Navigation Links
Multiple organ disease cured by genes

Researchers University of Pennsylvania report the first ever use of gene therapy, in dogs, to cure a gene involving multiple body organs.// Mucopolysaccharidosis VII (MPS) is one of a group of rare genetic disorders called lysosomal storage diseases. Other examples include Tay Sachs disease and Gaucher disease. MPS involves an enzyme defect, leading to blindness, heart disease, and loss of mobility.

Most humans with MPS die in childhood. Researchers at the University of Pennsylvania have carried out the first ever gene therapy for MPS in dogs born with the disease. This introduces a healthy version of the defective enzyme, beta-glucuronidase, into the animals' liver. Treated dogs gained weight normally, compared to untreated animals, and showed none of the expected health problems.

This is the first time gene therapy has been used for a disease involving multiple organs. It could replace the standard treatment - which is to give injections of the missing enzyme. The therapy could also be used to treat other lysosomal storage diseases.


'"/>




Page: 1

Related medicine news :

1. Naked DNA Vaccination May Conquer Arthritis and Multiple Sclerosis
2. Adult stem cells in treatment for Multiple sclerosis (MS)
3. Life Quality For Patients With Multiple Sclerosis
4. Effective Pain Relief For Patients Suffering From Multiple Sclerosis
5. The Link Between Hepatitis B Vaccine And Multiple Sclerosis Questioned
6. Hope For Patients With Multiple Sclerosis
7. Individuals Born In May At A Higher Risk Of Developing Multiple Sclerosis
8. Debating The Link Between Sex Hormones And Multiple Sclerosis
9. Warning Issued by FDA on consumption of the drug Tysabri used to treat Multiple Sclerosis
10. Decreasing Multiple Births By Single Embryo Transfers
11. Physicians Lack Clinical Guidelines For Treating Elderly With Multiple Illnesses
Post Your Comments:
*Name:
*Comment:
*Email:


(Date:10/12/2017)... ... October 12, 2017 , ... ... for healthcare compliance program management, will showcase a range of technology and learning ... Assisted Living (NCAL) Convention and Expo to be held October 14–18, 2017 at ...
(Date:10/12/2017)... ... October 12, 2017 , ... IsoComforter, Inc. ( https://isocomforter.com ... the introduction of an innovative new design of the shoulder pad. The shoulder ... maximum comfort while controlling your pain while using cold therapy. By utilizing ice and ...
(Date:10/12/2017)... , ... October 12, 2017 , ... ... Hair Restoration, has recently contributed a medical article to the newly revamped ... Dr. Mohebi’s article spotlights the hair transplant procedure known as Follicular Unit ...
(Date:10/12/2017)... ... October 12, 2017 , ... Women-owned and ... 2017 Best and Brightest in Wellness® by Best and Brightest. OnSite Wellness will ... Friday, Oct. 20 from 7:30 a.m. to 2 p.m. at the Henry Autograph ...
(Date:10/12/2017)... D.C. (PRWEB) , ... October 12, 2017 , ... ... Cal Dining at the University of California Berkeley, and other leading institutions in ... the buying power of institutions to change the way animals are raised for ...
Breaking Medicine News(10 mins):
(Date:9/28/2017)... , Sept. 28, 2017 Cohen Veterans Bioscience ... the use of wearable and home sensors for real-time ... Early Signal Foundation, a nonprofit organization focused on disruptive ... provide an affordable analytical system to record and integrate ... ...
(Date:9/25/2017)... R.I. , Sept. 25, 2017  EpiVax, ... assessment, vaccine design, and immune-engineering today announced the ... on the development of personalized therapeutic cancer vaccines. ... has provided exclusive access to enabling technologies to ... Eng., MBA will lead EpiVax Oncology as Chief ...
(Date:9/19/2017)... venture-backed medical device company developing a non-invasive, robotically assisted, platform therapy that uses pulsed sound ... ... Jim Bertolina, PhD ... Tom Tefft ... device executive Josh Stopek , PhD, who has led R&D and business development teams ...
Breaking Medicine Technology: