Navigation Links
Initiating Rare Disease Drug Discovery Projects
Date:9/19/2012

NEW YORK, Sept. 19, 2012 /PRNewswire/ -- Reportlinker.com announces that a new market research report is available in its catalogue:

Initiating Rare Disease Drug Discovery Projects

http://www.reportlinker.com/p0968583/Initiating-Rare-Disease-Drug-Discovery-Projects.html#utm_source=prnewswire&utm_medium=pr&utm_campaign=Drug_Discovery_and_Development

In comparison with major diseases, the targeting of rare diseases poses many different challenges, necessitating consideration of bespoke R&D strategies for drug discovery efforts to be successful. This report examines the issues that need to be considered in the earliest stages of embarking on a rare disease project.Understand why rare diseases make attractive targets for launching new drug discovery projects.Identify the key challenges that are presented by low patient prevalences.Assess how the research strategy chosen can be influenced by the disease prevalence.Understand the importance of considering issues of similarity versus other orphan drugs.Compare the scenarios in which repurposing existing drugs offers advantages over the development of novel drugs, and vice versa.While disease prevalence has an impact on the commercial viability of a new treatment, returns are achievable even for ultra rare conditions. Rare diseases can provide sufficient opportunities for commercialization of multiple therapeutic agents. This is the case even for some ultra rare conditions such as Gaucher disease and Fabry disease.Both clinical experts and patient groups provide valuable resources in understanding a rare diseas
'/>"/>

SOURCE Reportlinker
Copyright©2012 PR Newswire.
All rights reserved

Page: 1 2 3

Related medicine technology :

1. Clinical Trial at Evergreen Healthcare Shows Intestinal Gel Reduces Symptoms of Advanced Parkinsons Disease
2. New post-hoc analyses examined Neupro® effects on pain, depressed mood, apathy and fatigue in patients with Parkinsons disease
3. New Clinical Endocrinology Guidelines Support Lp-PLA2 Measurement For Risk Assessment of Coronary Artery Disease
4. Ultragenyx Announces Phase 1 Results of UX001 in Hereditary Inclusion Body Myopathy (HIBM), a Rare Neuromuscular Disease
5. Chef Spike Mendelsohn Dishes on How to Turn Down the Heat on Acid Reflux Disease
6. New Published Guidelines to Help Physicians Diagnose and Treat Lupus Kidney Disease
7. The ALS Therapy Development Institute Partners with Neurotune to Investigate Potential Treatments for Motor Neuron Disease
8. Rigel Advances Asthma Programs: Two Inhaled Drug Candidates Take Aim at Acute and Chronic Lung Disease
9. Ceregene Parkinsons Disease Study Demonstrates Long-term Neurturin Expression and Enhanced Dopamine Activity 4 Years Following Delivery of CERE-120 (AAV2-neurturin)
10. UCB Proudly Reinforces Long-Standing Commitment to Crohns Disease Community at Digestive Disease Week 2012
11. Receptos to Deliver Scientific Presentation at Digestive Disease Week 2012 about the Therapeutic Role of RPC1063 in Inflammatory Bowel Disease
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:1/15/2014)... FRANKLIN, Ohio , Jan. 15, 2014  A novel wearable ... it easy and painless for patients to self-inject prescription drugs ... of disorders, including cancer, blood diseases, autoimmune deficiencies, and genetic ... expected to grow to $220B by 2018, according to analysts.   ...
(Date:1/14/2014)... 2014  Luminex Corporation (Nasdaq: LMNX ) today announced ... of 2013 on Monday, February 3, 2014. A press release ... of trading. (Logo: http://photos.prnewswire.com/prnh/20100104/LUMINEXLOGO ) ... operating highlights and financial results for the fourth quarter and ...
(Date:1/14/2014)... , Jan. 14, 2014 The Brandeis Medical Center, led ... a premier and affordable laser tattoo removal experience with ... Brandeis, focus is in providing high quality cosmetic services with cutting ... " Southern California has seen a ...
Breaking Medicine Technology:Enable Injections Presents A New Class of Injectors for Drug Delivery at PEPTalk, Drug Delivery Partnership Meetings 2Luminex Corporation Fourth Quarter Earnings Release Scheduled for February 3, 2014 2Luminex Corporation Fourth Quarter Earnings Release Scheduled for February 3, 2014 3Beverly Hills Physician Features Tattoo Removal with the Astanza Duality Laser, Offers $99 Special 2
... Fla., July 5, 2011 MSC Care Management, a ... management solutions to the workers, compensation industry, has launched ... to help relieve the administrative burden for claims adjusters ... a proprietary online tool that allows for faster and ...
... Tourette Syndrome Association, Inc., (TSA) has unveiled a 115-square ... generate awareness and acceptance of all people living with ... "We Have Tourette,s But Tourette,s Doesn,t Have Us" is ... everyday with the symptoms of involuntary sounds and movements ...
Cached Medicine Technology:MSC CareConnect Provides Real-Time, Online Communication and Referral Management to Claims Professionals 2EHE International Showcases The National Tourette Syndrome Association, Inc. with Month-Long Window Display in Rockefeller Center Plaza 2
(Date:4/23/2014)... predict which patients might suffer potentially fatal side-effects from ... assesses brain scans using pattern recognition software similar to ... been developed by researchers at Imperial College London. Results ... which used the software are published in the journal ... 15 million people each year worldwide. Ischemic strokes are ...
(Date:4/23/2014)... benefits of probiotics, antioxidants and other nutritional compounds, more ... industry is getting in on the action. But legitimate ... the industry is responding with clinical research to shore ... Chemical & Engineering News (C&EN), the weekly ... M. Bomgardner, a senior editor at C&EN, writes that ...
(Date:4/23/2014)... SEATTLE, Washington, April 21, 2014 Five for-profit ... total of $1.25 million in Proof of Concept ... from ideas into commercial products, the Life Sciences ... a $300,000 Entrepreneur Mentoring Program grant to the ... a statewide advisory network to train the next ...
(Date:4/23/2014)... Effects of Midlife Occupational and Leisure Time Physical Activity ... physical activity in midlife increases the risk of mobility ... the risk. This is found in a study which ... The study was conducted at the Gerontology Research Center ... , Heavy physical labor is often repetitive, wears the ...
(Date:4/23/2014)... shown that proliferation of endogenous neural precursor cells ... and axons. From the perspective of neural plasticity, ... University in China observed the effects of functional ... proliferation and expression of basic fibroblast growth factor ... on the infarct side. The researchers found that ...
Breaking Medicine News(10 mins):Health News:Airport security-style technology could help doctors decide on stroke treatment 2Health News:Airport security-style technology could help doctors decide on stroke treatment 3Health News:LSDF announces commercialization grants and Entrepreneur Mentoring Program 2Health News:Midlife occupational and leisure-time physical activity limits mobility in old age 2
... of bird flu which had reached a feverish pitch early in ... //if the virus has actually beaten a retreat. , ... flu is dynamic in the winter months, as the virus can ... The H5N1 virus which had earlier restricted itself to Southeast Asia ...
... the University of North Carolina at Chapel Hill School of ... according to a study by an international group of researchers. ... by Dr. Carol Otey and her former student, Dr. Mana ... in Boston. Otey has shown that palladin is involved in ...
... basic symptoms associated with ovarian cancer may aid clinicians ... a new study.// This index is expected to serve ... details of this study is published in the January ... of the American Cancer Society, the study reveals that ...
... thousands of quails at a farm in Kimje.// It was ... a farm in Kimje, 262 kilometers southwest of Seoul to the ... in the farm of the latest outbreak. ,This recent ... starting with an first outbreak of highly virulent H5N1 virus on ...
... (Australia) government has decided //to toughen its laws on anti-smoking. ... carrying children. This comes in the wake of ... dies every 18 days, when exposed to cigarette smoke. ... Queenslanders Report, 2006, made these comments. ,A review ...
... University School of Medicine have found out that successful lung ... in many smokers. This study published in the December issue ... look at smoking relapse among people who were "forced" to ... found that close to half of 154 smokers who had ...
Cached Medicine News:Health News:Gene Discovered by Researchers Tied to Pancreatic Cancer 2Health News:A Basic Symptom Index For Early Detection Of Ovarian Cancer 2Health News:Lung Cancer Surgeries Doesn’t Help Breaking Nicotine Dependence in Smoker 2Health News:Lung Cancer Surgeries Doesn’t Help Breaking Nicotine Dependence in Smoker 3
... components that comprise the SmartPill GI ... comprise the SmartPill GI Monitoring System: ... Receiver software and SmartPill MotiliGI software. ... indispensable parts of the SmartPill GI ...
... for POLYGRAM NET™ (PNET) works with ... record and analyze pressure, swallow, and ... procedures. The PNET software and Polygraf ... water-perfused manometry catheters and the RespSponse™ ...
... Advanced pH Analysis for POLYGRAM NET™ ... Testing Application. Like the standard application, Advanced ... by either the Digitrapper™ Catheter-Based pH Recorder ... ,Designed primarily for use by clinical ...
Capillaries available in glass and "non-PVC" plastic. Match different analyzer requirements. Variety of sizes match sample-volume requirements of individual analyzers....
Medicine Products: