Navigation Links
Multiple organ disease cured by genes

Researchers University of Pennsylvania report the first ever use of gene therapy, in dogs, to cure a gene involving multiple body organs.// Mucopolysaccharidosis VII (MPS) is one of a group of rare genetic disorders called lysosomal storage diseases. Other examples include Tay Sachs disease and Gaucher disease. MPS involves an enzyme defect, leading to blindness, heart disease, and loss of mobility.

Most humans with MPS die in childhood. Researchers at the University of Pennsylvania have carried out the first ever gene therapy for MPS in dogs born with the disease. This introduces a healthy version of the defective enzyme, beta-glucuronidase, into the animals' liver. Treated dogs gained weight normally, compared to untreated animals, and showed none of the expected health problems.

This is the first time gene therapy has been used for a disease involving multiple organs. It could replace the standard treatment - which is to give injections of the missing enzyme. The therapy could also be used to treat other lysosomal storage diseases.


'"/>




Page: 1

Related medicine news :

1. Naked DNA Vaccination May Conquer Arthritis and Multiple Sclerosis
2. Adult stem cells in treatment for Multiple sclerosis (MS)
3. Life Quality For Patients With Multiple Sclerosis
4. Effective Pain Relief For Patients Suffering From Multiple Sclerosis
5. The Link Between Hepatitis B Vaccine And Multiple Sclerosis Questioned
6. Hope For Patients With Multiple Sclerosis
7. Individuals Born In May At A Higher Risk Of Developing Multiple Sclerosis
8. Debating The Link Between Sex Hormones And Multiple Sclerosis
9. Warning Issued by FDA on consumption of the drug Tysabri used to treat Multiple Sclerosis
10. Decreasing Multiple Births By Single Embryo Transfers
11. Physicians Lack Clinical Guidelines For Treating Elderly With Multiple Illnesses
Post Your Comments:
*Name:
*Comment:
*Email:


(Date:3/24/2017)... ... March 24, 2017 , ... Empower Brokerage, ... their training and leads programs. , In February, 2017, Empower Brokerage introduced their ... Performance Partners is designed to teach how to maximize their sales efforts, as ...
(Date:3/24/2017)... ... March 24, 2017 , ... “Finding Christ Through Social Media: ... journal chronicling the writer’s path toward true communion with God. “Finding Christ Through ... is the creation of published author Lea Michelle Johnson, a follower of Christ, ...
(Date:3/24/2017)... (PRWEB) , ... March 24, 2017 , ... “Vintage and ... a retired minister and college Bible teacher residing in North Carolina with his wife, ... who have blessed them with six grandchildren. David is also the author of “Shadow ...
(Date:3/24/2017)... ... ... “The Adventures of Joey, The Dog Who Barks at Puddles”: a boisterous story ... fullest, as God intended. “The Adventures of Joey, The Dog Who Barks at Puddles” ... passion for writing, especially about truth and human behavior. , Published by Christian Faith ...
(Date:3/23/2017)... ... ... A recent report from the National Council on Teacher Quality (NCTQ) advocates for ... on a review of GPA and SAT/ACT requirements at 221 institutions in 25 states, ... that this higher bar should be set by states, by the Council for the ...
Breaking Medicine News(10 mins):
(Date:3/24/2017)... ShangPharma, a leading life science ... development and discovery services, technology, and investment ... today the intent for a strategic corporate ... the Contract Research Organizations (CRO) and Contract ... entities include ChemPartner Shanghai, ChemPartner Fengxian, ChemPartner ...
(Date:3/24/2017)... , March 24, 2017 A ReportsnReports.com ... has been growing rapidly as the global sales of Adcetris and ... growth in the antibody drug conjugates market is driven by large ... cancer and wider therapeutic window offered by ADCs. ... Browse 3 Tables and 94 Figures, ...
(Date:3/24/2017)... 24, 2017  Eli Lilly and Company (NYSE: ... invest $850 million in its U.S. operations in ... U.S. enterprise, including research laboratories, manufacturing sites, and ... driven by demand for Lilly products, as well ... development targeting cancer, pain, diabetes and other unmet ...
Breaking Medicine Technology: