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Ataluren Phase 2 Data in Nonsense Mutation Cystic Fibrosis Published in the European Respiratory Journal
Date:7/1/2011

he United States and Europe and over 50 percent of patients in Israel. Available treatments for CF are designed to alleviate symptoms rather than correct the underlying cause of the disease. Based on the current standard of care, the treatment burden for CF patients is high and, on average, adults with CF take 7 daily therapies. More information regarding CF is available through the Cystic Fibrosis Foundation (www.cff.org).

ABOUT THE HADASSAH UNIVERSITY MEDICAL CENTER

The Hadassah University Medical Center is a leading provider of medical and health services in Israel, known for its pioneering vision and enduring commitment to patient-centered care and groundbreaking research. Incorporating all medical and surgical sub-specialties, its 800-bed Ein Kerem tertiary care hospital, 300-bed Mt. Scopus community hospital and satellite sites serve more than 1 million people a year from throughout Jerusalem, Israel and the Middle East.

The Hadassah University Medical Center is the flagship project of Hadassah, the Women's Zionist Organization of America, Inc.

ABOUT PTC THERAPEUTICS, INC.

PTC is a biopharmaceutical company focused on the discovery, development and commercialization of orally administered small-molecule drugs that target post-transcriptional control processes. Post-transcriptional control processes regulate the rate and timing of protein production and are of central importance to proper cellular function. PTC's internally discovered pipeline addresses multiple therapeutic areas, including rare genetic disorders, oncology, and infectious diseases. PTC has developed proprietary technologies that it applies in its drug discovery activities and are the basis for collaborations with leading biopharmaceutical companies. For more information, visit the company's web site at www.ptcbio.com.

REFERENCES:

(1) McKone EF, Goss CH,
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