with Tovaxin for Multiple Sclerosis
10. Orexigen Therapeutics to Present Data on Contrave Impact on Visceral Fat and Insulin Resistance at American Diabetes Association 67th Scientific Sessions in Chicago June 23
11. Allos Therapeutics Reports Results for Phase 3 Enrich Study of Efaproxyn in Women With Brain Metastases Originating From Breast Cancer
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:11/22/2014)... Statistics released from a number of organizations ... during the holidays, beginning with Thanksgiving eve, which is ... The data, highlighted in an Infographic ... of their annual Sober Days for the Holidays ... drinking and increased rates of DUI injuries and deaths ...
(Date:11/22/2014)... HILL, N.C. , Nov. 21, 2014 /PRNewswire/ ... healthcare system. Undoubtedly, the growing influence of patients ... spend for marketing interactions. Now, more than ever, ... retain patients for medical products is essential. ... firm, Best Practices, LLC, benchmarked companies spent about ...
(Date:11/21/2014)...  Tandem Diabetes Care ® , Inc. (NASDAQ: ... and manufacturer of the t:slim ® Insulin ... non-profit dedicated to improving diabetes therapy management by ... diabetes data accessibility. This partnership will enable users ... development, to download and access data from their ...
Breaking Medicine Technology:Alarming Stats Show Holiday Drinking an Issue for Many 2New Report Details Importance of Adopting a "Patient Journey" Framework in Marketing 2Tandem Diabetes Care Announces Partnership with Tidepool to Further Expand Access to Diabetes Device Data 2Tandem Diabetes Care Announces Partnership with Tidepool to Further Expand Access to Diabetes Device Data 3
... Ganey Associates, Inc. today announced a broad partnership with ... help measure and improve satisfaction and engagement among patients, ... on October 1, 2009. , HMA owns and operates ... licensed beds, in non-urban communities located throughout the United ...
... CHICAGO and PALO ALTO, Calif., Oct. 14 ... first of its PRECISE Clinical Studies (Pulsed Plasma ... Surgical HEaling) demonstrating that its PEAK PlasmaBlade® tissue ... post-operative wound drainage, narcotic consumption, thermal injury, wound ...
Cached Medicine Technology:Press Ganey Partners With Health Management Associates 2PEAK Surgical Announces Results of First PRECISE Studies at American College of Surgeons' Clinical Congress 2PEAK Surgical Announces Results of First PRECISE Studies at American College of Surgeons' Clinical Congress 3
(Date:11/24/2014)... (PRWEB) November 24, 2014 "My friend ... was trying to cross the street in his motorized ... never saw him. I came up with this idea ... at night." , He developed the Safety Lites to ... in low-lighting conditions. The device ensures that motorists can ...
(Date:11/23/2014)... iFitDress.com, a well-known wedding dress manufacturer, has unveiled ... They are now offered at deeply discounted prices, up ... now to Dec. 15. The main purpose of the promotion ... high quality items are ideal options for ladies who are ... money. All its new mint cocktail dresses are very beautiful; ...
(Date:11/23/2014)... The report, “Market Snapshot: Aesthetic Lasers ... Asia-Pacific” provides quantitative analysis of the three aesthetic ... body contouring devices, non-invasive body contouring devices and ... data by revenue and volume over the 2006 ... South Korea, Australia and India. It uses data ...
(Date:11/23/2014)... Pro Ace Care, a renowned Vancouver hot water tank ... an 8 year warranty on its selected hot water tanks. ... due to the impending winter season, it was important for ... service that the company provides. As a result, Pro Ace ... and Bradford hot water tanks. , “Every installer who ...
(Date:11/23/2014)... (HealthDay News) -- Close friends have more influence on ... a new study says. "We,ve known for ... influence on individual alcohol use, but there are no ... and the friend group,s influence on those decisions," Jonathon ... Public Health, said in a university news release. ...
Breaking Medicine News(10 mins):Health News:Trendy Long Black Evening Gowns Now Provided By iFitDress.com 2Health News:Aesthetic Lasers and Energy Devices Market in APAC (China, Japan, South Korea, Australia and India) to 2020 2Health News:Aesthetic Lasers and Energy Devices Market in APAC (China, Japan, South Korea, Australia and India) to 2020 3Health News:Aesthetic Lasers and Energy Devices Market in APAC (China, Japan, South Korea, Australia and India) to 2020 4Health News:Pro Ace Care Now Gives 8 Year Guarantee on Selected Vancouver Hot Water Tanks 2Health News:Close Friends May Be Key to Teens' Drinking 2
... Research (ISSCR) commends the recent launch of a ... and designed to share advances in stem cell ... of interest concerning stem cell research in Michigan: ... Michigan,s Proposal 2, a state initiative to accelerate ...
... 2008) -- Weill Cornell Medical College announced today that ... from the Bill & Melinda Gates Foundation. The grants ... of the Fusion Mechanism Used by Viruses for Entry: ... Dr. Anne Moscona, and "Senescent and Rejuvenated Mtb Subsets ...
... efficient use of procedures, WASHINGTON, Oct. 30 ... voluntary consensus standards to,encourage the appropriate and efficient ... of standards helps -- via measurement and,public reporting ... with,outpatient imaging while improving care for patients and ...
... FRANCISCO, Oct. 30 nCircle today announced it ... how to comply with,HIPAA security requirements and leverage ... a time of unprecedented risk and recent,government enforcements ... is now more than ever a top priority ...
... SAN DIEGO, Oct. 30 One errant cough or ... of illness and,resulting absenteeism. As the flu season approaches, ... productivity. The World Health,Organization estimates that the cost of ... costs and lost productivity can range from $71 billion,to ...
... Inc. (NYSE: MYL ),today announced that in accordance ... declared its quarterly dividend of $16.25 per,share (based on ... of $1,000.00 per share) payable on Nov. 17, 2008, ... 31, 2008., Mylan Inc., which provides products to ...
Cached Medicine News:Health News:International Society for Stem Cell Research Highlights New YouTube Channel Providing Accurate Scientific Perspectives on Stem Cell Research 2Health News:Weill Cornell Medical College receives 2 $100,000 grants for innovative global health research 2Health News:NQF Endorses Consensus Standards to Reduce Waste and Promote Safe and Effective Use of Imaging Procedures 2Health News:NQF Endorses Consensus Standards to Reduce Waste and Promote Safe and Effective Use of Imaging Procedures 3Health News:nCircle Announces Free Web Seminar - 'Automating HIPAA Compliance with Security & Configuration Auditing' 2Health News:Going 'Green' May Mean Fewer Colds This Season 2Health News:Going 'Green' May Mean Fewer Colds This Season 3
... PDCs computer-generated Thermal Printing Wristbands and ... direct thermal and thermal transfer printers. ... activate a heat-sensitive thermal coating under ... printers use heat to transfer highly ...
... Wristbands and Tags print in mere ... transfer printers. Direct thermal printers use ... coating under the bands protective surface. ... transfer highly durable ink from a ...
... coded patient identification bracelets (wristbands) and/or ... at patient care areas throughout the ... identification and in creating a positive ... back to the patient through the ...
... secure band is desired for adults and where an ... appropriate. The design allows for two bands to be ... on the wrist and the second to be held ... This is particularly useful in a hospital situation wherea ...
Medicine Products: