Navigation Links
Scientists Explore ‘muscle’ in a New Drug to Assuage Muscular Dystrophy Symptos

Muscular dystrophy is a debilitating cluster of genetic disorders that weaken the muscles to such an extent, ultimately crushing the victim’s mobility. The disorder// hampers the victim’s quality of life, while also reducing the lifespan.

Unfortunately, the cure for this disorder still remains a burning ambition for many scientists. Duchenne Muscular Dystrophy or DMD is the most notorious of muscular dystrophy disorders. Sadly, almost 100 male children are born with this crippling disorder each year.

An experimental drug has raised scientists’ hope in being able to repair the genetic aberration, so typical among victims of Duchenne Muscular Dystrophy. The drug PTC124 proved its mettle in repairing the lost muscle function during experiments conducted on rodents. Human trial for this drug is underway, though it might take a while before the results are out.

The drug sets about the repair process by enabling cells to decipher anomalies in the genetic code pertaining to a specific protein called dystrophin. This protein is absent in 15% of patients suffering Duchenne Muscular Dystrophy. In mice, the drug assisted in superseding the mutation in the dystrophin gene, which obstructs the production of the protein.

Expressing optimism over the potential of the new drug, lead researcher Dr H Lee Sweeney said, "This new class of treatment has the potential to help a large number of patients with different genetic diseases that have the same type of mutation."

Dr Marita Pohlschmidt, director of research at the Muscular Dystrophy Campaign, extremely happy with the results of this drug said, “This drug appears to have the potential to become a treatment in the longer term for some people with DMD. We look forward to the publication of the full results of these clinical trials so that we can see more clearly what the prospects and possible timescales are for treatment.”
SV/V
'"/>




Page: 1

Related medicine news :

1. Scientists plan human cloning clinic in the United States
2. Scientists found ancient Human Germ Killer
3. Scientists locate key hormone involved in appetite control
4. Scientists open the book of life
5. Scientists review SARS
6. Scientists crack dengue fever puzzle
7. Scientists push to lower hidden sodium in food
8. Indian Scientists Make Wide-Ranging Analysis And Annotation Of X Chromosome
9. Scientists have found effective brain regions for deep brain stimulation for Parkinson’s
10. Scientists reveal the secrets of sarcasm
11. Scientists Unveil Mechanism Behind Resistance to Severe Malaria
Post Your Comments:
*Name:
*Comment:
*Email:


(Date:4/21/2017)... ... April 21, 2017 , ... Contrary to popular ... violence is declining—and at noteworthy rates. Between 2002 and 2014, Salas-Wright and his ... in violence in the United States. The study, Trends in Fighting and ...
(Date:4/21/2017)... PA (PRWEB) , ... April 21, 2017 , ... Dudnyk ... new identity emphasizes the agency’s conviction that the full potential of specialty and orphan ... are equally appreciated and aligned. , “The Unifying Effect is at the heart ...
(Date:4/21/2017)... ... 21, 2017 , ... Crossover Symmetry , an evidence ... active lifestyle company that provides Human Performance Training and education to tactical athletes. ... responders, military officers and others in service through the development and conditioning of ...
(Date:4/21/2017)... ... April 21, 2017 , ... Metrasens is honoured ... Trade, the UK’s most prestigious award for business success. The company has ... revenues and has grown by a total of 400% over the last six ...
(Date:4/21/2017)... (PRWEB) , ... April 21, 2017 , ... Yisrayl Hawkins, Pastor and Overseer at The ... world leaders in hopes of squashing a global crisis with solution to peace plan. Yisrayl ... to work because the plan is given by the Creator Himself. , Yisrayl says ...
Breaking Medicine News(10 mins):
(Date:4/20/2017)... 20, 2017 Research and Markets ... Pipeline and Market Prospects: Addressing Production Complexities Through Risk ... offering. ... "Global Biosimilar Pipeline and Market Prospects: Overcoming Production Complexities ... in-depth assessment of the current trends in the global ...
(Date:4/20/2017)... -- Research and Markets has announced the addition of ... Expanding Injectables Market and Increasing Usage of Complex Biologics during the ... ... from USD 20 Billion in 2015 to around USD 26 Billion ... Innovation Driven by Rapidly Expanding Injectables Market and Increasing Usage of ...
(Date:4/20/2017)... , April 20, 2017   ZappRx, Inc ., a ... drug prescribing process, today announced it closed $25 million in ... venture capital firm based in Seattle ... Venture Partners . The Series B round included participation from ... in 2014, and GV (formerly Google Ventures). As ...
Breaking Medicine Technology: