- PTC Announces Initiation of Additional Phase 2b Clinical Trial Sites in
SOUTH PLAINFIELD, N.J., May 30 /PRNewswire/ -- PTC Therapeutics, Inc. (PTC) today announced that PTC124, the company's orally delivered investigational new drug for the treatment of genetic disorders due to nonsense mutations, was featured in a symposium at Myology 2008, the Third Annual Congress of Myology, on Friday, May 30 in Marseilles. The Congress serves as the annual meeting of The Association Francaise contre les Myopathies (French Muscular Dystrophy Association) and focuses on research, therapies and clinical trials for various forms of muscular dystrophy.
PTC124 is being studied in Duchenne muscular dystrophy (DMD), a progressive muscle disorder in which patients lack dystrophin, a protein that is critical to the structural stability of muscle fibers. PTC recently launched a global, registration-directed Phase 2b trial in DMD and Becker muscular dystrophy (BMD) to evaluate the efficacy of PTC124 as measured by improvements in the walking ability of patients with this progressive genetic disease.
Data from the previous Phase 2a study were presented and discussed by a panel of leading physicians and researchers, including: Dr. Thomas Voit, M.D., Medical and Scientific Director of the Myology Institute and Dr. Richard Finkel, M.D., Director of the Neuromuscular Program, Children's Hospital of Philadelphia, PA.
"PTC124 represents a promising new therapy for DMD/BMD, as there are currently no available treatments that address the underlying cause of this disease," stated Dr. Voit. "The Phase 2b PTC124 clinical trial sets a gold standard for future clinical trials in muscular dystrophies. I am delighted to be part of these groundbreaking studies."
|SOURCE PTC Therapeutics, Inc.|
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