Navigation Links
Inherited Orphan Blood Disorders Therapeutics Market to 2019 - Breakthrough Drugs Remain Elusive Against Backdrop of High Unmet Need
Date:1/29/2013

, in-depth profiling of major products and details of recent industry deals.

The report is built using data and information sourced from proprietary databases, primary and secondary research, and in-house analysis by GBI Research's team of industry experts.

The sickle cell anemia market will be the fastest growing of the three markets during the forecast period with a Compound Annual Growth Rate (CAGR) of 9% seeing it reach $70m in 2019. The thalassemia market will grow at a lower CAGR of 7% to reach $59m in 2019. HAE represents the largest but slowest growing market, expected to reach $1.89 billion by 2019 at a CAGR of 3%.

 

Scope

- Current and future treatment trends for three rare diseases

- Market forecasts for three rare diseases across seven major markets

- Analysis of the developmental pipelines for three rare diseases

- Information on recent industry deals

 

Reasons to buy

- Understand how the inherited orphan blood diseases market has developed and is continuing to develop within the featured markets

- Predict which products are likely to be most successful in the future

- Gain an understanding of the possible market available for specific products

 

Table of Contents

1 Table of Contents 4

1.1 List of Tables 6

1.2 List of Figures 6

2 Inherited Orphan Blood Diseases - Introduction 8

2.1 Overview 8

3 Inherited Orphan Blood Disorders - Therapeutic Landscape 9

3.1 Sickle Cell Anemia 9

3.1.1 Disease Overview 9

3.1.2 Revenues 14

3.1.3 Revenue Analysis by Country 14

3.1.4 Annual Cost of Therapy 18

3.1.5 Treatment Usage Patterns 19

3.1.6 Marketed Products 20

3.1.7 Market Drivers 21

3.1.8 Market Restraints 21

3.2 Sickle Cell Anemia: Research and Development Pipeline 22

3.2.1 Overview 22

3.2.2 Pipeline by Clinical Phase of De
'/>"/>

SOURCE Reportlinker
Copyright©2012 PR Newswire.
All rights reserved

Page: 1 2 3 4 5 6 7

Related medicine technology :

1. Savara Pharmaceuticals AeroVanc Granted U.S. Orphan Drug Designation for the Treatment of MRSA Lung Infection in Cystic Fibrosis Patients
2. FDA Grants Orphan Drug Status To Morphoteks Amatuximab (MORAb-009)
3. Albireo Has Been Granted Orphan Drug Designation for A4250 from the US FDA for the Treatment of Progressive Familial Intrahepatic Cholestasis (PFIC) and for Primary Biliary Cirrhosis (PBC)
4. EMA Grants Orphan Designation to Edison Pharmaceuticals for EPI-743 for Treatment of Leigh Syndrome
5. FDA Grants Orphan Drug Designation To GeNO LLC For Use Of Inhaled Nitric Oxide In Treatment Of Persistant Pulmonary Hypertension Of The Newborn (PPHN)
6. Albireo Receives Positive Opinion for Orphan Drug Designation for A4250 for Severe Liver Diseases
7. Grifols Initiates Safety Study of Inhaled Alpha1-Proteinase Inhibitor (Human) Following Orphan Drug Designation for Cystic Fibrosis
8. European Commission Grants Orphan Medicinal Product Designation for Emmaus Medicals Sickle Cell Treatment
9. CSL Behring Receives FDA Orphan Drug Designation for rIX-FP, a Novel Therapy in Development to Treat Congenital Factor IX Deficiency (Hemophilia B)
10. Tris Pharma Announces Approval of First-Ever Generic to Delsym® Dextromethorphan Polistirex Extended-Release Suspension
11. Perrigo Announces FDA Final Approval Of Tris Pharmas Dextromethorphan Polistirex Extended-Release Oral Suspension
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:8/28/2015)... y LONDRES, 28 de agosto de 2015 ... anunció hoy su participación en el  Congreso de ... soluciones cardiológicas más recientes y novedosas, entre ellas ... conectan a las personas y la tecnología con ... a diagnosticar, guiar los tratamientos y permitir atención ...
(Date:8/28/2015)... 2015 The global mHealth ... billion by 2020, growing at a CAGR of 47.6% ... by Grand View Research, Inc. Monitoring services is expected ... 2014 to 2020.      (Logo: http://photos.prnewswire.com/prnh/20150105/723757 ... rising incidences of chronic diseases such as cancer, heart ...
(Date:8/27/2015)... Aug. 27, 2015  A recent study by ... Journal, compared the Arthrosurface HemiCAP® Wave implant, which ... an "onlay" design implant for isolated patellofemoral disease. ... function and pain scores, none of the patients ... (OA). However, 53% of the patients in the ...
Breaking Medicine Technology:Philips presenta nuevas soluciones cardiológicas integradas para desarrollar procedimientos menos invasivos 2Philips presenta nuevas soluciones cardiológicas integradas para desarrollar procedimientos menos invasivos 3Philips presenta nuevas soluciones cardiológicas integradas para desarrollar procedimientos menos invasivos 4Philips presenta nuevas soluciones cardiológicas integradas para desarrollar procedimientos menos invasivos 5mHealth Market is Expected to Reach $49.12 Billion By 2020: Grand View Research, Inc. 2mHealth Market is Expected to Reach $49.12 Billion By 2020: Grand View Research, Inc. 3mHealth Market is Expected to Reach $49.12 Billion By 2020: Grand View Research, Inc. 4mHealth Market is Expected to Reach $49.12 Billion By 2020: Grand View Research, Inc. 5Study Demonstrates Dramatic Reduction in Progression of Osteoarthritis with the Arthrosurface "Inlay" Patellofemoral Implant Design Compared to Traditional "Onlay" Implant 2Study Demonstrates Dramatic Reduction in Progression of Osteoarthritis with the Arthrosurface "Inlay" Patellofemoral Implant Design Compared to Traditional "Onlay" Implant 3
... , SCOTTSDALE, Ariz., Oct. 14 When it comes ... it is easy to point a finger at a ... regulations. But new data from the 2009 Leadership Skills ... ( http://www.gottochange.com ), indicates that the root ...
... INDIANAPOLIS, Oct. 14 Eli Lilly and Company (NYSE: ... Tippecanoe Laboratories manufacturing facility to Evonik Industries AG, one ... located in Lafayette, Indiana, will remain in operation with ... and specialty chemical and animal health products. In connection ...
Cached Medicine Technology:Slumps in Pharmaceutical Profitability Tied to Insufficient Management Training 2Slumps in Pharmaceutical Profitability Tied to Insufficient Management Training 3Lilly to Sell Tippecanoe Manufacturing Site to Evonik Industries 2Lilly to Sell Tippecanoe Manufacturing Site to Evonik Industries 3Lilly to Sell Tippecanoe Manufacturing Site to Evonik Industries 4
(Date:8/29/2015)... York, NY (PRWEB) , ... August 29, 2015 , ... ... unofficial end of summer (which astronomically, officially ends on September 22nd this year). For ... summer-induced cyber security hangovers linger on which could prove far more costly than a ...
(Date:8/29/2015)... ... 2015 , ... The popular television program VOICES IN AMERICA, hosted by legendary ... be devoting an entire short segment to the subject of diabetes. Diabetes is a ... a daily basis, but recent advancements in medical science may prove to be a ...
(Date:8/28/2015)... ... , ... An online provider of CPAP machines, masks, supplies, and accessories, My ... affordable by offering shipping at no cost to you, directly to your door on ... size. My Cpap Store is located in Las Vegas, Nevada. , Sleep apnea is ...
(Date:8/28/2015)... ... , ... With the goal of furthering music education programs in schools, the ... County Fairgrounds in Mendon, IL on May 30th, 2015. Backed once again by Best ... the underfunded school districts of Mendon and its neighboring town of Quincy, IL. Best ...
(Date:8/28/2015)... ... August 28, 2015 , ... The 6th Annual Survivor in the City, ... added yet another accolade to its cadre of widespread support—an official letter of support ... help of the medical community and the University of Illinois at Chicago’s Department of ...
Breaking Medicine News(10 mins):Health News:Business Cyber Security – Come Out of the Summer with a Clean Slate 2Health News:Business Cyber Security – Come Out of the Summer with a Clean Slate 3Health News:Business Cyber Security – Come Out of the Summer with a Clean Slate 4Health News:My Cpap Store Now Offering Delivery Special 0 Cost to You 2Health News:Best Drug Rehabilitation Interviews Country-Rock Duo Highway Run at the 2015 "Music With A Mission" Benefit Concert 2Health News:Chicago Mayor Pens Official Support of Annual Survivor in the City Event Benefitting Brain Aneurysm Foundation 2Health News:Chicago Mayor Pens Official Support of Annual Survivor in the City Event Benefitting Brain Aneurysm Foundation 3
... MOBILE PHONE ALERT: Evidence and recommendations from scientists and physicians ... June 19 Prominent researchers around the world are raising ... Today there are 4 billion cell phones in the world, ... -- PDAs, Wi-Fi, cordless phones, baby monitors and more -- ...
... Pa., June 19 Kensey Nash Corporation (Nasdaq: ... innovative solutions and technologies for a wide range of ... adopted a stockholders, rights plan. The rights plan is ... potentially coercive takeover practices or takeover bids and to ...
... , BEIJING, June 19 /PRNewswire-Asia-FirstCall/ ... CMED ), a leading China-based medical device,company that develops, ... unaudited preliminary financial results for,the fourth fiscal quarter (,4Q ... March 31, 2009 (,FY2008,). The Company,s 2008 fiscal ...
... ... to be recognized with prestigious professional designation , ... Philadelphia, PA (Lexis Nexis) June 19, 2009 -- Galfand Berger, a Philadelphia-based ... decades, today announced that three of its attorneys have been named by Pennsylvania Super Lawyers ...
... Bariatric Advantage, Division ... scheduled for June 21-26 in Dallas, TX. , ... Irvine, CA (PRWEB) June 19, 2009 -- Bariatric Advantage, Division of Catalina ... June 21-26 in Dallas, TX. "The new products have been developed to meet the ...
... for Good Times , , MALIBU, Calif., June 18 ... championship event that features the highest quality wave-riding skills the ... Saturday and Sunday, June 20 and June 21. The ... help children with Cancer, is free to the public. , ...
Cached Medicine News:Health News:'Radiation Rescue: 4 Steps to Safeguard Your Family from the Other Inconvenient Truth - The Health Hazards of Wireless Technology' 2Health News:Kensey Nash Corporation Adopts Stockholder Rights Plan 2Health News:Kensey Nash Corporation Adopts Stockholder Rights Plan 3Health News:Kensey Nash Corporation Adopts Stockholder Rights Plan 4Health News:China Medical Technologies Announces Selected Unaudited Preliminary Financial Results for the Fourth Fiscal Quarter and Full Year Ended March 31, 2009 2Health News:China Medical Technologies Announces Selected Unaudited Preliminary Financial Results for the Fourth Fiscal Quarter and Full Year Ended March 31, 2009 3Health News:Three Attorneys from Philadelphia's Galfand Berger Honored as Pennsylvania Super Lawyers 2Health News:Bariatric Advantage to Introduce Ten (10) New Products at ASMBS 2
... Eppendorf Reference Series 2000 Pipette is a ... a compact and robust design, and superior ... used to operate the measuring stroke and ... Product features:Eppendorf "pipette/tip" system ensures utmost accuracy ...
Inquire...
... Pipette is a synonym for pipetting accuracy, ... design, and superior operating comfort. Its single, ... measuring stroke and blow-out as well as ... ensures utmost accuracy and precision. Ejection sleeve ...
... Reference Series 2000 Pipette is a synonym ... compact and robust design, and superior operating ... to operate the measuring stroke and blow-out ... features:Eppendorf "pipette/tip" system ensures utmost accuracy and ...
Medicine Products: