Navigation Links
Gene Therapy Technique for Inherited Heart Problems in The Pipeline

with scientists at the California National Primate Research Center at the University of California at Davis showed that AAV-9 easily passes into the heart muscle in primates after a single intravenous injection, and the effects are long lasting. ‘AAV-9 had a particular affinity for heart muscle that AAV-8 didn't,’ Byrne said. ‘Right now AAV-9 seems to be our best solution for heart problems. ‘The primates were done to give us insight into how this could be used in children,’ he said, adding that UF researchers hope to launch a trial in patients with Pompe disease early next year. ‘Many of the inborn errors have their most feared effects early in life, so we're pushing toward being able to do prevent disease as opposed to trying to correct later. We keep trying to get closer and closer to clinical studies that will help patients-that's the real goal.’

R. Jude Samulski, Ph.D., director of the Gene Therapy Center at the University of North Carolina-Chapel Hill, said each viral type is ‘like a FedEx truck that carries a ZIP code that determines where the truck is going to take its payload to.’ ‘Laboratories are engineering new ZIP codes onto these vectors so they can try to control where they go,’ he said. Then they become more like a traditional drug that has these properties and only these properties. We're using templates out in Mother Nature as our blueprint. Once we learn these places where they work, then we can strategically control them and use them for our advantage. It's an exciting time in this area. ‘I equate it to the space program,’ he added. ‘We don't know who Neil Armstrong is yet, who's going to be the one to make this work, but we know we're going to the moon. Everybody engineering things is part of that effort. What Barry has done is more significant than what people imagined. It's close to the Holy Grail when you get it to work in small animals and then you get it to work in large animals. What you have left is to go into humans. It's real
'"/>




Page: 1 2 3 4

Related medicine news :

1. Cancer Doctors Okays Controversial Prostate Therapy
2. Consensus on "Combination Therapy" for Breast Cancer
3. Gene Therapy shows promise in treating Hemophilia
4. "Make AIDS Therapy affordable" - Physicians demand
5. Hormone replacement Therapy a headache
6. Simple Therapy
7. Therapy for stopping the spread of cancer cells
8. Gene Therapy Destroys Pancreatic Cancer Cells
9. Letrozole Beats Tamoxifen in Breast Cancer Therapy
10. Garlic Supplements Impede HIV Therapy
11. Gene Therapy For Cystic Fibrosis
Post Your Comments:
*Name:
*Comment:
*Email:
TAG: Gene Therapy Technique for Inherited Heart Problems The Pipeline

(Date:12/25/2014)... 2014 The report “TS-1 (Colorectal Cancer) ... the current treatment landscape, unmet needs, current pipeline and ... an anti-cancer drug which is typically used for treating ... used for treating gastric cancer and pancreatic cancer. TS-1 ... drug was first approved in 1999 in Japan for ...
(Date:12/25/2014)... Recently, Dylan Queen, a famous online company ... collection of discounted prom dresses, most of which are ... of the company, the promotion is valid until Jan. ... expand the UK market. , The prom dresses in ... and styles: A-line strapless, empire strapless chiffon, one shoulder, ...
(Date:12/25/2014)... Helen Harris’ RP (Retinitis Pigmentosa) International founder ... an 8 year battle with breast cancer. , ... her home in Woodland Hills California after an 8 ... , As the founder and volunteer President of ... championed many of today's greatest breakthroughs in restoring and ...
(Date:12/25/2014)... 25, 2014 (HealthDay News) -- The risk of burns ... so you need to be extra cautious, an expert ... see a significant increase in patients coming in with ... Suffolk County Volunteer Firefighters Burn Center of Stony Brook ... be full of joy, but if not careful, could ...
(Date:12/25/2014)... AngelWeddingDress.com tries its best to translate the experience of ... has introduced its new collection of 2015 prom dresses, ... new prom outfits are guaranteed to contain the perfect ... specially designed for 2015. Anyone who wants to buy ... website before Jan. 26, 2015, the deadline of the ...
Breaking Medicine News(10 mins):Health News:TS-1 Colorectal Cancer Market Analysis and Forecast to 2023 Report at RnRMarketReserach.com 2Health News:TS-1 Colorectal Cancer Market Analysis and Forecast to 2023 Report at RnRMarketReserach.com 3Health News:Dylan Queen: Cheap Prom Dresses for the UK Market 2Health News:RP International founder, Helen Harris Dies on Christmas Eve Just Hours Before Her Holiday Television Broadcast to Raise Funds to Cure Blindness was Broadcasted Nationally 2Health News:RP International founder, Helen Harris Dies on Christmas Eve Just Hours Before Her Holiday Television Broadcast to Raise Funds to Cure Blindness was Broadcasted Nationally 3Health News:RP International founder, Helen Harris Dies on Christmas Eve Just Hours Before Her Holiday Television Broadcast to Raise Funds to Cure Blindness was Broadcasted Nationally 4Health News:Don't Let Burns Mar Your Holidays 2Health News:Angelweddingdress 2015 Prom Dresses Online Now 2
... SAN DIEGO, Dec. 13 BioMed Realty Trust, Inc.,(NYSE: ... directors has declared a,fourth quarter 2007 dividend of $0.31 ... an annualized dividend of $1.24 per common share., ... declared a,dividend of $0.46094 per share of the company,s ...
... to persist with using creams, supplements and plastic surgery to ... new research says. , A study of 297 women ... more motivated to persist with special diets, vitamins, creams, Botox ... failed to make them look significantly younger. , The ...
... The HealthCentral,Network, Inc. ( http://www.HealthCentral.com ) has ... for its breast cancer site,MyBreastCancerNetwork.com, and its ... health industry innovation on the Web, the ... consumer disease-focused site.,MyBreastCancerNetwork.com won a Gold Award ...
... savings for,improving Medicare program; National Kidney Foundation, Renal ... submit letters to,Capitol Hill in favor of ESRD ... --,a coalition of patient advocates, dialysis professionals, care ... care for,individuals with chronic kidney disease -- and ...
... lead to new treatments for sleep disorders ... switch that activates the genetic mechanism regulating the body,s ... Irvine, researchers. , They added that the switch offers ... treat sleep disorders and related problems. , The study ...
... delivered today at a press conference hosted by ... agreement with Independent,Health, BUFFALO, N.Y., Dec. 12 ... Nielsen, M.D., AMA President-elect:, "The American Medical ... care, and initiatives that measure and compare physician,performance ...
Cached Medicine News:Health News:BioMed Realty Trust Declares Fourth Quarter 2007 Common Stock and Preferred Stock Dividends 2Health News:Women persist in plastic surgery treatments that are not working, research says 2Health News:The HealthCentral Network Wins eHealthcare Awards for Breast Cancer and Migraine Web Sites 2Health News:Kidney Patient Organizations, Kidney Community Come Out in Support of Medicare Secondary Payer (MSP) Extension 2Health News:Kidney Patient Organizations, Kidney Community Come Out in Support of Medicare Secondary Payer (MSP) Extension 3Health News:AMA Commends Independent Health for Joining Industry Shift on Physician Performance Measurement 2
(Date:12/24/2014)... RALEIGH, N.C. , Dec. 23, 2014 /PRNewswire/ ... (NASDAQ: ENDP ) (TSX: ENL), and BioDelivery ... today that they have submitted a New Drug Application ... Food and Drug Administration (FDA).  Buprenorphine HCl Buccal Film ... enough to require daily, around-the-clock, long-term opioid treatment and ...
(Date:12/22/2014)... , Dec. 22, 2014 NxStage Medical, ... of innovative dialysis products, announced today that the ... its System One™ to perform hemodialysis overnight while ... home nocturnal hemodialysis. NxStage,s® System One is the ... FDA for this indication. Home ...
(Date:12/22/2014)... , Dec. 22, 2014   TRU-D SmartUVC ... no-touch UV disinfection robot, announced today that the General ... contract through November 2019.   This newly ... engage all levels of government purchasers, including Department of ... well as Homeland Security contacts purchasing solutions for the ...
Breaking Medicine Technology:Endo Pharmaceuticals and BioDelivery Sciences Announce NDA Submission for Buprenorphine HCl Buccal Film for the Management of Moderate to Severe Chronic Pain 2Endo Pharmaceuticals and BioDelivery Sciences Announce NDA Submission for Buprenorphine HCl Buccal Film for the Management of Moderate to Severe Chronic Pain 3Endo Pharmaceuticals and BioDelivery Sciences Announce NDA Submission for Buprenorphine HCl Buccal Film for the Management of Moderate to Severe Chronic Pain 4Endo Pharmaceuticals and BioDelivery Sciences Announce NDA Submission for Buprenorphine HCl Buccal Film for the Management of Moderate to Severe Chronic Pain 5NxStage Receives FDA Clearance for Home Nocturnal Hemodialysis 2NxStage Receives FDA Clearance for Home Nocturnal Hemodialysis 3TRU-D SmartUVC LLC Awarded General Services Administration Contract to Expand Government Customer Base 2
... acute lymphoblastic,leukemia combined with molecular science could help ... MEMPHIS, Tenn., March 20 The dramatic,increase that ... with acute,lymphoblastic leukemia (ALL) will be difficult to ... to an article,by St. Jude Children,s Research Hospital ...
... 20 NanoBio Corporation,announced today that it has ... phase 2 study of NB-002, a topical lotion ... the results clearly,justify completing the study, according to ... to grow out a clear nail after,successfully treating ...
Cached Medicine Technology:Molecular Science Could Further Improve Leukemia Survival, Say St. Jude Researchers 2NanoBio Corporation Completes Interim Analysis of Phase 2 Clinical Trial in Onychomycosis 2
... to optimize the accuracy and precision of ... is widely recognized by customers throughout the ... over the years and now covers a ... including filter tips, certified pure tips, stepper ...
... Finntips have been designed to optimize ... quality of our tip products is widely ... Finntip range has been extended over the ... of standard and special tips including filter ...
... plastic-wrapped racks of 96 tips, Sterilized Diamond- ... autoclave. Sterilized Diamond Tips are irradiated by ... delivered with a certificate of sterilization, specifying ... are certified free of detectable Rnase, Dnase, ...
... conveniently in plastic-wrapped racks of 96 tips, ... need to autoclave. Sterilized Diamond Tips are ... and are delivered with a certificate of ... Diamond Tips are certified free of detectable ...
Medicine Products: