BETHESDA, Md., Nov. 1, 2011 /PRNewswire-USNewswire/ -- For the first time, a drug that's designed to treat the underlying cause of cystic fibrosis, Kalydeco™ (ivacaftor), is under review by the U.S. Food and Drug Administration for possible approval in 2012. This milestone comes as the largest international gathering of cystic fibrosis experts kicks off in Anaheim, Calif., Nov. 3 – 5, 2011.
Kalydeco (kuh-LYE-deh-koh) is designed to address the genetic defect in cystic fibrosis in select patient groups, unlike all CF therapies now on the market, which only treat symptoms of the disease. It was formerly known as VX-770.
At the 25th annual North American Cystic Fibrosis Conference (NACFC), physicians, scientists and clinicians will present data and workshops on the latest advancements in CF related to research, care and drug development, including new clinical data on Kalydeco.
Key conference topics include:
Cystic fibrosis is a genetic disease that causes life-threatening lung infections and premature death. An estimated 30,000 people in the United States, and about 70,000 people worldwide, have CF. Ten million Americans are symptomless carriers of a defective CF gene. Fifty years ago, most children with CF died before reaching kindergarten. Today, because of Cystic Fibrosis Foundation-supported drug research and care, many people with CF are living into their 30s, 40s and beyond.
The 25th Annual North American Cystic Fibrosis Conference, the largest international gathering of cystic fibrosis research scientists and clinicians.
WHEN & WHERE:
Thursday, Nov. 3 – Satu
|SOURCE Cystic Fibrosis Foundation|
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