Navigation Links
Muscular Dystrophy May Be Cured By Gene Therapy

Muscular dystrophy may also be cured by a gene therapy technique which has been promising where hemophilia and skin diseases are concerned, according to the Stanford University School of Medicine researchers // . The gene dystrophin was introduced into mice by the researchers as a part of the experiment. According to Thomas Rando, MD, there is nothing new in using gene therapy for treating muscular dystrophy, as different techniques have already been used with varying degrees of success.

The gene therapy technique Rando and postdoctoral fellow Carmen Bertoni, PhD, used was developed by Michele Calos, PhD, associate professor of genetics. One of the main advantages of this method is that it could potentially provide a long-term fix for a variety of genetic diseases, including muscular dystrophy.

In muscular dystrophy, the muscle cells break down and are slowly replaced by fat. Eventually people with the disease are confined to a wheelchair and usually die in their 20s. There is currently no effective treatment for the disease, which explains why gene therapy remains a hope despite the significant hurdles.

Rando said the PNAS paper highlights an additional requirement for any gene therapy to be successful: the introduced gene must produce healthy dystrophin protein in large quantities in order to repair the entire muscle cell. Previous muscular dystrophy gene therapy studies did not look at whether the introduced dystrophin spread along the entire length of the muscle cell, which can be many millimeters long in mice or inches long in humans.

Edited (ANI)
'"/>




Page: 1

Related medicine news :

1. Hope for Babies Born With Spinal Muscular Atrophy
2. Gene Therapy Gives Hope For Patients With Muscular Dystrophy
3. The Use Of Oral Steroids For Muscular Dystrophy Questioned
4. Different Drug May Help Children With Duchenne Muscular Dystrophy
5. Hope For Patients With Muscular Dystrophy
6. Gene Therapy Overcomes Heart Failure In Muscular Dystrophy
7. Importance Of Early Diagnosis And Treatment For Muscular Dystrophy Patients
8. First Gene Therapy Human Trial For Muscular Dystrophy In Progress
9. Muscular Dystrophy Reversed In Lab Mice
10. Men Take to Unhealthy Practices to be More Muscular
11. Toxic Strand Of RNA Causes Myotonic Muscular dystrophy
Post Your Comments:
*Name:
*Comment:
*Email:


(Date:8/22/2017)... ... August 22, 2017 , ... “Call Of Spiritual Duty”: a revelation in an ... author, C.S. Lizarde. Growing up on the streets of North Visalia, California, Carlos ... to apply the Biblical keys to his life, he noticed immediately that opportunities and ...
(Date:8/21/2017)... City, NY (PRWEB) , ... August 22, 2017 ... ... honors Judith I. Stevens as a 2017-2018 inductee into its ... for leadership in entrepreneurship. NAPW is the nation’s leading networking organization exclusively for ...
(Date:8/21/2017)... ... August 21, 2017 , ... Five chefs from local ... for Alzheimer’s Family Center. , Guests will be able to vote for their ... Braised Lamb Shank with Fennel Dill Salad, Feta Cheese Sauce & Garlic Pita Crisp, ...
(Date:8/21/2017)... ... 2017 , ... PIXACORE , an independent full-service agency with a decade ... of the year by MM&M. , This is the first time PIXACORE has made ... the agency. PIXACORE’s newfound recognition reflects its steady trajectory of growth and recent ...
(Date:8/21/2017)... GA (PRWEB) , ... August 21, 2017 , ... The ... Design Excellence Awards (IDSA IDEA®) 2017 Ceremony and Gala on Aug. 19, 2017 ... in one of the world’s most prestigious and rigorous design competitions. See all the ...
Breaking Medicine News(10 mins):
(Date:8/7/2017)... -- Endo International plc (NASDAQ: ENDP ) today ... known U.S. mesh product liability claims and that it ... U.S. claims at reasonable values. Under the agreements, Endo ... of 2017 and continuing through the fourth quarter of ... the Company intends to increase its mesh product liability ...
(Date:8/3/2017)... 3, 2017  Opioid addiction and other drugs of ... costs and threatening outcomes, were problems taken on directly ... industry that support them, met this week. This according ... that drugs of abuse, procalcitonin and acute kidney injury ... organization,s 69th meeting in San Diego, CA. ...
(Date:8/2/2017)... -- Life Flight Network and PeaceHealth Oregon Network announced they renewed ... operational efficiency for patients at hospitals in Eugene ... Grove , and Florence, Oregon , ... Network work collaboratively to move patients who require the highest ... sensitive emergency exists. ...
Breaking Medicine Technology: