Navigation Links
Ataluren Phase 3 trial results in nonsense mutation cystic fibrosis
Date:5/16/2014

s study were CF pulmonary exacerbations and were considered unrelated to ataluren treatment. Eight patients in the ataluren arm and three patients in the placebo arm discontinued treatment due to an adverse event.

"We are very encouraged by the data from this trial. Given spirometry and pulmonary exacerbation results in the subgroup of patients not receiving chronic inhaled tobramycin, and a favorable safety profile, this study supports further clinical testing of ataluren as a potential first-in-class treatment for nmCF patients not receiving chronic inhaled tobramycin," stated Stuart W. Peltz, Ph.D., Chief Executive Officer of PTC Therapeutics, Inc. "We look forward to initiating a confirmatory ataluren trial in nmCF patients later this year."


'/>"/>

Contact: Katelyn McCarthy
katelyn.mccarthy@uhhospitals.org
216-767-8582
University Hospitals Case Medical Center
Source:Eurekalert

Page: 1 2 3

Related medicine news :

1. Moffitt Cancer Centers phase 3 study may be game-changer for acute myeloid leukemia
2. Celldexs Phase 1 study of CDX-1401 published in Science Translational Medicine
3. Moffitt Cancer Center begins Phase I clinical trial of new immunotherapy
4. Phase II trial of Bevacizumab (Avastin) in locally advanced cervical cancer promising
5. North Shore-LIJ Completes Last Phase of $50M Upgrade of its Diagnostic Imaging Systems, $12M for GE Low-Dose CT Scanners to Reduce Patients’ Radiation Exposure
6. Stryker Hip Lawsuit News: Phase II of Mediation Set to Begin in Stryker Hip Recall Litigation Underway in New Jersey State Court, Bernstein Liebhard LLP Reports
7. LFoundry Rousset LF 110 Flash Technology Enters Industrial Phase
8. “Final Phase Fat Loss” Introduces To People An Innovative Bodyweight Training Program – Vinamy
9. CS Caregiver University Announces Its First Phase of Inductive Training for the Month of October
10. Rockland Immunochemicals Awarded Phase I SBIR Funding to Develop Novel Agents for Cancer Diagnosis and Targeted Therapy
11. For first time, drug developed based on zebrafish studies passes Phase I clinical trial
Post Your Comments:
*Name:
*Comment:
*Email:
(Date:7/31/2015)... ... July 31, 2015 , ... There’s no better way to enjoy the summer ... to cook the next meal, making July the most appropriate to be National Hot ... and recipes. , Make the next cookout different than the ones in the past. ...
(Date:7/31/2015)... ... July 31, 2015 , ... Facebook, Twitter, Linkedin and ... their social media profiles to better connect with the public. The agency website ... information, share insights and opinions. The Rally Insurance Group, Inc.’s pledge to provide ...
(Date:7/31/2015)... ... July 31, 2015 , ... M3 USA MDLinx.com, source of the Smartest Doc ... Exam Courses. , The additions of Gastroenterology, Pulmonology and Allergy/Immunology round out an ... preparing for the exam easy and painless. MDLinx offers thousands of board-exam style ...
(Date:7/31/2015)... ... July 31, 2015 , ... According to the article published July 27 on ... courthouse was contained and extinguished by the city’s fire department before it caused major damage ... the time of the fire, and it was a fire alarm system that tipped off ...
(Date:7/31/2015)... ... July 31, 2015 , ... Well-known for its unique ... wedding cakes with custom designs, making life just a little bit sweeter ... wedding cakes for each customer who orders one. , The bakery provides a full ...
Breaking Medicine News(10 mins):Health News:King Kullen Honors National Hot Dog and Blueberry Month 2Health News:King Kullen Honors National Hot Dog and Blueberry Month 3Health News:Rally Insurance Group, Inc. Connects to Customers Through Re-branded Social Media Profiles 2Health News:MDLinx Offers Three New Board Exam Prep Courses - Gastroenterology, Pulmonology and Allergy/Immunology 2Health News:MDLinx Offers Three New Board Exam Prep Courses - Gastroenterology, Pulmonology and Allergy/Immunology 3Health News:Article on Recent Pasadena Courtroom Fire Highlights the Effectiveness of Fire Alarm Systems, Says Fire Protection Group Inc 2Health News:Article on Recent Pasadena Courtroom Fire Highlights the Effectiveness of Fire Alarm Systems, Says Fire Protection Group Inc 3Health News:Pastry Palace of Las Vegas Announces It Is Now Offering Custom Wedding Cakes in Las Vegas 2
... says that a serving or two of dark or bitter ... comes as a breath of fresh “sweet” air from Swiss ... at Zurich's University hospital. They investigated and found after tests ... cocoa content (75 per cent) improved their blood circulation "significantly". ...
... Executive Director Peter Ellis has revealed that a version of the ... dysfunction market is much larger when compared to that of men, ... pill for that, according to Ellis. The desire, arousal and pain ... the pill, which will make it all the more difficult to ...
... flight attendants working for a National European Airline from ... they rate their health as poor when they have ... to the other women who are working with the ... attention, being proposed, ogled at, subjected to offensive remarks ...
... brandy per day reportedly has a similar antioxidant potential which ... belonging to the Monash University. This does not mean that ... can continue along with drinking brandy. ,Red ... arteries are de-sludged by its consumption in addition to it ...
... at risk for high blood pressure, heart disease and ... current issue of the American Journal of Preventive Medicine. ... blood pressure, or hypertension, generally consume less sodium than ... than recommended levels, according to lead researcher Umed Ajani, ...
... The National Institutes of Health (NIH) has revealed that the ... the youngsters in the US. There has however been an ... purposes. The University of Michigan conducted the 2005 Monitoring the ... overall results were good. , ,It found that cigarette ...
Cached Medicine News:Health News:Americans Consume Far Too Much Salt and Sodium 2Health News:Drug Use On The Decline Among US Youth 2
(Date:7/30/2015)... July 30, 2015  Amgen (NASDAQ: AMGN ) today ... managing director of Warburg Pincus LLC, to the Amgen Board ... Fred Hassan and the deep, global experience he ... Robert A. Bradway , chairman and chief executive officer ... will serve Amgen well." Mr. Hassan has been ...
(Date:7/30/2015)... WOODCLIFF LAKE, N.J. , July 30, 2015 /PRNewswire/ ... submitted simultaneously in the United States ... (to the FDA, EMA and MHLW, respectively) for eribulin, ... sarcoma (STS) who have received prior chemotherapy for advanced ... are based on data from a pivotal global Phase ...
(Date:7/30/2015)... NEW YORK , July 30, 2015 ... releases a new research report with market ... size, share, forecast, porter analysis, recent developments, ... Global Industry Insight: Biosensors Market ...      (Logo: http://photos.prnewswire.com/prnh/20150727/756778 ) ...
Breaking Medicine Technology:Amgen Announces Appointment Of Fred Hassan To Board Of Directors 2Amgen Announces Appointment Of Fred Hassan To Board Of Directors 3Eisai Submits Simultaneous Regulatory Applications for Eribulin in Soft Tissue Sarcoma in the United States, European Union and Japan 2Eisai Submits Simultaneous Regulatory Applications for Eribulin in Soft Tissue Sarcoma in the United States, European Union and Japan 3Eisai Submits Simultaneous Regulatory Applications for Eribulin in Soft Tissue Sarcoma in the United States, European Union and Japan 4Eisai Submits Simultaneous Regulatory Applications for Eribulin in Soft Tissue Sarcoma in the United States, European Union and Japan 5Global Biosensors Market (Size of $12,964 Million in 2014) to Witness 10% CAGR During 2015 - 2020 2Global Biosensors Market (Size of $12,964 Million in 2014) to Witness 10% CAGR During 2015 - 2020 3Global Biosensors Market (Size of $12,964 Million in 2014) to Witness 10% CAGR During 2015 - 2020 4Global Biosensors Market (Size of $12,964 Million in 2014) to Witness 10% CAGR During 2015 - 2020 5
... SmallCapVoice.com, Inc. announced today that a ... Inc. (OTCQB: MDHI), manufacturer of the MediPendant™, ... allows the users to speak and listen ... The interview can be heard at ...
... Genomic Health, Inc . (Nasdaq: GHDX ... Chief Financial Officer, will present at the JMP Securities Healthcare ... at 3:00 p.m. Eastern Time (ET).   To ... visit the Investor Relations section of Genomic Health,s website at ...
Cached Medicine Technology:A New Audio Interview with Medical Alarm Concepts Holdings, Inc., CEO, Howard Teicher, is now at SmallCapVoice.com 2Genomic Health to Present at the JMP Securities Healthcare Conference 2Genomic Health to Present at the JMP Securities Healthcare Conference 3
... The VITROS HBsAg assay is ... by the U.S. Food and ... in a random,access format on ... Intellicheck. Now you can run ...
... For use as a non-reactive quality assurance ... immunodeficiency virus type 1 (anti-HIV-1), antibody to ... to human immunodeficiency virus type 1 (HIV-1 ... I (anti-HTLV-I), antibody to hepatitis C virus ...
... comprehensive line of pregnancy tests including rapid ... convenient one-step stick and cassette formats. The ... Easy HCG is a 25 mIU urine ... HCG II provides 25mIU sensitivity for ...
... comprehensive line of pregnancy tests including rapid ... convenient one-step stick and cassette formats. The ... Easy HCG is a 25 mIU urine ... HCG II provides 25mIU sensitivity for ...
Medicine Products: