Navigation Links
Families of Spinal Muscular Atrophy Receives FDA Orphan Drug Designation For Quinazoline495 For The Treatment of Spinal Muscular Atrophy
Date:8/28/2009

e Orphan Drug Act facilitates a close working relationship between regulatory agencies and companies aimed at accelerating the drug development and approval processes for treatment of rare diseases. Since the Act was passed in 1983, the Food and Drug Administration (FDA) has approved more than 200 new orphan products.

For further information, please see: http://www.fda.gov/orphan/oda.html

About Families of Spinal Muscular Atrophy:

Families of Spinal Muscular Atrophy is dedicated to creating a treatment and cure by:

  • Funding and advancing a comprehensive research program;
  • Supporting SMA families through networking, information and services;
  • Improving care for all SMA patients;
  • Educating health professionals and the public about SMA;
  • Enlisting government support for SMA;
  • Embracing all touched by SMA in a caring community.

Our vision is a world where Spinal Muscular Atrophy is treatable and curable.

A small group of parents started Families of SMA in 1984. They wanted to raise funds for SMA research to cure the disease, and support all affected families. Back then, very little was known about Spinal Muscular Atrophy. Very little research was being conducted. No one knew the cause of the disease let alone how to find a treatment and a cure. There were no family support services and no clinical trials. Patients and families affected by SMA were on their own and had little hope.

Today, FSMA has a different story to tell. Families of SMA has created hope for the SMA community that did not exist in 1984. FSMA has raised and funded over $50 million for SMA research. Support comes from generous individual donations and numerous fundraising events held by volunteer families an
'/>"/>

SOURCE Families of Spinal Muscular Atrophy
Copyright©2009 PR Newswire.
All rights reserved

Page: 1 2 3 4

Related medicine technology :

1. DNA Helps Reunite Children With Their Families
2. Families of Spinal Muscular Atrophy Announces Latest Developments on Three SMA Drug Discovery Programs
3. Video: New Survey Finds Mothers See Influenza as a Serious Health Threat, but Often Dont Get Their Families Vaccinated
4. Video: Novartis Vaccines and PTA Battle Flu: Public Health Vaccination Initiative Urges Families Lets Fight Flu Together!
5. Helping Families Cope After an Injury
6. Health Experts and Families Encourage Annual Childhood Flu Vaccination to Reduce Flu-Related Illnesses and Deaths in Children
7. Actress and Mother Jennifer Garner Kicks Off American Lung Associations Faces of Influenza Awareness Campaign, Encouraging Families to Get Vaccinated Against Influenza
8. New Research May Lead to Earlier Diagnosis and Treatment of Primary Biliary Cirrhosis in Families
9. New Research Shows Effectiveness of Stereotactic Body Radiotherapy for Spinal Tumors
10. Bone Biologics Announces Significant Milestone for Spinal Fusion Surgery Using Recombinant Protein and Demineralized Bone Matrix
11. Congresswoman Supporting Spinal Cord Research Intended to Benefit U.S. Veterans
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:5/22/2015)... May 22, 2015  RegeneRx Biopharmaceuticals, Inc. (OTCQB: RGRX), ... repair and regeneration, today announced that J.J. Finkelstein ... present a corporate overview at two upcoming investor conferences. ... SeeThruEquity 4 th Annual Microcap Conference on Thursday ... at 11:00 am EDT.  A webcast will ...
(Date:5/22/2015)... 22, 2015 According to a ... Product (Consumables, Instruments, Services), by Test Type (Indirect, Enzyme-based, ... Cytometry), by End Users - Global Forecast to 2020", ... expected to reach $736.85 Million by 2020 from $452.36 ... Browse 71 market data Tables and ...
(Date:5/22/2015)...  In a sweeping analysis assessing the current state ... researchers conclude that there remains considerable room for ... age groups, but especially for adolescents and young adults. ... treatment, underscoring the need to address barriers to care ... type 1 patients achieve optimal metabolic control. ...
Breaking Medicine Technology:RegeneRx to Present at 2 Investor Conferences 2RegeneRx to Present at 2 Investor Conferences 3Oxidative Stress Assays Market Worth $736.85 Million by 2020 2Oxidative Stress Assays Market Worth $736.85 Million by 2020 3Oxidative Stress Assays Market Worth $736.85 Million by 2020 4Study Reveals Poor Disease Control Among Adolescents and Young Adults with Type 1 Diabetes 2Study Reveals Poor Disease Control Among Adolescents and Young Adults with Type 1 Diabetes 3Study Reveals Poor Disease Control Among Adolescents and Young Adults with Type 1 Diabetes 4Study Reveals Poor Disease Control Among Adolescents and Young Adults with Type 1 Diabetes 5
... YORK, April 12, 2011 Reportlinker.com announces that ... its catalogue: Cardiac Markers ... Forecast to 2017 ... Pipeline Analysis, Competitive Landscape and Market Forecast to ...
... April 12, 2011 Reportlinker.com announces that a new ... Europe Nephrology and Urology Devices Market Outlook ... Europe Nephrology and Urology Devices Market Outlook to ... new report, "Europe Nephrology and Urology Devices Market Outlook ...
Cached Medicine Technology:Reportlinker Adds Cardiac Markers - Global Pipeline Analysis, Competitive Landscape and Market Forecast to 2017 2Reportlinker Adds Cardiac Markers - Global Pipeline Analysis, Competitive Landscape and Market Forecast to 2017 3Reportlinker Adds Cardiac Markers - Global Pipeline Analysis, Competitive Landscape and Market Forecast to 2017 4Reportlinker Adds Cardiac Markers - Global Pipeline Analysis, Competitive Landscape and Market Forecast to 2017 5Reportlinker Adds Cardiac Markers - Global Pipeline Analysis, Competitive Landscape and Market Forecast to 2017 6Reportlinker Adds Cardiac Markers - Global Pipeline Analysis, Competitive Landscape and Market Forecast to 2017 7Reportlinker Adds Cardiac Markers - Global Pipeline Analysis, Competitive Landscape and Market Forecast to 2017 8Reportlinker Adds Cardiac Markers - Global Pipeline Analysis, Competitive Landscape and Market Forecast to 2017 9Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 2Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 3Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 4Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 5Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 6Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 7Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 8Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 9Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 10Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 11Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 12Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 13Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 14Reportlinker Adds Europe Nephrology and Urology Devices Market Outlook to 2017 15
(Date:5/22/2015)... ZH Healthcare (ZH), a ... that Bill Lane, joins ZH’s Advisory Board. ... first of its kind, Freemium SaaS, Electronic Health ... Records (EHR) with an integrated practice management system ... portal, and more. Combined with its Revenue Cycle ...
(Date:5/22/2015)... 22, 2015 sweetFrog Enterprises, LLC. is pleased ... Texas. Jacksonville is now the 16th sweetFrog store located in ... listed as #22 on the Inc. 500 list of fastest ... and worked in East Texas for 20 years and love ... of the Jacksonville, and nearby Palestine, sweetFrog locations. “We are ...
(Date:5/22/2015)... AZ (PRWEB) May 22, 2015 In ... Olympics, Parker and Sons is offering to donate $5 ... installing an AC unit or water softening system. Customers ... behalf; Parker and Sons gets business; and the Special ... , The Special Olympics helps over 4.4 million athletes, ...
(Date:5/22/2015)... Bryce Henson, local fitness icon and ... Camp, recently accepted his program’s 100th client. Henson says ... of his location evidences the powerful impact his boot ... Body Boot Camp is the nation’s most popular and ... of locations across North America, Europe and Australia. Anaheim ...
(Date:5/22/2015)... Aliso Viejo, CA (PRWEB) May 22, 2015 ... 30 editable lower thirds designed exclusively for Final Cut ... creatively compatible with any design. , Intuitive on-screen-controls ... each unique lower third. Reflections, colors, layouts, and much ... the Inspector window. , Pro3rd Impression ...
Breaking Medicine News(10 mins):Health News:ZH Healthcare Adds Bill Lane to Advisory Board 2Health News:sweetFrog Opens New Location in Jacksonville, Texas 2Health News:Parker and Sons is Proud to Support the Special Olympics with Their Everybody Wins Program 2Health News:Healthy Living Brought to Anaheim— New Fitness Boot Camp Acquires 100 Clients 2Health News:Developers at Pixel Film Studios Release Pro3rd Impression for Final Cut Pro X. 2
... Foundation for Marriage and Family, NEW YORK, ... innovative program, "Supporting Healthy Marriage" to members,of the ... the program, administered by University Behavioral Associates, the,behavioral ... solid foundation,for marriage and family through communication, managing ...
... reduce lead dust during renovations , , MONDAY, March ... issued new rules designed to protect children from ... to homes and buildings. , Starting in ... standards" that are designed to reduce potential exposure ...
... 31 PPD, Inc. (Nasdaq:,PPDI) today announced it ... of global clinical development. In this role, he ... operations in,North America; Latin America; Europe, Middle East ... an exceptional resume with strong leadership,across a variety ...
... blocker beat pairing it with diuretic; Celebrex study finds ... 31 (HealthDay News) -- A large trial shows that ... in individuals with high blood pressure who are at ... percent reduction in the risks of death, heart attack, ...
... March 31 Seriously wounded veterans will learn,to ski, ... they may,have thought they would never do -- at ... to April 4 in Snowmass Village, Colo., TriWest ... in 21 western states, signed as the clinic,s host ...
... from 3 to 13 minutes, contrary to popular fantasy ... to a survey of U.S. and Canadian sex therapists., ... conducted a survey of 50 full members of the ... physicians, social workers, marriage/family therapists and nurses who have ...
Cached Medicine News:Health News:'Supporting Healthy Marriage' Program Offered by Montefiore 2Health News:New Rule Seeks to Protect Kids From Lead Paint 2Health News:PPD Names Mike Wilkinson Executive Vice President of Global Clinical Development 2Health News:PPD Names Mike Wilkinson Executive Vice President of Global Clinical Development 3Health News:Two Drugs Better Than One for High Blood Pressure 2Health News:Two Drugs Better Than One for High Blood Pressure 3Health News:Wounded Warriors Rig for Skiing, Rock Climbing, Other Winter Sports 2Health News:Good sexual intercourse lasts minutes, not hours, therapists say 2
For injecting anesthetics into the muscle cone. 25G x 1 1/2 in (.50 x 38mm)...
For administering local anesthetic prior to ophthalmic surgery. 27G x 1 1/4 in (.40 x 32mm). May also be used for retrobulbar administration....
... is the most versatile diagnostic tool in ... solutions for glaucoma, diabetic retinopathy, age-related macular ... RTA is the only system in the ... pole and the optic nerve areas in ...
... Meta-4 Computerized ENG utilizes a ... comprehensive nystagmus and ocular motor ... storage, data analysis and reanalysis ... data in the Meta-4 software ...
Medicine Products: