Navigation Links
Gene Therapy Provides Vision to People who Were Nearly Blind
Date:4/27/2008

he success in the first three patients, however, will position the researchers well to plan Phase II clinical studies to evaluate the treatment's potential effectiveness in younger children who were born blind from LCA. The investigators believe the treatment has the potential to give near-normal vision to these children.

The first step toward the development of this treatment began with the discovery of the RPE65 gene in 1993. In 2000, the first dog born blind from LCA, a Briard named Lancelot, was successfully treated with gene therapy, and has been seeing well since then with just a single treatment. More than 50 dogs have now been treated successfully and are all seeing well. Clinical trials of the procedure began in October 2007 at the Foundation-funded Children's Hospital of Philadelphia (CHOP)-Penn Pediatric Center for Retinal Degenerations in Philadelphia.

More than 10 million people across the United States are affected by retinal degenerative diseases which include: macular degeneration, retinitis pigmentosa, and Usher syndrome.

About the Foundation Fighting Blindness

The Foundation Fighting Blindness (http://www.FightBlindness.org) is the largest source of non-governmental funding for retinal degenerative disease research in the world. The urgent mission of the Foundation Fighting Blindness is to drive the research that will provide preventions, treatments and cures for people affected by retinitis pigmentosa, macular degeneration, Usher syndrome, and the entire spectrum of retinal degenerative diseases.


'/>"/>
SOURCE Foundation Fighting Blindness
Copyright©2008 PR Newswire.
All rights reserved

Page: 1 2

Related medicine technology :

1. Dr. Calvin Grant Presents Results from Xibrom(TM) Combination Therapy with Lucentis(R) at the 2008 Annual Meeting of the Association for Research in Vision and Ophthalmology (ARVO)
2. FTY720, a novel oral therapy in development for MS, shows sustained benefits for the majority of patients after three years of treatment
3. In Blood Vessel Stents, Innovative Materials Allow Better Control, Delivery of Gene Therapy
4. Karmanos Researchers Find Non-Toxic Agents Added to Conventional Chemotherapy Decrease Survival of Colon Cancer Cells
5. ALS Therapy Development Institute Signs Collaboration Agreement with the Allen Institute for Brain Science
6. MAP Pharmaceuticals Reports Positive Results From Phase 2a Clinical Trial of Combination Therapy in Adult Asthmatics
7. CV Therapeutics Anti-Ischemic Therapy Ranexa(R) Significantly Reduces Cardiac Chest Pain Symptoms and Recurrent Ischemia in MERLIN-TIMI 36 Patients With Angina
8. Final Data From the Bioheart Seismic Trial Suggest Safety, Efficacy of Autologous Stem-Cell Therapy for Treating Congestive Heart Failure
9. Final Data From the SEISMIC Trial Suggest Safety, Efficacy of Autologous Stem- Cell Therapy for Treating Congestive Heart Failure
10. NeoVista Presents One Year Data on Novel Wet AMD Therapy at Macula Society
11. Early Research Suggests Umbilical Cord Blood Cell Therapy May Reduce Progression of Alzheimers Disease
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:10/19/2014)... October 19, 2014 Große ... Das Problem dabei ist, dass große Pharmafirmen ... Kompetenz zu teilen. Es war deshalb ... wir uns umso mehr, dass es uns gelungen ... bei Kühlketten aufzuschreiben - mit einem Vorbehalt - ...
(Date:10/17/2014)... HILL, N.C. , Oct. 17, 2014 /PRNewswire/ ... insights is a critical success factor in today,s ... must develop market research organizations that effectively and ... location, specialty or service area. ... create value and earn recognition from internal clients ...
(Date:10/17/2014)... Oct. 17, 2014 UBM Medica US announces that ... online community and information resource for neurologists and other healthcare ... Alzheimer disease , with discussions of the latest developments ... million Americans have Parkinson disease , more than the total ... Lou Gehrig disease. Diagnosis can be difficult because there ...
Breaking Medicine Technology:Vergleichsbericht zu Pharma-Kühlketten und CRT 2Effective Training Programs for Market Research Groups can Boost Overall Organizational Success 2Neurology Times Features Coverage of Parkinson and Alzheimer Disease 2Neurology Times Features Coverage of Parkinson and Alzheimer Disease 3
... March 19, 2012  BioStorage Technologies, a global provider ... cold chain logistics for the bioscience industry, announced ... webinar titled, "Comprehensive Sample Management: Leveraging an Onsite ... Thursday, March 22, from 11:00 AM to 12:30 ...
... Reportlinker.com announces that a new market research ... Branded Prescription Pharmaceutical Sales ... http://www.reportlinker.com/p0799256/Branded-Prescription-Pharmaceutical-Sales-Outlook-to-2016.html#utm_source=prnewswire&utm_medium=pr&utm_campaign=Pharmaceutical ... achieved sales of $558bn having experienced a ...
Cached Medicine Technology:BioStorage Technologies to Host Live Webinar on Optimizing the Value of Sample Assets 2Branded Prescription Pharmaceutical Sales Outlook to 2016 2Branded Prescription Pharmaceutical Sales Outlook to 2016 3Branded Prescription Pharmaceutical Sales Outlook to 2016 4Branded Prescription Pharmaceutical Sales Outlook to 2016 5
(Date:10/20/2014)... 2014 Principle Business Enterprises, a family ... manufacturing top-of-the-line absorbent products. The company has recently ... popular brand, Tranquility® Premium Protection absorbent products. The ... gave its packaging a new look, and is currently ... to the public. , The new website, developed with ...
(Date:10/20/2014)... 2014 Based on a proprietary ... imaging assays capable of determining DNA sequence, location ... these three dimensions of high-resolution data, dGH assays ... widest range of disease-causing genetic rearrangements, including chromosomal ... genomic tools, including today’s advanced sequencing technologies. , ...
(Date:10/20/2014)... Punzoné , the first line of ultra-premium organic ... to celebrate this month. October marks Italian Heritage Month – ... of Americans of Italian heritage and Italians in America. October ... its favorite Italian cocktails and encourages everyone to enjoy its ... it is only in a glass. , Punzoné continues ...
(Date:10/19/2014)... 2014 Recently, BambooIndustry.com, one of the ... new range of bamboo deckings . Moreover, the ... items; they are now available at deeply discounted rates. ... is hard to overstate the significance of online business ... online services. The company’s workers are striving to deliver ...
(Date:10/19/2014)... Recently, Fancyflyingfox.com, an innovative company that ... announced its latest designs of 2014 mother of ... elegant outfits are offered with big discounts, up to ... October 30 can enjoy this special offer. , ... it has become one of the leading brands in ...
Breaking Medicine News(10 mins):Health News:Tranquility® Premium Protection Incontinence Products Releases New Logo and Website 2Health News:KromaTiD Launches Genome Screening and Discovery Services 2Health News:KromaTiD Launches Genome Screening and Discovery Services 3Health News:Celebrate Italian Heritage Month With Authentic Cocktails from Punzoné: The Only Ultra Premium Line of Organic Imported Italian Vodka 2Health News:Celebrate Italian Heritage Month With Authentic Cocktails from Punzoné: The Only Ultra Premium Line of Organic Imported Italian Vodka 3Health News:Celebrate Italian Heritage Month With Authentic Cocktails from Punzoné: The Only Ultra Premium Line of Organic Imported Italian Vodka 4Health News:High Quality Bamboo Deckings, New Items Unveiled By BambooIndustry.com 2Health News:Fancyflyingfox.com Updates Its Website With New Mother Of The Bride Dresses For 2014 2
... Care is undertaking an electronic medical record integration project ... is a multi-year, multi-entity corporate initiative to implement common ... in processes and workflows across the system. Currently in ... next four years, the way UMass Memorial collects, views, ...
... people to stay binge-free , THURSDAY, April 1 (HealthDay ... eating is effective and can save patients money, according ... asked to read the book "Overcoming Binge Eating," which ... six-step self-help program using self-monitoring, self-control and problem-solving strategies. ...
... ... with half of their tour profits donated to relief efforts for Haiti and Hurricane Katrina ... Philadelphia, PA (PRWEB) ... for the Half 4 Humanity Tour beginning April 5, 2010. The tour will ...
... Local swing set ... , ... When Tom Corcoran, owner of Kid Structures in Houston, was approached with an opportunity ... would do it but when he could get started. Just days away from the anticipated two-hour ...
... a cell wall and fuse with it could offer researchers ... of individual cells. Everything from signals generated as cells ... to medication could be monitored for up to a week, ... are so destructive they usually only allow a few hours ...
... in time for baseball,s opening day, a series of articles ... fairness in elite sports and what it takes to stop ... questions about which athletes are really "female," are explored. ... the lead essay Thomas H. Murray, president of The Hastings ...
Cached Medicine News:Health News:UMass Memorial health care develops fully integrated EMR 2Health News:Short-Term Program for Binge Eaters Breaks New Ground 2Health News:Eric from Philly and Alia Announce the Half 4 Humanity Tour 2Health News:Eric from Philly and Alia Announce the Half 4 Humanity Tour 3Health News:Eric from Philly and Alia Announce the Half 4 Humanity Tour 4Health News:Eric from Philly and Alia Announce the Half 4 Humanity Tour 5Health News:Kid Structures Prepares Houston's Beach Family for New Adventures 2Health News:Kid Structures Prepares Houston's Beach Family for New Adventures 3Health News:Kid Structures Prepares Houston's Beach Family for New Adventures 4Health News:Nanoscale 'stealth' probe slides into cell walls seamlessly, say Stanford engineers 2Health News:Nanoscale 'stealth' probe slides into cell walls seamlessly, say Stanford engineers 3Health News:Baseball season opener: Athletes and ethicists look at fairness in sport 2
... The Finnpipette BioControl multichannel ... as the single channel model. ... all seven multichannel and five ... Both pipettes have a recharge ...
... solution and best value in high performance ... and ultra lightweight design reduce hand fatigue ... long, lever tip ejector , Color coding ... tips or for greater performance use Hamilton ...
... Pipette is ideal for all liquid handling ... ergonomically-placed operating buttons, and various dispensing techniques ... diluting make this a lab favorite. It ... manual pipette without any adverse effects on ...
... Unparalleled Comfort Pick one of our pipettors ... the trigger and ejector positionsright where they should ... are ergonomically designed to help avoid repetitive stress ... Productivity In The Palm Of Your Hand ...
Medicine Products: