Navigation Links
Gene Therapy Shows Promise for Muscular Dystrophy
Date:5/21/2010

Small study found technique restored some muscle function for months

FRIDAY, May 21 (HealthDay News) -- Scientists have succeeded in using gene therapy to restore some muscle function in patients with a certain type of muscular dystrophy.

This is the first time such a feat has been performed in humans, state the authors, who are presenting their findings at the annual meeting of the American Society of Gene & Cell Therapy in Washington, D.C.

"This study provides additional information regarding the feasibility of gene therapy for the treatment of muscular dystrophy," said Dr. Valerie Cwik, executive vice president and research and medical director of the Muscular Dystrophy Association, which helped fund the research. "Specifically, it provides proof of principle, in people, for sustained gene expression [for at least six months] following treatment."

"This study has shown that a normal gene packed into a virus and injected directly into a muscle can actually produce the protein that is either defective or missing in this particular form of muscular dystrophy," added Dr. Rabi Tawil, a professor of neurology at the University of Rochester Medical Center. "Similar studies have been done in animal models, and this is the first to show a similar result in humans."

If replicated, the findings could provide hope for people with this and other forms of muscular dystrophy.

"Reversing or significantly blunting the severity of this weakness and wasting will give these patients major improvement in their quality of life, enhance their independence, and increase the likelihood that they can obtain employment," said Dr. Richard Moxley, director of the Neuromuscular Disease Center, also at the University of Rochester Medical Center.

The patients in this study had limb-girdle muscular dystrophy (LGMD), which is characterized by muscle weakness around the hips and shoulders. The condition resul
'/>"/>

Copyright©2010 ScoutNews,LLC.
All rights reserved

Page: 1 2 3

Related medicine news :

1. Targeted therapy prolongs life in patients with HER2-positive breast cancer
2. PharmMD Secures Investments to Fund New Opportunities in Medication Therapy Management
3. More smokers kick the habit with extended nicotine patch therapy, Penn research shows
4. Experts Issue Warning on Prostate Hormone Therapy
5. ASGCT: Gene Therapy Shows Promise for Patients with Pompe Disease
6. AAPM statement on quality radiation therapy
7. Congress Urged to Take Immediate Action to Ensure Frail Patients Continue to Receive Critical Therapy Services
8. Intensive Insulin Therapy Wont Boost Septic Shock Survival
9. News brief: Dermatologic infections in cancer patients treated with EGFRI therapy
10. A new target for lymphoma therapy
11. NCCN Guidelines for Non-Small Cell Lung Cancer Updated to Incorporate Maintenance Therapy
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:12/21/2014)... (PRWEB) December 21, 2014 AngelWeddingDress.com’s new ... There is a total of 1,000 new designs in ... the coming spring 2015. , AngelWeddingDress.com promises ... female shoppers with wardrobe essentials while many fashion trends ... problems, the customer service team at AngelWeddingDress.com is ready ...
(Date:12/21/2014)... AlignLife of Norton Shores is ... the same time helping people get their health back. ... committed to serving those persons in Muskegon County who are ... the quality of life. Dr. Michael Rykse wanted to do ... local community and he knew he found that when he ...
(Date:12/21/2014)... December 21, 2014 Theme ... a new intro plugin for Final Cut Pro X ... videos, logos, and more with absolute ease.” Said Christiana ... users the tools needed to easily animate their media ... Cut Pro X users to animate pictures, videos, logos, ...
(Date:12/20/2014)... 2014 BambooIndustry.com is a professional company ... The business has recently shown its new engineered bamboo ... its bamboo flooring models. , BambooIndustry.com’s customers come from ... and more. According to the CEO of the company, ... fast in the past few years, and the demand ...
(Date:12/20/2014)... (PRWEB) December 20, 2014 Dress company LunaDress ... dresses, and announced its Christmas Sale, offering big discounts on ... “Every girl has an idea to own a perfect wedding ... for your wedding dress, then come to LunaDress. Many different ... for you. Visit our website now and enjoy the current ...
Breaking Medicine News(10 mins):Health News:2015 Spring Wedding Dresses From AngelWeddingDress Just Released 2Health News:AlignLife of Norton Shores Makes a Brighter Christmas for Kids in Muskegon 2Health News:Announcing a new plugin for Final Cut Pro X ProMotion from Pixel Film Studios. 2Health News:BammbooIndustry.com: Big Discounts On All Kinds Of Bamboo Flooring Collections 2Health News:2015 Collection of Wedding Dresses from LunaDress Online on Sale Now 2
... and sensor standardization, ... process efficiencies and reduces costs, IRVINE, Calif., ... the inventor of Pulse CO-Oximetry and,Measure-Through-Motion-and-Low-Perfusion Pulse Oximetry, ... hospital-wide implementation,of Masimo SET pulse oximetry. The New ...
... Colo., May 9 ABR-Affinity,BioReagents, a leading ... new distribution agreements with LuBioScience GmbH,headquartered in ... Hungary, further expanding its already extensive network ... more than 30 years of expertise in ...
... to reach,stricken Myanmar, EVANSTON, Ill., May 9 ... cyclone ravaged Myanmar, among the first,charities actually to ... relief organization supported by Rotary clubs around the ... was on the ground Thursday (May,8) preparing to ...
... SheKnows.com,( http://www.SheKnows.com ), one of the fastest growing, ... as winner of America,s Most,Extreme Moms contest by ... (Photo: http://www.newscom.com/cgi-bin/prnh/20080509/LAF049 ), Stevenson lives in ... strip mine infiltration. "We,re trying to derail a ...
... vegetables reduced brain plaques in mouse experiments , , FRIDAY, ... many fruits and vegetables, may be able to battle ... , In experiments with mice, two flavonoids called luteolin ... harmful plaques that build up in the brains of ...
... The U.S. Air Force has paid a family,$5 million ... childbirth at,a military hospital. The amount is a record ... damage because of the negligence of,government employees, according to ... Duckworth was born on September 4, 2004 at the ...
Cached Medicine News:Health News:Saint Barnabas Medical Center Converts to Masimo SET Technology - Establishing a Foundation for the Future of Pulse Oximetry 2Health News:Saint Barnabas Medical Center Converts to Masimo SET Technology - Establishing a Foundation for the Future of Pulse Oximetry 3Health News:Saint Barnabas Medical Center Converts to Masimo SET Technology - Establishing a Foundation for the Future of Pulse Oximetry 4Health News:Saint Barnabas Medical Center Converts to Masimo SET Technology - Establishing a Foundation for the Future of Pulse Oximetry 5Health News:ABR-Affinity BioReagents Inks New Distribution Agreements in Switzerland and Hungary 2Health News:Rotary Clubs Provide Emergency Shelters, Supplies to Cyclone Victims 2Health News:SheKnows Names America's Most Extreme Mom for Mother's Day 2Health News:Flavonoids May Help Treat Alzheimer's 2Health News:Flavonoids May Help Treat Alzheimer's 3Health News:U.S. Air Force Pays Record Amount for Baby Injured in Government Hospital 2
(Date:12/19/2014)... -- TODAY, AEGATE, the leader in medicine ... appointment of Peter Fox as Chief Technology ... Partner Officer. Peter has served as Development ... by Oracle in 2011. Prior to Datanomic, ... and subsequently Convergys, a world renowned billing system ...
(Date:12/19/2014)... BOCA RATON, Fla. , Dec. 19, 2014 /PRNewswire/ ... entered into a multi-product agreement with MSN Laboratories Pvt. ... Breckenridge and MSN expect to commercialize several new ANDAs. ... manufacture, and supply the products exclusively to Breckenridge for ... the products under its label.  Breckenridge and MSN have ...
(Date:12/19/2014)... , Dec. 19, 2014  Monarch America Inc. (OTCQB: ... Corp.) is pleased to provide this review of the ... in 2015. "Over this past year, we ... I am extremely proud to say that Monarch America ... than it has ever been," stated Eric Hagen ...
Breaking Medicine Technology:Aegate Appoints new CTO and Chief Channels & Partner Officer 2Aegate Appoints new CTO and Chief Channels & Partner Officer 3Aegate Appoints new CTO and Chief Channels & Partner Officer 4Breckenridge Pharmaceutical signs Multi-Product Generic Agreement with MSN Laboratories Pvt. Ltd. 2Monarch America Inc. CEO Reviews Recent Achievements and Provides Outlook for 2015 2Monarch America Inc. CEO Reviews Recent Achievements and Provides Outlook for 2015 3
... MYL ) today announced that it has notified The ... (Nasdaq: NDAQ ), that it intends to voluntarily de-list ... Market, on which the notes trade under the ticker symbol "MYLNG," ... The notes will continue to trade over-the-counter (OTC) with trade data ...
... Ultra Clean Holdings, Inc. (Nasdaq: UCTT ), ... semiconductor capital equipment, medical device, energy, research, and flat ... Executive Officer, and Casey Eichler, Chief Financial Officer, will ... will take place at the New York Palace Hotel, ...
Cached Medicine Technology:Mylan Announces Voluntary De-listing of 1.25% Senior Convertible Notes Due 2012 from Nasdaq 2
... national reference laboratory and a worldwide leader ... offers an extensive test menu of highly ... and anatomic pathology. Owned by the University ... than half of the nation's university teaching ...
... a national reference laboratory and a worldwide ... ARUP offers an extensive test menu of ... clinical and anatomic pathology. Owned by the ... more than half of the nation's university ...
... reference laboratory and a worldwide leader in ... an extensive test menu of highly complex ... anatomic pathology. Owned by the University of ... half of the nation's university teaching hospitals ...
... is a national reference laboratory and a ... development. ARUP offers an extensive test menu ... in clinical and anatomic pathology. Owned by ... include more than half of the nation's ...
Medicine Products: