Navigation Links
Cure For Pompe Disease

Pompe disease is a rare inherited enzyme deficiency that destroys muscles and can kill infants at a very young age. Myozyme is a drug developed by Genzyme// to treat this disease. Genzyme, a biotechnology company in Cambridge, Mass said that it has spent more than $500 million since 1998 to develop Myozyme.

It has also received incentives provided by the federal government to develop medicines against such disease collectively called orphans disease. The drug after passing through a variety of tests and trails has won the federal approval to sell the drug in the market. Genzyme officials said that the dug Myozyme, would cost about $200,000 to $300,000 a year. The disease incidence is less than 10000 people and they are all grateful for Genzyme's drugs. Genzyme said that it will provide the drug free of cost to those who cannot pay for it. During the clinical trail from 2003-05 the drug was administered to 18 infants.

They all lived until they were at least 18 months old, or about a year after starting treatment, and most are still alive today. The warning on the drug label says that Myozyme can also cause life-threatening anaphylactic or allergic reactions. Dr. David Meeker, president of the Genzyme division that developed Myozyme said that a new blood test was offered to diagnose the disease rapidly which could lead to earlier treatment with better outcome. But further tests are necessary to determine the effect of the drug against Pompe disease that begins later in childhood or in adulthood.


'"/>




Page: 1

Related medicine news :

1. Transdermal HRT not cardioprotective in postmenopausal women with Coronary Artery Disease
2. Vitamins-The answer to Heart Disease?
3. Link between Constipation and Parkinsons Disease
4. Levels Of Blood Proteins May Help Heart Disease Care
5. New Drug PP188 Helps Sickle Cell Disease
6. Gene Treatment for Heart Disease
7. Legume Consumption Can Cut Heart Disease Risk
8. Link Between Infection And Heart Disease
9. Celiac Disease in Type 1 Diabetes
10. Shunt for Alzheimers Disease
11. High iron levels may cause Cardiovascular Disease in women
Post Your Comments:
*Name:
*Comment:
*Email:
TAG: Cure For Pompe Disease

(Date:8/31/2015)... ... August 31, 2015 , ... Move over shave cream. Roll ... and barbershops are scrambling to meet it. , Reports published this year (Mintel data) ... haircare. But the data also reflects that men are getting more done at barbershops ...
(Date:8/31/2015)... ... August 31, 2015 , ... ... (ACLM), the nation’s medical professional association for physicians and allied health professionals ... the Lifestyle Medicine Foundation, announced today the establishment of the Lifestyle Medicine ...
(Date:8/31/2015)... , ... August 31, 2015 , ... ... in and around Grand Prairie, is teaming up with the Tarrant County chapter ... area. , Meals on Wheels is the oldest and largest national organization that ...
(Date:8/31/2015)... ... August 31, 2015 , ... Chicago-based company The Mood ... to raise money and awareness for breast and ovarian health. During September ... incandescent Mood-lite sold to Bright Pink® to encourage households, dorms, and offices around ...
(Date:8/31/2015)... Los Angeles, ACA (PRWEB) , ... August 31, 2015 , ... ... filling a growing niche in the digital healthcare industry. , Consumer driven health ... the field: one in an advisory and strategic role to the company, and another ...
Breaking Medicine News(10 mins):Health News:MENAJI Anti-Aging Eraser a New Sure-Fire Add-On Product for Barbershops 2Health News:MENAJI Anti-Aging Eraser a New Sure-Fire Add-On Product for Barbershops 3Health News:Nominations Sought for Awards Recognizing Exemplary Contribution to the Field of Lifestyle Medicine 2Health News:Nominations Sought for Awards Recognizing Exemplary Contribution to the Field of Lifestyle Medicine 3Health News:Westchester Insurance and the Meals on Wheels Association Announce Joint Charity Effort to Provide Nutritious Meals for Senior Citizens 2Health News:Westchester Insurance and the Meals on Wheels Association Announce Joint Charity Effort to Provide Nutritious Meals for Senior Citizens 3Health News:Mood-lites® is proud to launch “Brighten Our World" Campaign to Raise Money and Awareness for Breast and Ovarian Health Across America in Partnership with Bright Pink® 2Health News:Mood-lites® is proud to launch “Brighten Our World" Campaign to Raise Money and Awareness for Breast and Ovarian Health Across America in Partnership with Bright Pink® 3Health News:ZendyHealth Adds Two Prestigious Consumer Driven Health Plan (CDHP) Experts 2Health News:ZendyHealth Adds Two Prestigious Consumer Driven Health Plan (CDHP) Experts 3
... in the February issue of Radiology, a novel type ... in identifying blockages// in the arteries that carry blood ... provided highly accurate information about the supra-aortic arteries," said ... the David Geffen School of Medicine at UCLA in ...
... increase of HIV cases in Australia has prompted the government ... disease//. Gay sex has been found out to be main ... island continent. ,According to a study, there is ... a disturbing scenario. Health ministry is planning to spend $10 ...
... been granted ?25,000 for helping blind and partially sighted people ... National Institute for the Blind (RNIB) received a ?25,000 donation// ... launching the charity's Positive Steps programme, which provides motivational training ... will be conducted for those who are over 17 years ...
... leading public health experts said that NHS should consider ... charges//. Patients should contribute towards the cost of ... Tim Crayford, president of the Association of Directors of ... to be controlled and people should help pay for ...
... improve their smile but there is no guarantee of happiness ... results were published in the British Journal of Health Psychology. ... study looked at the impact of braces on more than ... little positive impact on their psychological health later in life. ...
... patients conclude that placing stents in carotid arteries to prevent ... at Sacred Heart Medical Center in Spokane, Washington by lead ... 37 stroke patients on whom the procedure was performed. ... reported an improvement in reasoning, memory and judgment. ...
Cached Medicine News:Health News:MR Angiography Detects Blocked Arteries Accurately 2
(Date:8/28/2015)... , Aug. 28, 2015  With the heroin ... reaching deadlier heights, Jacksonville -based Lakeview ... Hemphill is helping to explain why fentanyl is ... approximately 40 to 50 times more potent than pharmaceutical ... users as heroin, the risk of death skyrockets. ...
(Date:8/28/2015)... SAN FRANCISCO, Calif. , Aug. 28, 2015 /PRNewswire/ ... for the treatment of cancer, today announced the filing ... U.S. Securities and Exchange Commission (SEC) relating to a ... number of shares to be offered and the price ... CytomX intends to list its common stock under the ...
(Date:8/28/2015)... -- Research and Markets ( ... "Investigation Report on China,s Pranoprofen Market, 2010-2019" ... discovered by Welfide (Mitsubishi Tanabe Pharma Corporation formerly ... inflammatory drug, pranoprofen was later developed into eye ... trade name of pranopulin for the treatment of ...
Breaking Medicine Technology:Lakeview Health's Dr. Philip Hemphill Explains Why Heroin Addicts Are Now Dying of Fentanyl Overdoses 2CytomX Files Registration Statement for Proposed Initial Public Offering 2Investigation Report on China's Pranoprofen Market, 2010-2019 2
... on Benefit of Intensive Blood Sugar Control Are, Not Statistically Significant but ... ... Events, SAN FRANCISCO, June 8 Findings from ... study in high-risk diabetes patients were,released today at the 68th Scientific Sessions ...
... Therapy in Q1 2008, SAN FRANCISCO, June 7 ... Lilly and Company (NYSE: LLY ) today announced,additional ... diabetes who were,unable to achieve glycemic control through diet ... BYETTA(R) (exenatide),injection taken twice daily or placebo. Study findings ...
Cached Medicine Technology:Large, Long-Term Veterans Affairs Diabetes Trial (VADT) Reveals Important Cardiovascular Safety News on AVANDIA(R) 2Large, Long-Term Veterans Affairs Diabetes Trial (VADT) Reveals Important Cardiovascular Safety News on AVANDIA(R) 3Large, Long-Term Veterans Affairs Diabetes Trial (VADT) Reveals Important Cardiovascular Safety News on AVANDIA(R) 4Monotherapy BYETTA(R) (exenatide) Injection Study Results Presented at ADA 2008 Showed Adults with Type 2 Diabetes Experienced Improved Glycemic Control and Weight Loss 2Monotherapy BYETTA(R) (exenatide) Injection Study Results Presented at ADA 2008 Showed Adults with Type 2 Diabetes Experienced Improved Glycemic Control and Weight Loss 3Monotherapy BYETTA(R) (exenatide) Injection Study Results Presented at ADA 2008 Showed Adults with Type 2 Diabetes Experienced Improved Glycemic Control and Weight Loss 4Monotherapy BYETTA(R) (exenatide) Injection Study Results Presented at ADA 2008 Showed Adults with Type 2 Diabetes Experienced Improved Glycemic Control and Weight Loss 5Monotherapy BYETTA(R) (exenatide) Injection Study Results Presented at ADA 2008 Showed Adults with Type 2 Diabetes Experienced Improved Glycemic Control and Weight Loss 6Monotherapy BYETTA(R) (exenatide) Injection Study Results Presented at ADA 2008 Showed Adults with Type 2 Diabetes Experienced Improved Glycemic Control and Weight Loss 7
... Pediatric Flowmeters, ,Options: , ... S to model number. Example: ... add suffix C to model ... Double Flowmeters with Power Take-Off, ...
FM Style Neonatal Flowmeters (Brass Body)...
... Adult Flowmeters, ,Options: , ... S to model number. Example: ... add suffix C to model ... Double Flowmeters with Power Take-Off, ...
... designed specifically for detection of recent-onset neovascular ... perimeter maps and quantifies visual field defects ... AMD to the wet stage of the ... compensate for small visual field defects, the ...
Medicine Products: