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Experimental gene therapy treatment for Duchenne muscular dystrophy offers hope for youngster
Date:2/7/2013

and his study team are completing the protocol for each participant and analyzing the resulting data. They expect results sometime in late 2013 or 2014 once all the participants around the country have completed the trial.

In the meantime, even though no one knows whether Jacob received the genetic therapy drug or a placebo, his family is feeling good about being in a clinical trial. According to Jacob's dad, Timothy Rutt, the family even hopes to use some of its new frequent flyer miles for upcoming vacations.

"Jake really enjoyed being part of the study,'" said the elder Rutt, who, as the editor of an online news publication called altadenablog.com, has written about his son's participation. "We were proud that he showed a great deal of courage throughout the trial and understood its importance to kids like him."


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Contact: Charles Casey
charles.casey@ucdmc.ucdavis.edu
916-734-9048
University of California - Davis Health System
Source:Eurekalert

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