Navigation Links
Multiple organ disease cured by genes

Researchers University of Pennsylvania report the first ever use of gene therapy, in dogs, to cure a gene involving multiple body organs.// Mucopolysaccharidosis VII (MPS) is one of a group of rare genetic disorders called lysosomal storage diseases. Other examples include Tay Sachs disease and Gaucher disease. MPS involves an enzyme defect, leading to blindness, heart disease, and loss of mobility.

Most humans with MPS die in childhood. Researchers at the University of Pennsylvania have carried out the first ever gene therapy for MPS in dogs born with the disease. This introduces a healthy version of the defective enzyme, beta-glucuronidase, into the animals' liver. Treated dogs gained weight normally, compared to untreated animals, and showed none of the expected health problems.

This is the first time gene therapy has been used for a disease involving multiple organs. It could replace the standard treatment - which is to give injections of the missing enzyme. The therapy could also be used to treat other lysosomal storage diseases.


Page: 1

Related medicine news :

1. Naked DNA Vaccination May Conquer Arthritis and Multiple Sclerosis
2. Adult stem cells in treatment for Multiple sclerosis (MS)
3. Life Quality For Patients With Multiple Sclerosis
4. Effective Pain Relief For Patients Suffering From Multiple Sclerosis
5. The Link Between Hepatitis B Vaccine And Multiple Sclerosis Questioned
6. Hope For Patients With Multiple Sclerosis
7. Individuals Born In May At A Higher Risk Of Developing Multiple Sclerosis
8. Debating The Link Between Sex Hormones And Multiple Sclerosis
9. Warning Issued by FDA on consumption of the drug Tysabri used to treat Multiple Sclerosis
10. Decreasing Multiple Births By Single Embryo Transfers
11. Physicians Lack Clinical Guidelines For Treating Elderly With Multiple Illnesses
Post Your Comments:

(Date:6/24/2016)... , ... June 24, 2016 , ... Global law firm ... 2016 Legal Elite. The attorneys chosen by their peers for this recognition are considered ... Seven Greenberg Traurig Shareholders received special honors as members of this year’s Legal Elite ...
(Date:6/24/2016)... ... June 24, 2016 , ... Comfort Keepers® of San ... Society and the Road To Recovery® program to drive cancer patients to and from ... adults to ensure the highest quality of life and ongoing independence. Getting to ...
(Date:6/24/2016)... ... June 24, 2016 , ... People across the U.S. are sharpening their ... Award, an essay contest in which patients and their families pay tribute to a ... the 2016 National Society of Genetic Counselors (NSGC) Annual Education Conference (AEC) this September. ...
(Date:6/24/2016)... York, NY (PRWEB) , ... June 24, 2016 ... ... publication Haute Living, is proud to recognize Dr. Barry M. Weintraub as a ... that “the most beautiful women in the world, and the most handsome men, ...
(Date:6/24/2016)... ... June 24, 2016 , ... Strategic Capital Partners, LLC ... by obtaining investment capital for emerging technology companies. SCP has delivered investment ... resulted in more than a million dollars of capital investment for five companies. ...
Breaking Medicine News(10 mins):
(Date:6/24/2016)... -- Dehaier Medical Systems Ltd. (NASDAQ: DHRM ... sells medical devices and wearable sleep respiratory products in ... agreement with Hongyuan Supply Chain Management Co., Ltd. (hereinafter ... 2016, to develop Dehaier,s new Internet medical technology business. ... leverage Hongyuan Supply Chain,s sales platform to reach Dehaier,s ...
(Date:6/24/2016)... 24, 2016 According to a ... (Standard Pen Needles, Safety Pen Needles), Needle Length (4mm, ... Hormone), Mode of Purchase (Retail, Non-Retail) - Trends & ... studies the market for the forecast period of 2016 ... 2.81 Billion by 2021 from USD 1.65 Billion in ...
(Date:6/24/2016)... Tenn. , June 24, 2016  Arkis ... providing less invasive and more durable cerebrospinal fluid ... in funding.  The Series-A funding is led by ... Lighthouse Fund, and other private investors.  Arkis, new ... neurosurgical instrumentation and the market release of its ...
Breaking Medicine Technology: