Navigation Links
Muscular Dystrophy May Be Cured By Gene Therapy

Muscular dystrophy may also be cured by a gene therapy technique which has been promising where hemophilia and skin diseases are concerned, according to the Stanford University School of Medicine researchers // . The gene dystrophin was introduced into mice by the researchers as a part of the experiment. According to Thomas Rando, MD, there is nothing new in using gene therapy for treating muscular dystrophy, as different techniques have already been used with varying degrees of success.

The gene therapy technique Rando and postdoctoral fellow Carmen Bertoni, PhD, used was developed by Michele Calos, PhD, associate professor of genetics. One of the main advantages of this method is that it could potentially provide a long-term fix for a variety of genetic diseases, including muscular dystrophy.

In muscular dystrophy, the muscle cells break down and are slowly replaced by fat. Eventually people with the disease are confined to a wheelchair and usually die in their 20s. There is currently no effective treatment for the disease, which explains why gene therapy remains a hope despite the significant hurdles.

Rando said the PNAS paper highlights an additional requirement for any gene therapy to be successful: the introduced gene must produce healthy dystrophin protein in large quantities in order to repair the entire muscle cell. Previous muscular dystrophy gene therapy studies did not look at whether the introduced dystrophin spread along the entire length of the muscle cell, which can be many millimeters long in mice or inches long in humans.

Edited (ANI)
'"/>




Page: 1

Related medicine news :

1. Hope for Babies Born With Spinal Muscular Atrophy
2. Gene Therapy Gives Hope For Patients With Muscular Dystrophy
3. The Use Of Oral Steroids For Muscular Dystrophy Questioned
4. Different Drug May Help Children With Duchenne Muscular Dystrophy
5. Hope For Patients With Muscular Dystrophy
6. Gene Therapy Overcomes Heart Failure In Muscular Dystrophy
7. Importance Of Early Diagnosis And Treatment For Muscular Dystrophy Patients
8. First Gene Therapy Human Trial For Muscular Dystrophy In Progress
9. Muscular Dystrophy Reversed In Lab Mice
10. Men Take to Unhealthy Practices to be More Muscular
11. Toxic Strand Of RNA Causes Myotonic Muscular dystrophy
Post Your Comments:
*Name:
*Comment:
*Email:


(Date:3/28/2017)... ... ... For many women, getting birth control isn’t as easy as it should be. In fact, ... to a health care facility or a pharmacy within 60 minutes of where they live. ... for many who are faced with health or personal issues that leave them homebound. To ...
(Date:3/28/2017)... ... March 28, 2017 , ... ... to be invited to the Siemens Healthineers annual customer education symposium, a world-class ... will take place from March 27 - 31, 2017 at the Atlanta Marriott ...
(Date:3/28/2017)... ... ... Isabella Wentz, PharmD, FASCP, one of the leading thyroid experts of the world, is ... about journey and research recently on a blog and discussed some major aspects of ... deal with thyroid disease. , Dr. Wentz completed her graduation from the Midwestern ...
(Date:3/28/2017)... ... March 28, 2017 , ... ... medical society dedicated to advancing the science and clinical practice of radiosurgery, ... RSSearch Patient Registry, a multi-institutional, observational registry established to standardize data collection ...
(Date:3/28/2017)... ... 28, 2017 , ... Z-Medica, LLC, a leading developer and ... (UPMC) will acquire QuikClot® Bleeding Control Kits® (BCK) to equip up to 1,000 ... efforts by the American College of Surgeons, U.S. Department of Defense, Department of ...
Breaking Medicine News(10 mins):
(Date:3/28/2017)... CITY, Calif. , March 28, 2017 /PRNewswire/ ... company focused on the development and commercialization of ... pain, announced that the European Medicines Agency (EMA) ... sublingual tablet, 30 mcg) Marketing Authorisation Application (MAA) ... of the MAA is underway. The MAA for ...
(Date:3/28/2017)... Mass. , March 28, 2017 ... company developing innovative therapeutics that address significant unmet ... a patent from the Japan Patent Office (JPO) ... connective tissue growth factor (CTGF) for the treatment ... limited to skin fibrosis and proliferative retinopathy (Japanese ...
(Date:3/28/2017)... , March 28, 2017 The ... reach USD 8.0 billion by 2025, according to a ... incidence of infectious diseases and cancer is expected to ... disease diagnosis over the coming years. In addition, higher ... autologous and allogenic stem cell therapy, due to adverse ...
Breaking Medicine Technology: