Navigation Links
Amicus Therapeutics Begins Phase 2 Clinical Trial of AT2220 in Pompe Disease
Date:6/3/2008

1 and 2 years of age. The late onset form of the disease begins between childhood and adulthood and has a slower rate of progression that is characterized by musculoskeletal and pulmonary symptoms that usually lead to progressive weakness and respiratory insufficiency. A high majority of patients have the late onset form of the disease. The U.S. Food and Drug Administration's Office of Orphan Products Development has granted orphan drug designation for the active ingredient in AT2220 in the United States.

About Amicus Therapeutics

Amicus Therapeutics is a biopharmaceutical company developing novel, oral therapeutics known as pharmacological chaperones for the treatment of a range of human genetic diseases. Pharmacological chaperone technology involves the use of small molecules that selectively bind to and stabilize proteins in cells, leading to improved protein folding and trafficking, and increased activity. Amicus is initially targeting lysosomal storage disorders, which are severe, chronic genetic diseases with unmet medical needs. Amicus has completed Phase 2 clinical trials of Amigal(TM) for the treatment of Fabry disease and is conducting Phase 2 clinical trials of Plicera(TM) for the treatment of Gaucher disease.

Forward-Looking Statements

Amicus cautions you that statements included in this press release that are not a description of historical facts are "forward-looking statements" within the meaning of Section 21E of the Private Securities Litigation Reform Act of 1995. Words such as, but not limited to, "look forward to," "believe," "expect," "anticipate," "estimate," "intend," "plan," "targets," "likely," "will," "would," "should" and "could," and similar expressions or words identify forward-looking statements. Such forward-looking statements are based upon current expectations that involve risks, changes in circumstances, assumptions and uncertainties. The inclusion of forward-looking statements should not be regarded as a
'/>"/>

SOURCE Amicus Therapeutics
Copyright©2008 PR Newswire.
All rights reserved

1

GOOD

Page: 1 2 3 4

Related medicine technology :

1. Amicus Therapeutics Announces Second Quarter 2007 Financial Results
2. Amicus Therapeutics Announces Plans to Present Phase 1 Data for AT2220 for Pompe Disease
3. Amicus Therapeutics Announces Positive Results From Two Phase 1 Clinical Studies of AT2220 for Pompe Disease
4. Amicus Therapeutics to Present at the 26th Annual JPMorgan Healthcare Conference
5. Amicus Therapeutics Presents Data from Clinical Ex Vivo Response Study and Phase 1 Studies of AT2220
6. Vicus Therapeutics to Present at the 234th American Chemical Society National Meeting in Boston, MA
7. Allos Therapeutics Initiates Study of PDX in Patients with Cutaneous T-Cell Lymphoma
8. TorreyPines Therapeutics Completes Patient Enrollment in Phase IIb Clinical Trial of Tezampanel for the Treatment of Acute Migraine Headache
9. CV Therapeutics Announces Eight Abstracts Accepted for Presentation at the European Society of Cardiology Congress 2007
10. Pharmacopeia Assists the World Health Organization in the Discovery of Novel Therapeutics for the Treatment of Malaria
11. Protalix BioTherapeutics Treats First Patient in Phase III Clinical Trial of prGCD
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:12/17/2009)... Dec. 17 Decision Resources, one of ... on pharmaceutical and healthcare issues, finds that over ... is a high need for diabetes drugs with ... say there is a high need for additional ... agents with excellent glucose lowering ability and physicians ...
(Date:12/17/2009)... Dec. 17 The Make-A-Wish Foundation announced ... donation from the LATISSE ® ... by Allergan, Inc. ,, Based on the tradition ... wish come true, the campaign launched earlier this ... Make-A-Wish Foundation by leveraging the excitement around the ...
(Date:12/16/2009)... Today, a group of national medical societies launched a ... Patient Protection and Affordable Care Act, currently under consideration ... a final vote in the coming days. The ... against a health care bill that is "bad medicine" ... our health care system needs reform - but the ...
Breaking Medicine Technology:Over 70 Percent of Physicians Say There Is a High Need for More Diabetes Drugs with Novel Mechanisms of Action While 15 Percent Say the Same for DPP-IV Inhibitors 2Over 70 Percent of Physicians Say There Is a High Need for More Diabetes Drugs with Novel Mechanisms of Action While 15 Percent Say the Same for DPP-IV Inhibitors 3The Make-A-Wish Foundation(R) Receives $1 Million Donation from LATISSE(R) Wishes Campaign 2The Make-A-Wish Foundation(R) Receives $1 Million Donation from LATISSE(R) Wishes Campaign 3The Make-A-Wish Foundation(R) Receives $1 Million Donation from LATISSE(R) Wishes Campaign 4The Make-A-Wish Foundation(R) Receives $1 Million Donation from LATISSE(R) Wishes Campaign 5Physician Groups Oppose Current Senate Health Care Reform Bill 2Caraco Pharmaceutical Laboratories Ltd Markets Generic Acular 28R 29 Opthalmic Solution 6042 1Caraco Pharmaceutical Laboratories Ltd Markets Generic Acular 28R 29 Opthalmic Solution 6042 2Health Fears Are Nothing to Sneeze At 60820 1Health Fears Are Nothing to Sneeze At 60820 2Health Fears Are Nothing to Sneeze At 60820 3New E Book Addresses LGBTQ Issues in the Education of Healthcare Professionals 60816 1New E Book Addresses LGBTQ Issues in the Education of Healthcare Professionals 60816 2New E Book Addresses LGBTQ Issues in the Education of Healthcare Professionals 60816 3
... Inc. (Nasdaq: VNDA ) announced today that ... the U.S. Food and Drug Administration (FDA),for iloperidone, ... The application includes data from 35 clinical,trials and ... Iloperidone has demonstrated efficacy in treating the symptoms ...
... Dosage form is Patient Friendly ... -, BOTHELL, Wash., Sept. 26 Nastech,Pharmaceutical Company ... of a,Phase 2 clinical trial evaluating the Company,s rapid-acting ... diabetes. The study is a,randomized, crossover study evaluating formulations ...
Other Medicine Technology:Vanda Pharmaceuticals Submits Iloperidone New Drug Application 2Vanda Pharmaceuticals Submits Iloperidone New Drug Application 3Vanda Pharmaceuticals Submits Iloperidone New Drug Application 4Nastech Pharmaceutical Company Announces Initiation of Phase 2 Clinical Trial for Insulin Nasal Spray to Treat Diabetes 2Nastech Pharmaceutical Company Announces Initiation of Phase 2 Clinical Trial for Insulin Nasal Spray to Treat Diabetes 3
(Date:12/17/2009)... Iraq, U.S. Air Force pediatric surgeon Dr. Chris Coppola scrubbed in ... and bleeding in the swollen right lobe of his brain. Now, ... a non-military effort to provide medical aid to children living in ... ... December 17, 2009 -- , , ,During his first night ...
(Date:12/17/2009)... neck and low back pain is now available in Rockville and ... nerve problems. Patients sometimes even fall asleep during their treatment. ... ... sufferers from all over Maryland can now rejoice as The Spinal ... save and improve degenerated discs., , ,Humans are constantly under pressure ...
(Date:12/17/2009)... ATLANTA, Dec. 17 Today, CDC,s Morbidity ... showing that the number of state-level epidemiologists has ... of over 10% since 2006. There was also ... this same period, including epidemiology capacity for bioterrorism ... subject areas such as occupational health, substance abuse, ...
(Date:12/17/2009)... The National Council on Disability ... JW Marriott Houston, 5150 Westheimer, Houston, TX, beginning at ... at 11:00 a.m. on Thursday, January 21, 2010. This ... believes it is vital to hear from communities around ... for people with disabilities. This meeting will provide another ...
(Date:12/17/2009)... December 17, 2009 Racial and ethnic disparities ... can be detected early and treated successfully, including ... by researchers at Columbia University,s Mailman School of ... (HICCC) at Columbia University Medical Center/NewYork-Presbyterian Hospital. ... have more limited early detection and treatment options, ...
Breaking Medicine News(10 mins):Health News:U.S. Pediatric Surgeon Heals War's Youngest Victims in Iraq, Donates Medical Aid to Displaced Children in Kabul, Afghanistan 2Health News:U.S. Pediatric Surgeon Heals War's Youngest Victims in Iraq, Donates Medical Aid to Displaced Children in Kabul, Afghanistan 3Health News:Rockville and Gaithersburg Now Has Spinal Decompression Therapy 2Health News:Rockville and Gaithersburg Now Has Spinal Decompression Therapy 3Health News:CSTE National Assessment Finds Critical Public Health Disease Surveillance Capacity Lacking 2Health News:National Council on Disability to Hold Houston Meeting to Hear Issues Affecting People With Disabilities 2Health News:Cancer survival disparities for most minority populations increase as cancers become more treatable 2
... calories and have higher heart rates, researchers say , , ... video games, and playing active versions of these games ... Hong Kong researchers report. , In fact, children ... burn four times as many calories a minute than ...
... with medication, appears effective in stabilizing symptoms of ... a report in the September issue of ... JAMA/Archives journals. , Between one-half and two-thirds of ... age 18, according to background information in the ...
... ... - World Vision,s emergency supplies ready in Mississippi, Dallas; more on ... community "on the frontlines" helping vulnerable, ... low-income families, SEATTLE, Sept. 1 As Hurricane Gustav lashes,Louisiana ...
... is available in Spanish . , The ... by Dr. Leo Kanner of the Johns Hopkins Hospital (USA), ... same time an Austrian scientist, Dr. Hans Asperger, described a ... Syndrome, characterised by higher cognitive abilities and more normal language ...
... DALLAS, Sept. 1 Susan G. Komen for ... movement, and its sister organization,the Susan G. Komen ... to educate attendees of the Republican National Convention,about ... access to,screening and treatment for the uninsured and ...
... Reel Lives: The Cancer Chronicles Film Festival awards prizes to top ... ... from Switzerland has been,awarded the Grand Prize in the first ever Reel ... prizes were,also awarded to The Truth About Cancer (USA) for Best Reportage, ...
Other Medicine News:Health News:Active Video Games Help Kids Exercise 2Health News:Active Video Games Help Kids Exercise 3Health News:Family therapy helps relieve depression symptoms in bipolar teens 2Health News:Gustav: World Vision Teams Assist Evacuees in Jackson and Dallas, Prepare Response 2Health News:Gustav: World Vision Teams Assist Evacuees in Jackson and Dallas, Prepare Response 3Health News:The first autism disease genes 2Health News:The first autism disease genes 3Health News:The first autism disease genes 4Health News:The first autism disease genes 5Health News:Komen Travels to Republican Convention to Raise Awareness of Breast Cancer Issues 2Health News:Chrigu Wins Grand Prize at First Ever International Documentary Film Festival on Cancer 2Health News:Chrigu Wins Grand Prize at First Ever International Documentary Film Festival on Cancer 3Health News:Chrigu Wins Grand Prize at First Ever International Documentary Film Festival on Cancer 4
... The rHead Radial Implant System ... anatomic solution to radial head replacement. ... address varied patient anatomy while minimizing ... A uniquely designed alignment guide assists ...
For use in implant arthroplasty associated with comminuted fractures, or rheumatoid, degenerative or post-traumatic disease of the radial head. Designed for higher demand patients requiring superior ...
For connection to the bipolar output of electrosurgical generators....
This legless table has adjustable height and blade post. Includes standard 2" (5 cm) pad....
Medicine Products: