Navigation Links
McGill's 'Orphan Drug' research offers hope
Date:6/1/2010

This release is available in French.

In addition to their suffering, rare disease patients often have to face the harsh reality that few pharmaceutical companies will ever be able to offer new treatments for their condition because the costs of new treatments will never be recovered from such a small market. But there are ways they can be helped. The U.S. Food and Drug Administration's "Orphan Drug Designation" offers a wide range of benefits that help organizations developing treatments for diseases and conditions affecting fewer than 200,000 patients in the United States. It was recently granted to McGill University for research conducted at the MUHC into the use of the drug fenretinide for the treatment of pulmonary infections caused by Pseudomonas aeruginosa in patients with Cystic Fibrosis (CF).

CF is a chronic, hereditary disease affecting the respiratory and digestive systems of approximately 70,000 people worldwide. Pseudomonas aeruginosa infects more than 80 per cent of CF patients and contributes to the decline in pulmonary function the ability of the body to pump blood between the heart and the lungs. The infection is a major cause of sickness and death and is difficult to treat since it is resistant to many drugs.

"We strongly believe that fenretinide has the potential to improve morbidity and prognosis in CF patients at different levels," said Dr. Danuta Radzioch, a professor of Experimental Medicine at the MUHC and McGill's Faculty of Medicine. "Our research has demonstrated that fenretinide reduced lung inflammation as well as the frequency and the severity of pulmonary infections." Fenretinide is a drug that was originally investigated for potential use in the treatment of cancer but has not been commercially available.

Orphan Drug Designation provides opportunities for grant funding toward clinical-trial costs, tax ad
'/>"/>

Contact: William Raillant-Clark
william.raillant-clark@mcgill.ca
514-398-2189
McGill University
Source:Eurekalert

Page: 1 2

Related medicine news :

1. NextAid Presents BIDS BUILD HOPE Online Auction to Benefit Projects on the Ground in Africa on World AIDS Orphans Day
2. Celebrity Event to Help Haitian Orphans Devastated by Earthquake
3. Foster care associated with improved growth, intelligence compared to orphanage care
4. International Collaboration: FDA and European Medicines Agency Agree to Accept a Single Orphan Drug Designation Annual Report
5. Aton Pharma Announces Michael H. Richardson to Head Orphan Drug Division
6. International Breast Milk Project Delivers Donor Breast Milk to Orphaned and Sick Babies in Haiti
7. Orphans International Worldwide Haiti Near Jacmel to Grow After Earthquake
8. Haitian Orphanage Receives BPA-Free Baby Bottle Donation from Glendale Company
9. Israel Flying Aid, Orange Israel Create Haiti Orphanage, Provide Humanitarian Aid
10. Haitian Orphanage Takes Quick Action to Fill Void after Devastating Earthquakes
11. BHR Pharma Files Investigational New Drug Application, Receives Orphan Drug Designation, for Traumatic Brain Injury Treatment
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:4/18/2015)... (PRWEB) April 18, 2015 Lower-auto-insurance.com has ... accurate auto insurance quotes . , ... policies by comparing quotes. A professional insurance brokerage website ... insurance quotes, in a simple, convenient way. The whole ... to anyone. , Comparing online car insurance quotes ...
(Date:4/18/2015)... (PRWEB) April 18, 2015 Thousand of ... on behalf of individuals who were allegedly harmed by ... to move forward in the U.S. District Court, Northern ... 10th, the Court has amended an earlier Case Management ... Among other things, the new amendment permits the claims ...
(Date:4/18/2015)... 18, 2015 More than 2000 styles ... at TheCelebrityDresses.com, the #1 online store carrying celebrity inspired ... girls have got their perfect dresses for their prom. ... fashion prom dresses at TheCelebrityDresses.com would be an ideal ... than 2000 prom dresses inspired by the most loved ...
(Date:4/18/2015)... April 18, 2015 Aureus Medical ... staffing, including physical therapy jobs, has announced that ... South Carolina Physical Therapy Association Annual Conference to ... Center in Greenville, SC. , The SCAPTA ... exhibits with products and services. , Representatives ...
(Date:4/18/2015)... PHOENIX, ARIZONA – In March, Mark ... other secure destruction professionals across the United States, earned ... will now display “CSDS” as a professional title with ... National Association of Information Destruction 2015 Annual Conference began ... Of the 20 people who took the exam, Ona ...
Breaking Medicine News(10 mins):Health News:Auto Insurance Quotes Can Provide Accurate Results! 2Health News:DePuy Pinnacle Hip Lawsuits: Federal Litigation Amends Case Management Order to Allow for Joinder of Unrelated Claims 2Health News:DePuy Pinnacle Hip Lawsuits: Federal Litigation Amends Case Management Order to Allow for Joinder of Unrelated Claims 3Health News:Prom Dresses 2015 on Sale at TheCelebrityDresses.com 2Health News:Healthcare Staffing Leader, Aureus Medical Group, to Exhibit at the South Carolina Physical Therapy Association Annual Conference 2
... The Mall at The Source in Westbury, NY. , ... Freeport, NY ... Merchants Protective Co., Inc. (NYMPC) as the exclusive provider of fire-alarm services ... , ,Under the agreement, NYMPC will take over all ongoing maintenance for ...
... LOS ANGELES, Dec. 12 SEIU announced today that,its ... of a,single local uniting the state,s long-term care workers. ... decision-making,body, will weigh the results of the non-binding advisory ... the representation of California,long-term care workers. , ...
... Other drugs in pipeline also hold promise against ... 11 (HealthDay News) -- Researchers continue to test ... three decades after tamoxifen changed the medical landscape ... women with estrogen receptor-positive tumors. , Encouraging findings ...
... Centers Receive Annual HeartMath® Awards , ... Boulder Creek, ... commitment to taking care of patients by taking care of their ... improve their facilities by embracing that philosophy has earned each the ...
... The Ohio Nurses Association reached and ratified an ... December 9, 2008. The 3-year contract includes a pay increase ... , The RNs employed by the ... Each and every day they provide compassionate care to individuals ...
... Reviews Strategies and Progress , , NEW ... announced that Stephen Hughes, Smart Balance Chairman and CEO, spoke at a ... York, NY, at noon EST on Thursday, December 11, 2008. , ... the meeting about the Company,s focus on the strategic leverage of its ...
Cached Medicine News:Health News:Simon Property Group Selects New York Merchants Protective Co., Inc. for Fire-alarm Services 2Health News:Simon Property Group Selects New York Merchants Protective Co., Inc. for Fire-alarm Services 3Health News:California SEIU Members Support Single Union Uniting Long-Term Care Workers 2Health News:California SEIU Members Support Single Union Uniting Long-Term Care Workers 3Health News:Osteoporosis Drug Seems to Shrink Breast Tumors 2Health News:Osteoporosis Drug Seems to Shrink Breast Tumors 3Health News:Patient Care Means Employee Care at Illinois Hospitals 2Health News:Patient Care Means Employee Care at Illinois Hospitals 3Health News:Patient Care Means Employee Care at Illinois Hospitals 4Health News:Patient Care Means Employee Care at Illinois Hospitals 5Health News:Patient Care Means Employee Care at Illinois Hospitals 6Health News:Smart Balance Presented to the Consumer Analyst Group of New York 2Health News:Smart Balance Presented to the Consumer Analyst Group of New York 3
(Date:4/17/2015)... Va. , April 17, 2015   ... distribution of radiopharmaceuticals, announced today that it has signed ... Molecular North America, Inc. (IBAM NA), to Illinois Health and ... to operate as an independent company headquartered in ... positioned to take advantage of new product and footprint ...
(Date:4/17/2015)... Bionomics Limited (ASX:BNO, ADR:BMICY), a biopharmaceutical company ... for the treatment of cancer and diseases of the ... from three of its most advanced oncology programs at ... th Annual Meeting being held from April 18-22, ... The presentation on the BNC105 program ...
(Date:4/16/2015)... 2015 A drug commonly taken to prevent seizures ... multiple sclerosis (MS), according to a study released today that ... Annual Meeting in Washington, DC , April ... people with MS experience at some point in their life ... carrying vision from the eye to the brain gets inflamed," ...
Breaking Medicine Technology:Health Care System to Acquire IBA Molecular North America 2Health Care System to Acquire IBA Molecular North America 3Bionomics Showcases Oncology Drug Development Programs at 2015 AACR Annual Meeting 2Bionomics Showcases Oncology Drug Development Programs at 2015 AACR Annual Meeting 3Bionomics Showcases Oncology Drug Development Programs at 2015 AACR Annual Meeting 4Bionomics Showcases Oncology Drug Development Programs at 2015 AACR Annual Meeting 5Epilepsy Drug May Preserve Eyesight for People with MS 2
... is a national reference laboratory and a ... development. ARUP offers an extensive test menu ... in clinical and anatomic pathology. Owned by ... include more than half of the nation's ...
... national reference laboratory and a worldwide leader ... offers an extensive test menu of highly ... and anatomic pathology. Owned by the University ... than half of the nation's university teaching ...
... reference laboratory and a worldwide leader in ... an extensive test menu of highly complex ... anatomic pathology. Owned by the University of ... half of the nation's university teaching hospitals ...
... reference laboratory and a worldwide leader in ... an extensive test menu of highly complex ... anatomic pathology. Owned by the University of ... half of the nation's university teaching hospitals ...
Medicine Products: