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Orphan Drugs for Cancer: R&D and Market 2013-2023

NEW YORK, Sept. 2, 2013 /PRNewswire/ -- announces that a new market research report is available in its catalogue:

Orphan Drugs for Cancer: R&D and Market 2013-2023

Report Details

Orphan cancer drugs - new study shows you trends, R&D, and sales forecasts

What's the future of orphan medicines to treat cancers? Visiongain's new report gives you revenue predictions from 2013. There you explore results, R&D, opportunities, and potential sales.

Orphan drugs can be profitable. In our analysis you see forecasted sales to 2023 at overall world market, submarket, product, and national level. You see the potential of treatments for rare cancers. Try our report now, helping you stay ahead.

Trends and revenue potentials of that rising pharma segment

Many opportunities remain for orphan medicines in cancer care. In our new study you assess treatments and their potential returns. You also investigate what affects their sales.

Read on, then, to explore that industry and see what its future market could be worth.

Forecasts 2013-2023 and other analyses - find commercial opportunities

Besides revenue forecasting to 2023, our new work shows historical data, growth rates, and market shares. There you discover original analysis, seeing business outlooks and developments. You also get 64 tables, 52 charts, and two interviews with companies.

It can be hard to find data on rare diseases - all that searching. But now you can stay ahead in knowledge for applied oncology, benefiting your research, analyses, and decisions.

Finding information you need on rare cancer indications just got easier. You save time too. In our study you hear what's going on, also seeing where needs and money lie.

Avoid falling behind then. The following sections show what you get in our new investigation.

Prospects from 2013 for the world market and submarkets

Our new report shows revenue to 2023 for the overall world market. It also shows you individual revenue forecasts to 2023 for five orphan cancer submarkets:• Leukaemia• Multiple myeloma• Lymphoma• Glioma• Other disorders.

How will those segments develop? See which parts can generate most money. Explore biologicals (biologics) - esp. monoclonal antibodies (mAbs) - and small-molecule drugs. There you identify potential for treating tumours (tumors) and other forms of rare cancer.

What's the secret of making money there? Our study gives you a feel, then, for what stimulates and restrains that industry and market. See what's possible and likely.

Find sales predictions by product, too, hearing how they can succeed.

Forecasts from 2013 for orphan anticancer brands

How will orphan cancer drugs perform to 2023 at world level? Our report forecasts revenues of 12 leading drugs and six recently-approved products, including these brands:

• Rituxan

• Glivec

• Revlimid

• Velcade

• Cometriq

• Stivarga.

There you discover how high sales can go, 2013 to 2023, finding drugs and years with highest predicted growth and revenues. Also you examine competition. You see what's happening, then, understanding challenges, trends, competitors, and opportunities.

Our study also divides its overall world forecast into those for geographical regions.

National markets - what demand for orphan anticancer agents?

From 2013 to 2023 the US, the EU, and Japan offer the greatest opportunity for companies developing and producing therapies for rare cancer indications.

Our analyses show you individual revenue forecasts to 2023 for 11 national markets:• US• Japan• Germany, France, UK, Italy, and Spain (EU5), also with EU regional prediction• Brazil, Russia, India, and China (BRIC).

There you find countries with highest revenues and potential sales growth. Our work explains. You explore prospects for treating unusual and under-treated cancers. See effects of existing and future treatments.

Research and development - you assess trends, possibilities, and innovations

What about R&D - pipelines for new drugs? You assess trends and technologies there, especially in these applications:

• Leukaemia

• Myelodysplastic syndromes (MDS)

• Lymphoma

• Multiple myeloma

• Glioma.

In 2013 more than 30 agents hold orphan drug status as candidates for treating haematological cancers. Technology for tumours also holds promise. More than 100 orphan anticancer agents exist in mid-to-late stage clinical development, our study finds.

You hear, then, about innovations in oncological R&D. Many molecular pathways and targets exist. Discover progress and find what it means. Our study explains, discussing issues to help your work.

Forces affecting developers, producers, and sellers

Our report shows you issues and events affecting the orphan cancer medicines industry and market from 2013, including these:

• Regulations - regional and national

• Antibodies, toxin fragments, and other novel immunotherapies

• Potential of tyrosine kinase inhibitors

• Therapeutic vaccines

• Expansions of indications.

The study discusses other aspects of the technology too, including these:• Costs of therapy and issues for regulators, governments, and other payers• Biosimilars and generics as competition for original drugs• Challenges and opportunities in patient recruitment• Companion diagnostics and personalised therapies.

There you explore political, economic, social, and technological questions, assessing outlooks for business. Also you gain regulatory insights. See, then, what restrains and what helps that pharma segment. Discover what its present and future hold.

Companies and 2017 market value - what happens next?

From 2013, new treatments hold great potential for investments, medical advances and revenues. Our analysis predicts the world market for orphan cancer drugs will reach $50.3bn in 2017, with high growth from 2013 to 2023.

See what's possible there - the expected gains. Our report shows what technologies and players hold greatest potential. You explore activities of these companies and many others:• Novartis• Celgene• Onyx Pharmaceuticals• Bristol-Myers Squibb• Johnson & Johnson• Merck & Co.

You find 140 organisations covered. You also read two interviews with leaders in the industry. Discover what companies think, say, and do, helping you stay ahead.

Information found nowhere else

In particular, then, our investigation gives you these advantages:

• Revenues to 2023 for orphan cancer drugs at world level, with forecasting of 5 submarkets and 18 products - assess potentials for investments and sales

• Forecasts to 2023 for 11 national markets in the Americas, Europe, and Asia - investigate countries for revenues and expected growth

• Prospects for established competitors and new entrants - explore activities, results, R&D, and outlooks for future success.

Orphan Drugs for Cancer: R&D and Market 2013-2023

gives independent analysis. There you receive business intelligence found only in our work, finding where money lies.

With that report you are less likely to fall behind in knowledge or miss sales opportunity. See there how you could benefit your research, analysis, and decisions. Explore progress and possibilities. Also find how you can save time and get recognition for insight.

Orphan anticancer drugs - assess potentials now, seeing what you can gain

Our new report is for everyone analysing biopharma and orphan diseases. Find sales predications with discussions. Avoid missing out then - please order the report now.

Visiongain is a trading partner with the US Federal GovernmentCCR Ref number: KD4R6

Table of Contents 1. Executive Summary

1.1 Orphan Drugs for Cancer: Market Overview 2013

1.2 Report Contents

1.3 Research and Analysis Methods

2. Introduction to Orphan Drugs in Cancer

2.1 Defining Orphan Diseases2.2 What Are the Major Orphan Cancer Indications?2.2.1 Leukaemia: The Most Common Blood Cancer2.2.2 Lymphoma2.2.3 Multiple Myeloma2.2.4 Other Orphan Cancer Indications2.3 Orphan Drug Designation2.3.1 What Benefits Come with Orphan Drug Designation?2.4 Demand for Orphan Drugs2.4.1 Development of Orphan Drugs

3. The World Orphan Cancer Drugs Market 2013-2023

3.1 How Large is the Orphan Drugs Market in 2013?

3.1.1 Cancer is the Largest Sector of the Orphan Drugs Market

3.2 The Orphan Cancer Drugs Market 2013-2023

3.2.1 What Will Drive Growth in the Market to 2023?

3.2.2 Market Restraints 2013-2023

3.3 Orphan Drugs in Leukaemia: Submarket 2013-2023

3.3.1 Leukaemia: Submarket Forecast 2013-2023

3.3.2 Next Generation Tyrosine Kinase Inhibitors to Drive Growth

3.4 Orphan Drugs in Lymphoma: Submarket 2013-2023

3.4.1 Lymphoma: Submarket Forecast 2013-2023

3.4.2 Monoclonal Antibody Therapies Will Dominate the Submarket 2013-2023

3.5 Orphan Drugs in Multiple Myeloma: Submarket 2013-2023

3.5.1 Multiple Myeloma: Submarket Forecast 2013-2023

3.5.2 There Are Many New Therapies in Development

3.6 Orphan Drugs in Glioma: Submarket 2013-2023

3.6.1 Glioma: Submarket Forecast 2013-2023

3.6.2 Therapeutic Vaccines Will Provide a Novel Treatment Strategy 2016-2023

4. Leading and Emerging National Markets for Rare Cancer Indications 2013-2023

4.1 Leading National Markets 20134.1.1 National Market Forecasts 2013-20234.2 The US: The Leading Market for Orphan Cancer Drugs 2013-20234.2.1 Orphan Drug Regulations in the US4.2.2 Benefits for Orphan Drug Developers4.2.3 US Orphan Cancer Drugs Market Forecast 2013-20234.3 Orphan Drugs in the EU 2013-20234.3.1 The Incentives for Orphan Drug Development in the EU4.3.2 The EU Orphan Cancer Drugs Market Forecast 2013-20234.3.3 Orphan Cancer Drugs in the EU5 Submarkets 2013-20234.4 The Japanese Orphan Cancer Drugs Market 2013-20234.4.1 Orphan Drug Regulations and Benefits4.4.2 Japanese Orphan Cancer Drugs Submarket Forecast 2013-20234.5 The Potential for Orphan Cancer Drugs in Emerging Markets 2013-20234.5.1 Brazil4.5.2 Russia: Attempts to Introduce Orphan Designation and Incentives 2010-20134.5.3 India: Generics Will Limit Branded Rare Cancer Drug Uptake4.5.4 China

5. Outlook for Leading Orphan Drugs 2013-2023

5.1 Rituxan (Roche/Biogen Idec) Is the Bestselling Orphan Cancer Drug

5.1.1 Roche is Developing a Next Generation Rituxan

5.1.2 Rituxan: Revenue Forecast 2013-2023

5.2 Glivec (Novartis): A Leukaemia Market Leader

5.2.1 The Challenge of Tasigna and Generics

5.2.2 Glivec: Revenue Forecast 2013-2023

5.3 Revlimid (Celgene) Is the Leading Therapy for Multiple Myeloma

5.3.1 Celgene Is Adding New Indications for Revlimid

5.3.2 Revlimid: Revenue Forecast 2013-2023

5.4 Alimta (Eli Lilly)

5.4.1 Revenue Growth Driven by Uptake in NSCLC 2008-2012

5.4.2 Alimta: Revenue Forecast 2013-2023

5.5 Velcade (J&J/Takeda)

5.5.1 Strong Revenue Growth in Markets Worldwide 2008-2012

5.5.2 Velcade Faces Significant Competition in Multiple Myeloma 2013-2023

5.6 Nexavar (Bayer/Onyx Pharmaceuticals)

5.6.1 Nexavar Has Shown Promise in Thyroid Cancer

5.6.2 Nexavar: Revenue Forecast 2013-2023

5.7 Tasigna (Novartis)

5.7.1 Tasigna Is More Effective than Glivec and Sprycel

5.7.2 Will Tasigna Replace Glivec 2013-2023?

5.8 Temodar (Merck & Co.)

5.8.1 Temodar Competes with Generics in the EU

5.8.2 Temodar: Continued Revenue Decline 2013-2023

5.9 Vidaza (Celgene/Nippon Shinyaku)

5.9.1 Vidaza: Revenue Growth 2008-2012

5.9.2 Celgene Is Developing an Oral Azacitidine Formulation

5.9.3 Vidaza Revenue Forecast 2013-2023: When Will Generic Competition Arrive?

5.10 Sprycel (Bristol-Myers Squibb/Otsuka Pharmaceutical)

5.10.1 Sprycel: Financial Performance 2008-2012

5.10.2 Sprycel: Revenue Forecast 2013-2023

5.11 Afinitor (Novartis)

5.11.1 Approval in Breast Cancer Drives Revenue Growth 2012

5.11.2 Afinitor: Revenue Forecast

5.12 Yervoy

5.12.1 Yervoy May Be Effective as a Combination Therapy

5.12.2 Yervoy: Revenue Forecast 2013-2023

5.13 Outlook for Orphan Cancer Drugs Approved in 2012 and 2013

5.13.1 New Therapies for Multiple Myeloma Pomalyst: A Next Generation Thalidomide Derivative Kyprolis (Onyx Pharmaceuticals) Pomalyst versus Kyprolis Pomalyst and Kyprolis: Revenue Forecast 2013-2023

5.13.2 Three New Drugs Approved for CML in 2012 Bosulif (Pfizer): A TKI Targeting New Mutations Iclusig (ARIAD Pharmaceuticals) Bosulif and Iclusig: Revenue Forecast 2013-2023 Synribo (Teva)

5.13.3 Commercial Prospects for Marqibo (Talon Therapeutics)

5.13.4 Cometriq (Exelixis) Cometriq: Revenue Forecast 2013-2023

5.13.5 Stivarga (Bayer/Onyx Pharmaceuticals): Opportunities in Stomach and Liver Cancer Stivarga: Revenue Forecast 2013-2023

5.14 Other Leading Cancer Therapies Approved for Orphan Indications 2012

5.14.1 Avastin (Roche) Avastin Shows Promise in Glioblastoma

5.14.2 Erbitux (Bristol-Myers Squibb/Eli Lilly/Merck Serono) Attempts to Expand Approved Indications

5.14.3 Herceptin (Roche)

6. Orphan Cancer Drugs: R&D Pipeline 2013

6.1 Orphan Drugs in the Leukaemia Pipeline 20136.1.1 Obinutuzumab (Roche)6.1.2 Dacogen: Eisai Seeks Approval for AML in the US6.1.3 CPX-351 (Celator Pharmaceuticals)6.1.4 Dinaciclib (Merck & Co.)6.1.5 EZN-2285 (Sigma-Tau Pharmaceuticals): Reformulation for Improved Dosing6.1.6 Ibrutinib (J&J/Pharmacyclics): Awarded Breakthrough Status in Multiple Indications6.1.7 Midostaurin (Novartis): Targeting the FLT3 Gene6.1.8 Moxetumomab Pasudotox (MedImmune): Combining Antibodies and Toxin Fragments6.1.9 Vosaroxin (Sunesis Pharmaceuticals)6.1.10 Alvocidib (Tolero Pharmaceuticals)6.1.11 Blinatumomab (Amgen): Complete Response in Two Thirds of Patients6.1.12 CNDO-109 (Coronado Biosciences)6.1.13 Tosedostat (Chroma Therapeutics/Cell Therapeutics)6.1.14 TRU-016 (Emergent BioSolutions)6.1.15 Veltuzumab (Immunomedics)6.2 Orphan Drugs in the MDS Pipeline 20136.2.1 Rigosertib (Onconova Therapeutics/Baxter)6.2.2 Sapacitabine (Cyclacel Pharmaceuticals)6.2.3 StemEx (Gamida Cell): A Regenerative Medicine Approach to Treating Cancer6.2.4 Pacritinib (Cell Therapeutics): Approval Possible in 20166.2.5 Telintra (Telik)6.3 Orphan Drugs in the Lymphoma Pipeline 20136.3.1 Mechlorethamine Gel (Ceptaris Therapeutics): Fast and Accurate Dosing for Patients6.3.2 BiovaxID (BioVest International): A Therapeutic Vaccine for Follicular Lymphoma6.3.3 Belinostat (Topotarget/Spectrum Pharmaceuticals)6.3.4 Epratuzumab (Immunomedics)6.3.5 Faridak (Novartis): Approval in Myeloma in 2014?6.3.6 Mogamulizumab (Kyowa Hakko Kirin/Amgen)6.3.7 Darinaparsin (ZIOPHARM Oncology)6.3.8 Mocetinostat: MethylGene Is Seeking a Development Partner6.3.9 Resminostat (4SC)6.4 Orphan Drugs in the Multiple Myeloma Pipeline 20136.4.1 Aplidin (PharmaMar)6.4.2 Elotuzumab (AbbVie/Bristol-Myers Squibb)6.4.3 Ixazomib (Millennium Pharmaceuticals): An Oral Proteasome Inhibitor to Replace Velcade?6.4.4 Captisol-Enabled Melphalan (Spectrum Pharmaceuticals)6.4.5 Siltuximab (J&J)6.5 Orphan Glioma Pipeline: Led by Novel Immunotherapies6.5.1 Rindopepimut (Celldex Therapeutics)6.5.2 DCVax-L (Northwest Biotherapeutics)6.5.3 ICT-107 (ImmunoCellular Therapeutics)6.5.4 Trans-Sodium Crocetinate (TSC, Diffusion Pharmaceuticals): Phase II Results Expected in 20146.5.5 Cotara (Peregrine Pharmaceuticals): Over a Decade in Clinical Development6.5.6 VAL-083 (Del Mar Pharmaceuticals): Avoiding MGMT Resistance Pathways

7. Orphan Drugs in Cancer: Industry Trends 2013-2023

7.1 Orphan Drugs in Cancer: Strengths and Weaknesses 2013

7.2 Orphan Drugs in Cancer: Opportunities and Threats 2013-2023

7.3 Orphan Drugs in Cancer: STEP Analysis 2013-2023

7.3.1 Social Factors Ethical Considerations for Orphan Drug Development

7.3.2 Technological Developments Increased Understanding of Disease Will Drive Innovation

7.3.3 Economic Pressures Influencing Orphan Drug Uptake Orphan Drugs Tend to be Expensive

7.3.4 Political Issues: The Role of Government and Regulatory Bodies in the Market Harmonising Global Regulatory Pathways

7.4 Trends in Orphan Cancer Drug Development

7.4.1 Clinical Trials for Orphan Drugs Are Adverse Events More Acceptable for Orphan Drugs? Challenges and Opportunities in Patient Recruitment

7.4.2 Biomarkers for Orphan Cancer Indications Companion Diagnostics

7.4.3 The Role of Public Funding in Orphan Drug Development

7.5 Commercialising Orphan Drugs in Cancer

7.5.1 Pricing of Orphan Drugs May Become Crucial to Success

7.5.2 Market and Patient Access Are Crucial for Orphan Drug Success

7.5.3 Repositioning Drugs for Orphan Cancer Indications Expanding Beyond Orphan Indications

7.5.4 Big Pharma and Orphan Cancer Drugs Orphan Drugs Fit the Personalised Medicine Model

7.5.5 Common Market Entry Strategies

7.5.6 Orphan Indications as an Opportunity for Generic Drug Manufacturers

8. Research Interviews

8.1 Jeffrey Bacha, President and CEO, Del Mar Pharmaceuticals8.1.1 Del Mar Pharmaceuticals8.1.2 Applying for Orphan Drug Status8.1.3 The Benefits of Orphan Drug Designation8.1.4 Clinical Trials for Orphan Drugs8.1.5 Market Access in Glioblastoma8.1.6 VAL-083 and the Future Glioblastoma Market8.1.7 Immunotherapies for Glioblastoma8.1.8 Development of VAL-0838.1.9 Future Development of VAL-0838.2 David Kalergis, CEO, Diffusion Pharmaceuticals8.2.1 Diffusion Pharmaceuticals and TSC8.2.2 Seeking Orphan Drug Status8.2.3 Challenges in Orphan Drug Development8.2.4 TSC and the Glioblastoma Market

9. Conclusions from Our Study

9.1 The State of the Orphan Cancer Drugs Market 2012-2013

9.2 There Will Be Strong Growth in the Market 2013-2023

9.3 The US is the Largest National Market 2013-2023

9.4 There Are Long Pipelines in Many Disease Sectors in 2013

List of Tables

Table 1.1 Currency Exchange Rates

Table 1.2 Common Abbreviations Used in this Report

Table 2.1 EU Prevalence Statistics for Selected Rare Cancer Indications, 2013

Table 3.1 Global Orphan Cancer Drugs Market: Revenue ($bn) and Market Share (%) by Sector, 2012

Table 3.2 Global Orphan Cancer Drugs Market: Overall Market and Revenue Forecasts by Sector ($bn), 2012-2023

Table 3.3 Global Orphan Cancer Drug Market: Submarket Shares (%), 2012-2023

Table 3.4 Patent Expiries for Selected Orphan Cancer Drugs in the US and EU, 2009-2024

Table 3.5 Leukaemia Submarket Forecast ($bn), 2012-2023

Table 3.6 Lymphoma Submarket Forecast ($bn), 2012-2023

Table 3.7 Multiple Myeloma Submarket Forecast ($bn), 2012-2023

Table 3.8 Glioma Submarket Forecast ($bn), 2012-2023

Table 4.1 Orphan Cancer Drugs Market: Revenue ($bn) and Market Share (%) by Region, 2012

Table 4.2 Orphan Cancer Drugs Market: Regional Submarket Forecasts ($bn), 2012-2023

Table 4.3 Global Orphan Cancer Drug Market: Regional Submarket Shares (%), 2012-2023

Table 4.4 US Orphan Cancer Drugs: Submarket Forecast ($bn), 2012-2023

Table 4.5 Fee Reductions (%) Available for SMEs Developing Orphan Drugs in the EU, 2013

Table 4.6 EU5 Orphan Cancer Drugs Market: Revenue ($bn) and Market Share (%) by Country, 2012

Table 4.7 EU5 Orphan Cancer Drugs Market: National Submarket Forecasts ($bn), 2012-2023

Table 4.8 Japanese Orphan Cancer Drugs: Submarket Forecast ($bn), 2012-2023

Table 4.9 BRIC Orphan Cancer Drugs Market: National Submarket Forecasts ($bn), 2012-2023

Table 5.1 Top Orphan Cancer Drugs: Revenues ($bn) and Leading Revenue Shares (%), 2012

Table 5.2 Orphan Drug Designations in the US for Rituxan, 2013

Table 5.3 Rituxan: Revenue ($bn), 2008-2012

Table 5.4 Biosimilar Rituximab: Selected Pipeline, 2013

Table 5.5 Rituxan: Revenue Forecast ($bn), 2012-2023

Table 5.6 Orphan Drug Designations in the US for Glivec, 2013

Table 5.7 Glivec: Revenue ($bn), 2008-2012

Table 5.8 Glivec: Revenue Forecast ($bn), 2012-2023

Table 5.9 Revlimid: Revenue ($bn), 2006-2012

Table 5.10 Revlimid: Revenue Forecast ($bn), 2012-2023

Table 5.11 Alimta: Revenue ($bn), 2008-2012

Table 5.12 Alimta: Revenue Forecast ($bn), 2012-2023

Table 5.13 Velcade: Revenue by Company ($bn), 2008-2012

Table 5.14 Velcade: Revenue Forecast ($bn), 2012-2023

Table 5.15 Nexavar: Revenue ($bn), 2008-2012

Table 5.16 Nexavar: Revenue Forecast ($bn), 2012-2023

Table 5.17 Tasigna: Revenue ($bn), 2008-2012

Table 5.18 Tasigna: Revenue Forecast ($bn), 2012-2023

Table 5.19 Temodar: Revenue ($bn), 2010-2012

Table 5.20 Temodar: Revenue Forecast ($bn), 2012-2023

Table 5.21 Vidaza: Revenue by Company ($bn), 2008-2012

Table 5.22 Vidaza: Revenue Forecast ($bn), 2012-2023

Table 5.23 Sprycel: Revenue by Company ($bn), 2008-2012

Table 5.24 Sprycel: Revenue Forecast ($bn), 2012-2023

Table 5.25 Orphan Drug Designations in the US for Afinitor, 2013

Table 5.26 Afinitor: Revenue ($bn), 2009-2012

Table 5.27 Afinitor: Revenue Forecast ($bn), 2012-2023

Table 5.28 Yervoy: Revenue ($bn) 2011-2012

Table 5.29 Yervoy: Revenue Forecast ($bn), 2012-2023

Table 5.30 Kyprolis and Pomalyst: Revenue Forecasts ($bn), 2012-2023

Table 5.31 Bosulif and Iclusig: Revenue Forecasts ($bn), 2012-2023

Table 5.32 Cometriq: Revenue Forecast ($bn), 2012-2023

Table 5.33 Stivarga: Revenue Forecast ($bn), 2012-2023

Table 6.1 Selected Phase II and III Pipeline Orphan Candidates in Development for Leukaemia, 2013

Table 6.2 Ongoing Phase III Trials for Ibrutinib, 2013

Table 6.3 Ongoing Clinical Trials for Midostaurin, 2013

Table 6.4 Selected Phase II and III Pipeline Orphan Candidates in Development for MDS, 2013

Table 6.5 Phase II and III Pipeline Orphan Candidates in Development for Lymphoma, 2013

Table 6.6 Ongoing Phase II and III Trials for Mogamulizumab, 2013

Table 6.7 Selected Phase II and III Pipeline Orphan Candidates in Development for Multiple Myeloma, 2013

Table 6.8 Selected Phase II and III Pipeline Orphan Candidates in Development for Glioma, 2013

Table 7.1 Global Orphan Cancer Drugs Market: Strengths and Weaknesses, 2012-2013

Table 7.2 Global Orphan Cancer Drugs Market: Opportunities and Threats, 2013-2023

Table 7.3 Monthly and Annual Prices ($) in the US for Selected Orphan Cancer Drugs Approved 2011-2013

Table 9.1 Global Orphan Cancer Drugs Market: Revenue ($bn), and Market Share (%) by Sector, 2012, 2017 & 2023

Table 9.2 Global Orphan Cancer Drugs Market: Revenue ($bn), Market Share (%) by Region, 2012, 2017 & 2023

List of Figures

Figure 2.1 Orphan Disease Definitions by Country/Region, 2013

Figure 2.2 Orphan Drug Designation Benefits in Major Markets, 2013

Figure 3.1 Orphan Drug Approvals in the US, 2000-2013

Figure 3.2 Global Orphan Cancer Drugs Market: Market Share (%) by Sector, 2012

Figure 3.3 Global Orphan Cancer Drugs Market Forecast ($bn), 2012-2023

Figure 3.4 Global Orphan Cancer Drugs Market: Submarket Shares (%), 2017

Figure 3.5 Global Orphan Cancer Drugs Market: Submarket Shares (%), 2023

Figure 3.6 Global Orphan Cancer Drugs Market: Drivers and Restraints, 2013-2023

Figure 3.7 Leukaemia Submarket Forecast ($bn), 2012-2023

Figure 3.8 Lymphoma Submarket Forecast ($bn), 2012-2023

Figure 3.9 Multiple Myeloma Submarket Forecast ($bn), 2012-2023

Figure 3.10 Glioma Submarket Forecast ($bn), 2012-2023

Figure 4.1 Orphan Cancer Drug Market: Market Share (%) by Region, 2012

Figure 4.2 Orphan Cancer Drug Market: Market Share (%) by Region, 2017

Figure 4.3 Orphan Cancer Drug Market: Market Share (%) by Region, 2023

Figure 4.4 US Orphan Cancer Drugs: Submarket Forecast ($bn), 2012-2023

Figure 4.5 EU Orphan Cancer Drugs Market: Market Share (%) by Country, 2012

Figure 4.6 EU Orphan Cancer Drugs: Submarket Forecast ($bn), 2012-2023

Figure 4.7 EU5 Orphan Cancer Drugs National Market Forecasts ($bn), 2012-2023

Figure 4.8 Japanese Orphan Cancer Drugs: Submarket Forecast ($bn), 2012-2023

Figure 4.9 BRIC National Orphan Cancer Drug Submarket Forecasts ($bn), 2012-2023

Figure 5.1 Top Orphan Cancer Drugs: Revenue Shares (%), 2012

Figure 5.2 Rituxan: Revenue ($bn), 2008-2012

Figure 5.3 Rituxan: Revenue Forecast ($bn), 2012-2023

Figure 5.4 Glivec: Revenue ($bn), 2008-2012

Figure 5.5 Glivec: Revenue Forecast ($bn), 2012-2023

Figure 5.6 Revlimid: Revenue ($bn), 2006-2012

Figure 5.7 Revlimid: Revenue Forecast ($bn), 2012-2023

Figure 5.8 Alimta: Revenue ($bn), 2008-2012

Figure 5.9 Alimta: Revenue Forecast ($bn), 2012-2023

Figure 5.10 Velcade: Revenue by Company ($bn), 2008-2012

Figure 5.11 Velcade: Revenue Forecast ($bn), 2012-2023

Figure 5.12 Nexavar: Revenue ($bn), 2008-2012

Figure 5.13 Nexavar: Revenue Forecast ($bn), 2012-2023

Figure 5.14 Tasigna: Revenue ($bn), 2008-2012

Figure 5.15 Tasigna: Revenue Forecast ($bn), 2012-2023

Figure 5.16 Temodar: Revenue ($bn), 2010-2012

Figure 5.17 Temodar: Revenue Forecast ($bn), 2012-2023

Figure 5.18 Vidaza: Revenue by Company ($bn), 2008-2012

Figure 5.19 Vidaza: Revenue Forecast ($bn), 2012-2023

Figure 5.20 Sprycel: Revenue by Company ($bn), 2008-2012

Figure 5.21 Sprycel: Revenue Forecast ($bn), 2012-2023

Figure 5.22 Afinitor: Revenue ($bn), 2009-2012

Figure 5.23 Afinitor: Revenue Forecast ($bn), 2012-2023

Figure 5.24 Yervoy: Revenue ($bn), 2011-2012

Figure 5.25 Yervoy: Revenue Forecast ($bn), 2012-2023

Figure 5.26 Kyprolis and Pomalyst: Revenue Forecasts ($bn), 2012-2023

Figure 5.27 Bosulif and Iclusig: Revenue Forecasts ($bn), 2012-2023

Figure 5.28 Cometriq: Revenue Forecast ($bn), 2012-2023

Figure 5.29 Stivarga: Revenue Forecast ($bn), 2012-2023

Figure 9.1 Global Orphan Cancer Drugs Market: Revenue ($bn) by Sector, 2012, 2017 & 2023

Figure 9.2 Global Orphan Cancer Drugs Market: Revenue ($bn) by Region, 2012, 2017 & 2023

Companies Listed



Accentia Biopharmaceuticals


AEterna Zentaris

Agência Nacional de Vigilância Sanitária (ANVISA) [Brazil]

American Association for Cancer Research (AACR)

American Cancer Society

American Society of Clinical Oncology (ASCO)


APP (part of Fresenius Kabi)


ARIAD Pharmaceuticals


Baxter International


Biogen Idec

BioSante Pharmaceuticals

BioVest International

Boehringer Ingelheim

Bristol-Myers Squibb

Bundesamt für Gesundheit (BAG) [Switzerland]

Cambridge Antibody Technology (part of MedImmune, a division of AstraZeneca)


Cancer and Leukemia Group B (CALGB) [US]

Celator Pharmaceuticals


Cell Therapeutics

Celldex Therapeutics


Ceptaris Therapeutics

Children's Oncology Group (COG) [US]

Chroma Therapeutics

Chugai Pharmaceutical (part of Roche)

Clavis Pharma

Coronado Biosciences

Cyclacel Pharmaceuticals


Daiichi Sankyo

Dainippon Sumitomo Pharma

Del Mar Pharmaceuticals


Diffusion Pharmaceuticals

Dr. Reddy's Laboratories


Eli Lilly

EMA Committee for Orphan Medicinal Products (COMP) [EU]

Emergent BioSolutions

Enzon Pharmaceuticals

European Commission

European Medicines Agency (EMA)


Food and Drug Administration (FDA) [US]

Gamida Cell

Gedeon Richter


Genentech (part of Roche)

Grupo Zeltia


Guangxi Wuzhou Pharmaceutical


Icon Bioscience

ImmunoCellular Therapeutics


Independent Data Monitoring Committee (IDMC)

Institute of Cancer Research (ICR) [UK]

Intas Biopharmaceuticals

Intellectual Property Appellate Board (IPAB) [India]


Janssen Biotech (part of J&J)

Kyowa Hakko Kirin

Leukaemia and Lymphoma Society (LLS) [US]

LG Life Sciences

Ligand Pharmaceuticals



Medarex (part of Bristol-Myers Squibb)

MedImmune (part of AstraZeneca)

Merck & Co.

Merck Serono


Micromet (part of Amgen)

Millennium Pharmaceuticals (part of Takeda)

Ministry of Health, Labor and Welfare (MHLW) [Japan]

Natco Pharma

National Cancer Institute (NCI) [US]

National Cancer Research Institute (NCRI) [UK]

National Comprehensive Cancer Network (NCCN) [US]

National Congress of the Communist Party of China

National Health Service (NHS) [UK]

National Institute for Health and Care Excellence (NICE) [UK]

Nippon Shinyaku

Northwest Biotherapeutics


Nycomed (part of Takeda)

Onconova Therapeutics


Ono Pharmaceutical

Onyx Pharmaceuticals

Otsuka Pharmaceutical

PDL BioPharma

Peregrine Pharmaceuticals



PharmaMar (part of Grupo Zeltia)

Pharmion (part of Celgene)


Rare Diseases Europe (EURORDIS)

Reliance Life Sciences


Rockefeller University

Russian Ministry of Health


Samsung Bioepis

Sandoz (part of Novartis)


Schering-Plough (part of Merck & Co.)

Schnell Biopharmaceuticals

Scottish Medicines Consortium (SMC)

Seattle Genetics

Shanghai CP Guojian Pharmaceutical

Sigma-Tau Pharmaceuticals

Society for Neuro-Oncology

Solasia Pharma

Spectrum Pharmaceuticals

Stada Arzneimittel

Sunesis Pharmaceuticals

Supreme Court of India

Swedish Orphan Biovitrum (Sobi)

SymBio Pharmaceuticals

Takeda Pharmaceutical Company

Talon Therapeutics

Tamir Biotechnology (formerly Alfacell)


Teva Pharmaceutical Industries

Therapeutic Goods Administration (TGA) [Australia]

Tolero Pharmaceuticals



University of Illinois

University of Texas MD Anderson Cancer Center

Valeant Pharmaceuticals


World Health Organization (WHO)

Yakult Honsha


Zenyaku Kogyo


To order this report:Drug_and_Medication Industry: Orphan Drugs for Cancer: R&D and Market 2013-2023


Contact Clare:
US:(339) 368 6001
Intl:+1 339 368 6001


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